JP2022553375A5 - - Google Patents
Info
- Publication number
- JP2022553375A5 JP2022553375A5 JP2022523854A JP2022523854A JP2022553375A5 JP 2022553375 A5 JP2022553375 A5 JP 2022553375A5 JP 2022523854 A JP2022523854 A JP 2022523854A JP 2022523854 A JP2022523854 A JP 2022523854A JP 2022553375 A5 JP2022553375 A5 JP 2022553375A5
- Authority
- JP
- Japan
- Prior art keywords
- polynucleotide construct
- sequence
- seq
- composition
- expression cassette
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962924567P | 2019-10-22 | 2019-10-22 | |
| US62/924,567 | 2019-10-22 | ||
| PCT/US2020/056890 WO2021081225A1 (en) | 2019-10-22 | 2020-10-22 | Ornithine transcarbamylase (otc) constructs and methods of using the same |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2022553375A JP2022553375A (ja) | 2022-12-22 |
| JP2022553375A5 true JP2022553375A5 (enExample) | 2023-10-26 |
| JP7826197B2 JP7826197B2 (ja) | 2026-03-09 |
Family
ID=75620841
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022523854A Active JP7826197B2 (ja) | 2019-10-22 | 2020-10-22 | オルニチントランスカルバミラーゼ（ｏｔｃ）構築物およびそれを使用する方法 |
Country Status (9)
| Country | Link |
|---|---|
| US (1) | US20230001021A1 (enExample) |
| EP (1) | EP4048317A4 (enExample) |
| JP (1) | JP7826197B2 (enExample) |
| KR (1) | KR20240130161A (enExample) |
| CN (1) | CN116096428A (enExample) |
| AU (1) | AU2020371697A1 (enExample) |
| CA (1) | CA3158626A1 (enExample) |
| IL (1) | IL292420A (enExample) |
| WO (1) | WO2021081225A1 (enExample) |
Families Citing this family (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| HRP20240586T1 (hr) | 2018-10-09 | 2024-07-19 | The University Of British Columbia | Sastavi i sustavi koji sadrže transfekcijske sposobne vezikle bez organskih otapala i deterdženta i s njim povezanim postupcima |
| US20240216545A1 (en) * | 2021-04-28 | 2024-07-04 | Genevant Sciences Gmbh | Mrna delivery constructs and methods of using the same |
| KR20230083893A (ko) * | 2021-12-03 | 2023-06-12 | 고려대학교 산학협력단 | 번역 효율이 향상된 5'-utr, 이를 포함하는 합성 핵산 분자 및 이를 포함하는 백신 또는 치료제 조성물 |
| CN121335707A (zh) * | 2023-03-06 | 2026-01-13 | 通用药品有限责任公司 | 密码子优化及其使用方法 |
Family Cites Families (8)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| EP2817287B1 (en) | 2012-02-24 | 2018-10-03 | Arbutus Biopharma Corporation | Trialkyl cationic lipids and methods of use thereof |
| JP6620093B2 (ja) * | 2013-07-23 | 2019-12-11 | アービュートゥス バイオファーマ コーポレイションＡｒｂｕｔｕｓ Ｂｉｏｐｈａｒｍａ Ｃｏｒｐｏｒａｔｉｏｎ | メッセンジャーｒｎａを送達するための組成物及び方法 |
| AU2014296278C1 (en) * | 2013-07-30 | 2023-02-02 | Genevant Sciences Gmbh | Block copolymers and their conjugates or complexes with oligonucleotides |
| US9765477B2 (en) * | 2013-08-23 | 2017-09-19 | Dow Global Technologies Llc | Low density attached polyurethane foams made using a combination of frothing and blowing methods |
| JP2018509387A (ja) | 2015-01-21 | 2018-04-05 | フェーズアールエックス インコーポレイテッド | 細胞に治療および診断剤を送達するための方法、組成物、ならびにシステム |
| EP3469074B1 (en) * | 2016-06-13 | 2020-12-09 | Translate Bio, Inc. | Messenger rna therapy for the treatment of ornithine transcarbamylase deficiency |
| PT3568483T (pt) * | 2017-01-10 | 2025-11-18 | Childrens Medical Res Institute | Polinucleótidos e vetores para a expressão de transgenes |
| CA3079428A1 (en) * | 2017-11-22 | 2019-05-31 | Modernatx, Inc. | Polynucleotides encoding ornithine transcarbamylase for the treatment of urea cycle disorders |
-
2020
- 2020-10-22 KR KR1020227017024A patent/KR20240130161A/ko active Pending
- 2020-10-22 WO PCT/US2020/056890 patent/WO2021081225A1/en not_active Ceased
- 2020-10-22 CN CN202080089266.1A patent/CN116096428A/zh active Pending
- 2020-10-22 CA CA3158626A patent/CA3158626A1/en active Pending
- 2020-10-22 EP EP20878326.6A patent/EP4048317A4/en active Pending
- 2020-10-22 AU AU2020371697A patent/AU2020371697A1/en active Pending
- 2020-10-22 US US17/771,421 patent/US20230001021A1/en active Pending
- 2020-10-22 IL IL292420A patent/IL292420A/en unknown
- 2020-10-22 JP JP2022523854A patent/JP7826197B2/ja active Active
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