JP2024515317A5 - - Google Patents

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Publication number
JP2024515317A5
JP2024515317A5 JP2023566445A JP2023566445A JP2024515317A5 JP 2024515317 A5 JP2024515317 A5 JP 2024515317A5 JP 2023566445 A JP2023566445 A JP 2023566445A JP 2023566445 A JP2023566445 A JP 2023566445A JP 2024515317 A5 JP2024515317 A5 JP 2024515317A5
Authority
JP
Japan
Prior art keywords
polynucleotide construct
sequence
expression cassette
host cell
plasmid
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023566445A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024515317A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/IB2022/053966 external-priority patent/WO2022229903A1/en
Publication of JP2024515317A publication Critical patent/JP2024515317A/ja
Publication of JP2024515317A5 publication Critical patent/JP2024515317A5/ja
Pending legal-status Critical Current

Links

JP2023566445A 2021-04-28 2022-04-28 ｍＲＮＡ送達構築物およびそれを使用する方法 Pending JP2024515317A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163181115P 2021-04-28 2021-04-28
US63/181,115 2021-04-28
PCT/IB2022/053966 WO2022229903A1 (en) 2021-04-28 2022-04-28 Mrna delivery constructs and methods of using the same

Publications (2)

Publication Number Publication Date
JP2024515317A JP2024515317A (ja) 2024-04-08
JP2024515317A5 true JP2024515317A5 (enExample) 2025-05-09

Family

ID=81749469

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023566445A Pending JP2024515317A (ja) 2021-04-28 2022-04-28 ｍＲＮＡ送達構築物およびそれを使用する方法

Country Status (4)

Country Link
US (1) US20240216545A1 (enExample)
EP (1) EP4330404A1 (enExample)
JP (1) JP2024515317A (enExample)
WO (1) WO2022229903A1 (enExample)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN118021956A (zh) * 2022-11-11 2024-05-14 深圳先进技术研究院 一种编码抗禽流感H7N9病毒抗体的mRNA及其制法和应用

Family Cites Families (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP2817287B1 (en) 2012-02-24 2018-10-03 Arbutus Biopharma Corporation Trialkyl cationic lipids and methods of use thereof
WO2013151665A2 (en) * 2012-04-02 2013-10-10 modeRNA Therapeutics Modified polynucleotides for the production of proteins associated with human disease
CA3079428A1 (en) * 2017-11-22 2019-05-31 Modernatx, Inc. Polynucleotides encoding ornithine transcarbamylase for the treatment of urea cycle disorders
CN119570787A (zh) * 2018-05-11 2025-03-07 比姆医疗股份有限公司 使用可编程碱基编辑器系统遏止病原性突变的方法
CN113710799B (zh) * 2018-11-28 2024-11-12 克里斯珀医疗股份公司 用于在LNP中使用的编码CAS9的优化mRNA
KR20240130161A (ko) * 2019-10-22 2024-08-29 제네반트 사이언시즈 게엠베하 오르니틴 트랜스카르바밀라제 (otc) 구축물 및 그의 사용 방법

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