JP2022533983A5 - - Google Patents

Info

Publication number
JP2022533983A5
JP2022533983A5 JP2021568813A JP2021568813A JP2022533983A5 JP 2022533983 A5 JP2022533983 A5 JP 2022533983A5 JP 2021568813 A JP2021568813 A JP 2021568813A JP 2021568813 A JP2021568813 A JP 2021568813A JP 2022533983 A5 JP2022533983 A5 JP 2022533983A5
Authority
JP
Japan
Application number
JP2021568813A
Other languages
Japanese (ja)
Other versions
JP7707081B2 (ja
JPWO2020236352A5 (https=
JP2022533983A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2020/028352 external-priority patent/WO2020236352A1/en
Publication of JP2022533983A publication Critical patent/JP2022533983A/ja
Publication of JP2022533983A5 publication Critical patent/JP2022533983A5/ja
Publication of JPWO2020236352A5 publication Critical patent/JPWO2020236352A5/ja
Application granted granted Critical
Publication of JP7707081B2 publication Critical patent/JP7707081B2/ja
Active legal-status Critical Current
Anticipated expiration legal-status Critical

Links

JP2021568813A 2019-05-17 2020-04-15 網膜細胞を標的とした最適化された遺伝子治療 Active JP7707081B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201962849794P 2019-05-17 2019-05-17
US62/849,794 2019-05-17
PCT/US2020/028352 WO2020236352A1 (en) 2019-05-17 2020-04-15 Optimized gene therapy targeting retinal cells

Publications (4)

Publication Number Publication Date
JP2022533983A JP2022533983A (ja) 2022-07-27
JP2022533983A5 true JP2022533983A5 (https=) 2023-04-25
JPWO2020236352A5 JPWO2020236352A5 (https=) 2023-04-25
JP7707081B2 JP7707081B2 (ja) 2025-07-14

Family

ID=70482910

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2021568543A Pending JP2022533645A (ja) 2019-05-17 2020-04-15 グリコシドヒドロラーゼ酵素を使用する網膜細胞への遺伝子治療ベクターの送達の改善
JP2021568813A Active JP7707081B2 (ja) 2019-05-17 2020-04-15 網膜細胞を標的とした最適化された遺伝子治療

Family Applications Before (1)

Application Number Title Priority Date Filing Date
JP2021568543A Pending JP2022533645A (ja) 2019-05-17 2020-04-15 グリコシドヒドロラーゼ酵素を使用する網膜細胞への遺伝子治療ベクターの送達の改善

Country Status (10)

Country Link
US (2) US20220233655A1 (https=)
EP (2) EP3969060A1 (https=)
JP (2) JP2022533645A (https=)
KR (1) KR20220009427A (https=)
CN (1) CN114126667A (https=)
AR (1) AR118696A1 (https=)
AU (2) AU2020278960A1 (https=)
CA (2) CA3141020A1 (https=)
TW (1) TW202110486A (https=)
WO (2) WO2020236351A1 (https=)

Families Citing this family (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
IL294102A (en) * 2019-12-25 2022-08-01 Lumus Ltd Optical systems and methods for tracking eyes based on directing light from the eye through an optical arrangement associated with a light-directing optical element
CN114516901B (zh) * 2022-03-11 2023-01-17 上海勉亦生物科技有限公司 一种神经系统高亲和性的aav载体及其应用
CN115323001B (zh) * 2022-07-28 2024-11-26 深圳先进技术研究院 一种靶向视网膜的基因递送系统及其应用

Family Cites Families (36)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US5173414A (en) 1990-10-30 1992-12-22 Applied Immune Sciences, Inc. Production of recombinant adeno-associated virus vectors
PT733103E (pt) 1993-11-09 2004-07-30 Targeted Genetics Corp Criacao de elevados titulos de vectores de aav recombinantes
PT728214E (pt) 1993-11-09 2004-11-30 Ohio Med College Linhas celulares estaveis capazes de expressar o gene de replicacao do virus adeno-associado
US5658785A (en) 1994-06-06 1997-08-19 Children's Hospital, Inc. Adeno-associated virus materials and methods
US5856152A (en) 1994-10-28 1999-01-05 The Trustees Of The University Of Pennsylvania Hybrid adenovirus-AAV vector and methods of use therefor
AU707866B2 (en) 1994-12-06 1999-07-22 Targeted Genetics Corporation Packaging cell lines for generation of high titers of recombinant AAV vectors
FR2737730B1 (fr) 1995-08-10 1997-09-05 Pasteur Merieux Serums Vacc Procede de purification de virus par chromatographie
AU722196B2 (en) 1995-08-30 2000-07-27 Genzyme Corporation Chromatographic purification of adenovirus and AAV
EP1983057A3 (en) 1995-09-08 2009-01-07 Genzyme Corporation Improved AAV vectors for gene therapy
US5910434A (en) 1995-12-15 1999-06-08 Systemix, Inc. Method for obtaining retroviral packaging cell lines producing high transducing efficiency retroviral supernatant
EP0932418B1 (en) 1996-09-06 2007-12-05 The Trustees Of The University Of Pennsylvania Method for recombinant adeno-associated virus-directed gene therapy
US6566118B1 (en) 1997-09-05 2003-05-20 Targeted Genetics Corporation Methods for generating high titer helper-free preparations of released recombinant AAV vectors
JP2001514845A (ja) 1997-09-05 2001-09-18 ターゲティッド ジェネティクス コーポレイション 組換えaavベクターの高力価ヘルパーなし調製物を生成するための方法
US6258595B1 (en) 1999-03-18 2001-07-10 The Trustees Of The University Of Pennsylvania Compositions and methods for helper-free production of recombinant adeno-associated viruses
CA2406743A1 (en) 2000-04-28 2001-11-08 The Trustees Of The University Of Pennsylvania Recombinant aav vectors with aav5 capsids and aav5 vectors pseudotyped in heterologous capsids
US9233131B2 (en) 2003-06-30 2016-01-12 The Regents Of The University Of California Mutant adeno-associated virus virions and methods of use thereof
US9441244B2 (en) 2003-06-30 2016-09-13 The Regents Of The University Of California Mutant adeno-associated virus virions and methods of use thereof
WO2012109214A1 (en) * 2011-02-07 2012-08-16 The University Of North Carolina At Chapel Hill Targeted transduction of aav vectors
DK2675902T3 (da) * 2011-02-17 2019-06-03 Univ Pennsylvania Sammensætninger og fremgangsmåder til at ændre vævsspecificitet og forbedre aav9-medieret genoverførsel
US9434928B2 (en) 2011-11-23 2016-09-06 Nationwide Children's Hospital, Inc. Recombinant adeno-associated virus delivery of alpha-sarcoglycan polynucleotides
DE102012007232B4 (de) 2012-04-07 2014-03-13 Susanne Weller Verfahren zur Herstellung von rotierenden elektrischen Maschinen
AU2013296425B2 (en) * 2012-08-01 2018-06-07 Nationwide Children's Hospital Intrathecal delivery of recombinant adeno-associated virus 9
US9730888B2 (en) * 2013-03-14 2017-08-15 Wayne State University Method of enhancing delivery of therapeutic compounds to the eye
JP2015092462A (ja) 2013-09-30 2015-05-14 Tdk株式会社 正極及びそれを用いたリチウムイオン二次電池
WO2015126972A1 (en) * 2014-02-21 2015-08-27 University Of Florida Research Foundation, Inc. Methods and compositions for gene delivery to on bipolar cells
GB201403260D0 (en) * 2014-02-25 2014-04-09 Univ Manchester Treatment of retinal degeneration using gene therapy
JP6202701B2 (ja) 2014-03-21 2017-09-27 株式会社日立国際電気 基板処理装置、半導体装置の製造方法及びプログラム
IL248102B (en) * 2014-05-02 2022-07-01 Genzyme Corp aav vectors for gene therapy of the central nervous system and retina
JP6197169B2 (ja) 2014-09-29 2017-09-20 東芝メモリ株式会社 半導体装置の製造方法
CN107249646B (zh) * 2014-12-16 2021-06-29 内布拉斯加大学董事会 用于青少年巴滕病的基因疗法
JP6684343B2 (ja) * 2015-05-21 2020-04-22 アンスティチュ ナショナル ドゥ ラ サンテ エ ドゥ ラ ルシェルシュ メディカル ニューロン生存因子の相乗組み合わせ及びその使用
CA2994160C (en) * 2015-07-30 2021-08-10 Massachusetts Eye And Ear Infirmary Ancestral virus sequences and uses thereof
US20180236105A1 (en) * 2015-10-23 2018-08-23 University Of Iowa Research Foundation Methods for treating neurodegenerative diseases using gene therapy to delay disease onset and progression while providing cognitive protection
RU2764919C2 (ru) * 2016-06-13 2022-01-24 Дзе Юниверсити Оф Норт Каролина Эт Чепел Хилл Оптимизированные гены и экспрессионные кассеты cln1, и их применение
JP7048585B2 (ja) * 2016-09-22 2022-04-05 ソルボンヌ・ユニヴェルシテ 網膜変性疾患の処置に使用するための光遺伝学的に形質転換した光受容体前駆細胞
AU2018350990A1 (en) * 2017-10-18 2020-05-21 Regenxbio Inc. Treatment of ocular diseases and metastatic colon cancer with human post-translationally modified VEGF-Trap

Similar Documents

Publication Publication Date Title
JP2022533645A5 (https=)
JP2022533983A5 (https=)
CN305788214S (https=)
CN305792604S (https=)
CN305654299S (https=)
CN305536698S (https=)
CN305536176S (https=)
CN305661871S (https=)
CN305535959S (https=)
CN305535518S (https=)
CN305534442S (https=)
CN305534304S (https=)
CN305534248S (https=)
CN305533594S (https=)
CN305533575S (https=)
CN305531561S (https=)
CN305531182S (https=)
CN305530669S (https=)
CN305528892S (https=)
CN305528852S (https=)
CN305528501S (https=)
CN305773277S (https=)
CN305528414S (https=)
CN305528343S (https=)
CN305528137S (https=)