JP2022552940A5 - - Google Patents

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Publication number
JP2022552940A5
JP2022552940A5 JP2022517729A JP2022517729A JP2022552940A5 JP 2022552940 A5 JP2022552940 A5 JP 2022552940A5 JP 2022517729 A JP2022517729 A JP 2022517729A JP 2022517729 A JP2022517729 A JP 2022517729A JP 2022552940 A5 JP2022552940 A5 JP 2022552940A5
Authority
JP
Japan
Prior art keywords
nucleic acid
small molecule
thrombocytopenia
modification
molecule
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2022517729A
Other languages
English (en)
Japanese (ja)
Other versions
JP2022552940A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/CN2020/116227 external-priority patent/WO2021052470A1/zh
Publication of JP2022552940A publication Critical patent/JP2022552940A/ja
Publication of JP2022552940A5 publication Critical patent/JP2022552940A5/ja
Pending legal-status Critical Current

Links

JP2022517729A 2019-09-20 2020-09-18 血小板減少症を治療するための核酸分子及びその応用 Pending JP2022552940A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
CN201910891508.8 2019-09-20
CN201910891508 2019-09-20
PCT/CN2020/116227 WO2021052470A1 (zh) 2019-09-20 2020-09-18 用于治疗血小板减少症的核酸分子及其应用

Publications (2)

Publication Number Publication Date
JP2022552940A JP2022552940A (ja) 2022-12-21
JP2022552940A5 true JP2022552940A5 (https=) 2023-09-25

Family

ID=74883124

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2022517729A Pending JP2022552940A (ja) 2019-09-20 2020-09-18 血小板減少症を治療するための核酸分子及びその応用

Country Status (12)

Country Link
US (1) US20230212565A1 (https=)
EP (1) EP4036232A4 (https=)
JP (1) JP2022552940A (https=)
KR (1) KR20220070206A (https=)
CN (1) CN114585738A (https=)
AU (1) AU2020349991A1 (https=)
BR (1) BR112022005028A2 (https=)
CA (1) CA3148158A1 (https=)
CO (1) CO2022004857A2 (https=)
PE (1) PE20220604A1 (https=)
TW (1) TW202126808A (https=)
WO (1) WO2021052470A1 (https=)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN111849968A (zh) 2019-04-30 2020-10-30 中美瑞康核酸技术(南通)研究院有限公司 寡核苷酸分子及其在急性间歇性卟啉症治疗中的应用
WO2024216109A1 (en) * 2023-04-12 2024-10-17 Alnylam Pharmaceuticals, Inc. Formulations for oligonucleotide delivery

Family Cites Families (12)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US6270989B1 (en) * 1991-11-05 2001-08-07 Transkaryotic Therapies, Inc. Protein production and delivery
GB2285446B (en) * 1994-01-03 1999-07-28 Genentech Inc Thrombopoietin
EP1871426B1 (en) * 2005-04-15 2017-06-07 The Regents of The University of California Small activating rna molecules and their use
WO2007086990A2 (en) * 2005-11-17 2007-08-02 Board Of Regents, The University Of Texas System Modulation of gene expression by oligomers targeted to chromosomal dna
KR101766408B1 (ko) 2009-06-10 2017-08-10 알닐람 파마슈티칼스 인코포레이티드 향상된 지질 조성물
GB201010557D0 (en) * 2010-06-23 2010-08-11 Mina Therapeutics Ltd RNA molecules and uses thereof
KR102195514B1 (ko) * 2011-06-21 2020-12-29 미나 테라퓨틱스 리미티드 알부민 생산 및 세포 증식
CN106032532A (zh) * 2015-03-17 2016-10-19 中国医学科学院北京协和医院 一种小激活rna及其制备方法和应用
KR102599712B1 (ko) * 2015-04-22 2023-11-09 미나 테라퓨틱스 리미티드 C/EBP 알파 saRNA 조성물 및 사용 방법
US20180305689A1 (en) * 2015-04-22 2018-10-25 Mina Therapeutics Limited Sarna compositions and methods of use
JP2019500345A (ja) * 2015-12-14 2019-01-10 コールド スプリング ハーバー ラボラトリー 肝臓病の処置のための組成物および方法
CN106480028B (zh) * 2016-10-12 2019-04-05 上海市第七人民医院 TPO基因的saRNA分子及其应用

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