JP2022521776A5 - - Google Patents

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Publication number
JP2022521776A5
JP2022521776A5 JP2021549782A JP2021549782A JP2022521776A5 JP 2022521776 A5 JP2022521776 A5 JP 2022521776A5 JP 2021549782 A JP2021549782 A JP 2021549782A JP 2021549782 A JP2021549782 A JP 2021549782A JP 2022521776 A5 JP2022521776 A5 JP 2022521776A5
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JP
Japan
Prior art keywords
composition
raav
composition according
cell
sarcoglycan
Prior art date
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Pending
Application number
JP2021549782A
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English (en)
Japanese (ja)
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JP2022521776A (ja
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Priority claimed from PCT/US2020/019892 external-priority patent/WO2020176614A1/en
Publication of JP2022521776A publication Critical patent/JP2022521776A/ja
Publication of JP2022521776A5 publication Critical patent/JP2022521776A5/ja
Priority to JP2024109621A priority Critical patent/JP2024133657A/ja
Priority to JP2025139290A priority patent/JP2025170362A/ja
Pending legal-status Critical Current

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JP2021549782A 2019-02-26 2020-02-26 Β-サルコグリカンのアデノ随伴ウイルスベクター送達および筋ジストロフィーの治療 Pending JP2022521776A (ja)

Priority Applications (2)

Application Number Priority Date Filing Date Title
JP2024109621A JP2024133657A (ja) 2019-02-26 2024-07-08 Β-サルコグリカンのアデノ随伴ウイルスベクター送達および筋ジストロフィーの治療
JP2025139290A JP2025170362A (ja) 2019-02-26 2025-08-22 Β-サルコグリカンのアデノ随伴ウイルスベクター送達および筋ジストロフィーの治療

Applications Claiming Priority (13)

Application Number Priority Date Filing Date Title
US201962810917P 2019-02-26 2019-02-26
US62/810,917 2019-02-26
US201962834012P 2019-04-15 2019-04-15
US62/834,012 2019-04-15
US201962858644P 2019-06-07 2019-06-07
US62/858,644 2019-06-07
US201962881901P 2019-08-01 2019-08-01
US62/881,901 2019-08-01
US201962909564P 2019-10-02 2019-10-02
US62/909,564 2019-10-02
US201962910779P 2019-10-04 2019-10-04
US62/910,779 2019-10-04
PCT/US2020/019892 WO2020176614A1 (en) 2019-02-26 2020-02-26 Adeno-associated virus vector delivery of b-sarcoglycan and the treatment of muscular dystrophy

Related Child Applications (2)

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JP2024109621A Division JP2024133657A (ja) 2019-02-26 2024-07-08 Β-サルコグリカンのアデノ随伴ウイルスベクター送達および筋ジストロフィーの治療
JP2025139290A Division JP2025170362A (ja) 2019-02-26 2025-08-22 Β-サルコグリカンのアデノ随伴ウイルスベクター送達および筋ジストロフィーの治療

Publications (2)

Publication Number Publication Date
JP2022521776A JP2022521776A (ja) 2022-04-12
JP2022521776A5 true JP2022521776A5 (https=) 2023-03-06

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ID=70005777

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Application Number Title Priority Date Filing Date
JP2021549782A Pending JP2022521776A (ja) 2019-02-26 2020-02-26 Β-サルコグリカンのアデノ随伴ウイルスベクター送達および筋ジストロフィーの治療
JP2024109621A Pending JP2024133657A (ja) 2019-02-26 2024-07-08 Β-サルコグリカンのアデノ随伴ウイルスベクター送達および筋ジストロフィーの治療
JP2025139290A Pending JP2025170362A (ja) 2019-02-26 2025-08-22 Β-サルコグリカンのアデノ随伴ウイルスベクター送達および筋ジストロフィーの治療

Family Applications After (2)

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JP2024109621A Pending JP2024133657A (ja) 2019-02-26 2024-07-08 Β-サルコグリカンのアデノ随伴ウイルスベクター送達および筋ジストロフィーの治療
JP2025139290A Pending JP2025170362A (ja) 2019-02-26 2025-08-22 Β-サルコグリカンのアデノ随伴ウイルスベクター送達および筋ジストロフィーの治療

Country Status (16)

Country Link
US (1) US12377170B2 (https=)
EP (1) EP3930765A1 (https=)
JP (3) JP2022521776A (https=)
KR (1) KR20210133242A (https=)
CN (1) CN113766935A (https=)
AU (1) AU2020229340A1 (https=)
BR (1) BR112021016570A2 (https=)
CA (1) CA3131390A1 (https=)
CL (1) CL2021002236A1 (https=)
CO (1) CO2021012074A2 (https=)
IL (1) IL285849A (https=)
MX (1) MX2021010356A (https=)
SG (1) SG11202109113TA (https=)
TW (1) TW202045531A (https=)
WO (1) WO2020176614A1 (https=)
ZA (1) ZA202106017B (https=)

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TWI887479B (zh) 2020-09-08 2025-06-21 美商薩羅塔治療公司 表現γ-肌聚醣之腺相關病毒載體之全身性遞送及肌肉失養症之治療
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TWI889013B (zh) * 2023-11-17 2025-07-01 矽品精密工業股份有限公司 電子封裝件及其製法

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US20230390417A1 (en) 2022-06-02 2023-12-07 Research Institute At Nationwide Children's Hospital Recombinant Adeno-Associated Virus Products and Methods for Treating Limb Girdle Muscular Dystrophy 2A

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