JP2023540095A5 - - Google Patents

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Publication number
JP2023540095A5
JP2023540095A5 JP2023514417A JP2023514417A JP2023540095A5 JP 2023540095 A5 JP2023540095 A5 JP 2023540095A5 JP 2023514417 A JP2023514417 A JP 2023514417A JP 2023514417 A JP2023514417 A JP 2023514417A JP 2023540095 A5 JP2023540095 A5 JP 2023540095A5
Authority
JP
Japan
Application number
JP2023514417A
Other languages
Japanese (ja)
Other versions
JP2023540095A (ja
JPWO2022055791A5 (https=
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/048957 external-priority patent/WO2022055791A1/en
Publication of JP2023540095A publication Critical patent/JP2023540095A/ja
Publication of JP2023540095A5 publication Critical patent/JP2023540095A5/ja
Publication of JPWO2022055791A5 publication Critical patent/JPWO2022055791A5/ja
Pending legal-status Critical Current

Links

JP2023514417A 2020-09-08 2021-09-03 G-サルコグリカンを発現するアデノ随伴ウイルスベクターの全身送達および筋ジストロフィーの治療 Pending JP2023540095A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063075697P 2020-09-08 2020-09-08
US63/075,697 2020-09-08
PCT/US2021/048957 WO2022055791A1 (en) 2020-09-08 2021-09-03 Systemic delivery of adeno-associated virus vector expressing g-sarcoglycan and the treatment of muscular dystrophy

Publications (3)

Publication Number Publication Date
JP2023540095A JP2023540095A (ja) 2023-09-21
JP2023540095A5 true JP2023540095A5 (https=) 2024-09-11
JPWO2022055791A5 JPWO2022055791A5 (https=) 2024-09-11

Family

ID=78086895

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023514417A Pending JP2023540095A (ja) 2020-09-08 2021-09-03 G-サルコグリカンを発現するアデノ随伴ウイルスベクターの全身送達および筋ジストロフィーの治療

Country Status (14)

Country Link
US (2) US11925675B2 (https=)
EP (1) EP4204088A1 (https=)
JP (1) JP2023540095A (https=)
KR (1) KR20230066021A (https=)
CN (1) CN116134047A (https=)
AR (1) AR123445A1 (https=)
AU (1) AU2021340584A1 (https=)
BR (1) BR112023003736A2 (https=)
CA (1) CA3189647A1 (https=)
CO (1) CO2023004031A2 (https=)
IL (1) IL300986A (https=)
MX (1) MX2023002569A (https=)
TW (2) TW202541851A (https=)
WO (1) WO2022055791A1 (https=)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CA3005633C (en) 2015-11-16 2023-11-21 Research Institute Of Nationwide Children's Hospital Materials and methods for treatment of titin-based myopathies and other titinopathies
WO2025171086A1 (en) * 2024-02-07 2025-08-14 Asimov Inc. Promoters and uses thereof

Family Cites Families (24)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US5173414A (en) 1990-10-30 1992-12-22 Applied Immune Sciences, Inc. Production of recombinant adeno-associated virus vectors
PT733103E (pt) 1993-11-09 2004-07-30 Targeted Genetics Corp Criacao de elevados titulos de vectores de aav recombinantes
PT728214E (pt) 1993-11-09 2004-11-30 Ohio Med College Linhas celulares estaveis capazes de expressar o gene de replicacao do virus adeno-associado
US5658785A (en) 1994-06-06 1997-08-19 Children's Hospital, Inc. Adeno-associated virus materials and methods
US5856152A (en) 1994-10-28 1999-01-05 The Trustees Of The University Of Pennsylvania Hybrid adenovirus-AAV vector and methods of use therefor
AU707866B2 (en) 1994-12-06 1999-07-22 Targeted Genetics Corporation Packaging cell lines for generation of high titers of recombinant AAV vectors
FR2737730B1 (fr) 1995-08-10 1997-09-05 Pasteur Merieux Serums Vacc Procede de purification de virus par chromatographie
AU722196B2 (en) 1995-08-30 2000-07-27 Genzyme Corporation Chromatographic purification of adenovirus and AAV
EP1983057A3 (en) 1995-09-08 2009-01-07 Genzyme Corporation Improved AAV vectors for gene therapy
US5910434A (en) 1995-12-15 1999-06-08 Systemix, Inc. Method for obtaining retroviral packaging cell lines producing high transducing efficiency retroviral supernatant
EP0932418B1 (en) 1996-09-06 2007-12-05 The Trustees Of The University Of Pennsylvania Method for recombinant adeno-associated virus-directed gene therapy
JP2001514845A (ja) 1997-09-05 2001-09-18 ターゲティッド ジェネティクス コーポレイション 組換えaavベクターの高力価ヘルパーなし調製物を生成するための方法
US6566118B1 (en) 1997-09-05 2003-05-20 Targeted Genetics Corporation Methods for generating high titer helper-free preparations of released recombinant AAV vectors
US6258595B1 (en) 1999-03-18 2001-07-10 The Trustees Of The University Of Pennsylvania Compositions and methods for helper-free production of recombinant adeno-associated viruses
CA2406743A1 (en) 2000-04-28 2001-11-08 The Trustees Of The University Of Pennsylvania Recombinant aav vectors with aav5 capsids and aav5 vectors pseudotyped in heterologous capsids
AU2002248297A1 (en) 2001-01-05 2002-07-16 Children's Hospital, Inc. Aav2 vectors and methods
DE102012007232B4 (de) 2012-04-07 2014-03-13 Susanne Weller Verfahren zur Herstellung von rotierenden elektrischen Maschinen
JP2015092462A (ja) 2013-09-30 2015-05-14 Tdk株式会社 正極及びそれを用いたリチウムイオン二次電池
JP6202701B2 (ja) 2014-03-21 2017-09-27 株式会社日立国際電気 基板処理装置、半導体装置の製造方法及びプログラム
JP6197169B2 (ja) 2014-09-29 2017-09-20 東芝メモリ株式会社 半導体装置の製造方法
MX2020007876A (es) * 2018-01-31 2020-12-03 Res Inst Nationwide Childrens Hospital Terapia genica para la distrofia muscular de cinturas tipo 2c.
MX2021010356A (es) * 2019-02-26 2022-03-04 Res Inst Nationwide Childrens Hospital SUMINISTRO DE ß-SARCOGLICANO MEDIANTE VECTORES DE VIRUS ADENOASOCIADO Y EL TRATAMIENTO DE LA DISTROFIA MUSCULAR.
JP7847084B2 (ja) * 2019-12-16 2026-04-16 リサーチ インスティチュート アット ネイションワイド チルドレンズ ホスピタル ジストロフィン関連タンパク質複合体(dapc)を回復および維持するための組成物および方法
US20230256117A1 (en) * 2020-06-19 2023-08-17 Genethon Gene therapy expression system allowing an adequate expression in the muscles and in the heart of sgcg

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