JP2025510946A5 - - Google Patents

Info

Publication number
JP2025510946A5
JP2025510946A5 JP2024557464A JP2024557464A JP2025510946A5 JP 2025510946 A5 JP2025510946 A5 JP 2025510946A5 JP 2024557464 A JP2024557464 A JP 2024557464A JP 2024557464 A JP2024557464 A JP 2024557464A JP 2025510946 A5 JP2025510946 A5 JP 2025510946A5
Authority
JP
Japan
Prior art keywords
amino acid
seq
aav
acid sequence
capsid polypeptide
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024557464A
Other languages
English (en)
Japanese (ja)
Other versions
JP2025510946A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2023/016860 external-priority patent/WO2023192454A2/en
Publication of JP2025510946A publication Critical patent/JP2025510946A/ja
Publication of JP2025510946A5 publication Critical patent/JP2025510946A5/ja
Pending legal-status Critical Current

Links

JP2024557464A 2022-03-30 2023-03-30 網膜領域にまたがり核酸を送達するためのアデノ随伴ウイルスベクター Pending JP2025510946A (ja)

Applications Claiming Priority (13)

Application Number Priority Date Filing Date Title
US202263325543P 2022-03-30 2022-03-30
US202263325542P 2022-03-30 2022-03-30
US202263325544P 2022-03-30 2022-03-30
US202263325553P 2022-03-30 2022-03-30
US202263325558P 2022-03-30 2022-03-30
US202263325562P 2022-03-30 2022-03-30
US63/325,562 2022-03-30
US63/325,544 2022-03-30
US63/325,558 2022-03-30
US63/325,542 2022-03-30
US63/325,543 2022-03-30
US63/325,553 2022-03-30
PCT/US2023/016860 WO2023192454A2 (en) 2022-03-30 2023-03-30 Adeno-associated virus vectors for nucleic acid delivery across retinal regions

Publications (2)

Publication Number Publication Date
JP2025510946A JP2025510946A (ja) 2025-04-15
JP2025510946A5 true JP2025510946A5 (enExample) 2026-04-07

Family

ID=88203537

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024557464A Pending JP2025510946A (ja) 2022-03-30 2023-03-30 網膜領域にまたがり核酸を送達するためのアデノ随伴ウイルスベクター

Country Status (11)

Country Link
US (1) US20250222135A1 (enExample)
EP (1) EP4499847A4 (enExample)
JP (1) JP2025510946A (enExample)
KR (1) KR20240168434A (enExample)
CN (1) CN119213134A (enExample)
AU (1) AU2023245716A1 (enExample)
CA (1) CA3255242A1 (enExample)
IL (1) IL315751A (enExample)
MX (1) MX2024011862A (enExample)
TW (1) TW202405181A (enExample)
WO (1) WO2023192454A2 (enExample)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
TW202605144A (zh) * 2024-05-02 2026-02-01 美商艾維斯塔醫療公司 用於將治療性核酸遞送至視網膜細胞之腺相關病毒載體

Family Cites Families (7)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US6156303A (en) * 1997-06-11 2000-12-05 University Of Washington Adeno-associated virus (AAV) isolates and AAV vectors derived therefrom
US7504490B1 (en) * 1998-10-16 2009-03-17 Oscient Pharmaceuticals Corporation Nucleic acid and amino acid sequences relating to Apergillus fumigatus for diagnostics and therapeutics
US20040031072A1 (en) * 1999-05-06 2004-02-12 La Rosa Thomas J. Soy nucleic acid molecules and other molecules associated with transcription plants and uses thereof for plant improvement
DK3693025T3 (da) * 2011-04-22 2022-01-10 Univ California Adenoassocierede virus-virioner med variant capsid og fremgangsmåder til anvendelse heraf
KR20190075964A (ko) * 2016-10-13 2019-07-01 유니버시티 오브 매사추세츠 Aav 캡시드 설계
KR20250023600A (ko) * 2017-06-30 2025-02-18 더 리젠츠 오브 더 유니버시티 오브 캘리포니아 변이체 캡시드를 보유한 아데노-부속 바이러스 비리온 및 이의 사용 방법
IL299927A (en) * 2020-07-29 2023-03-01 Univ Florida Improved adeno-associated virus-mediated therapies for X-linked retinoschisis

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