JP2023540095A5 - - Google Patents
Info
- Publication number
- JP2023540095A5 JP2023540095A5 JP2023514417A JP2023514417A JP2023540095A5 JP 2023540095 A5 JP2023540095 A5 JP 2023540095A5 JP 2023514417 A JP2023514417 A JP 2023514417A JP 2023514417 A JP2023514417 A JP 2023514417A JP 2023540095 A5 JP2023540095 A5 JP 2023540095A5
- Authority
- JP
- Japan
- Prior art keywords
- composition according
- raav
- plasmid
- seq
- concentration
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202063075697P | 2020-09-08 | 2020-09-08 | |
| US63/075,697 | 2020-09-08 | ||
| PCT/US2021/048957 WO2022055791A1 (en) | 2020-09-08 | 2021-09-03 | Systemic delivery of adeno-associated virus vector expressing g-sarcoglycan and the treatment of muscular dystrophy |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2023540095A JP2023540095A (ja) | 2023-09-21 |
| JP2023540095A5 true JP2023540095A5 (https=) | 2024-09-11 |
Family
ID=78086895
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023514417A Pending JP2023540095A (ja) | 2020-09-08 | 2021-09-03 | Ｇ－サルコグリカンを発現するアデノ随伴ウイルスベクターの全身送達および筋ジストロフィーの治療 |
Country Status (14)
| Country | Link |
|---|---|
| US (2) | US11925675B2 (https=) |
| EP (1) | EP4204088A1 (https=) |
| JP (1) | JP2023540095A (https=) |
| KR (1) | KR20230066021A (https=) |
| CN (1) | CN116134047A (https=) |
| AR (1) | AR123445A1 (https=) |
| AU (1) | AU2021340584A1 (https=) |
| BR (1) | BR112023003736A2 (https=) |
| CA (1) | CA3189647A1 (https=) |
| CO (1) | CO2023004031A2 (https=) |
| IL (1) | IL300986A (https=) |
| MX (1) | MX2023002569A (https=) |
| TW (2) | TWI887479B (https=) |
| WO (1) | WO2022055791A1 (https=) |
Families Citing this family (2)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| KR102877920B1 (ko) | 2015-11-16 | 2025-10-30 | 더 리서치 인스티튜트 앳 네이션와이드 칠드런스 하스피탈 | 티틴-기반 근증 및 다른 티틴성병증의 치료를 위한 물질 및 방법 |
| WO2025171086A1 (en) * | 2024-02-07 | 2025-08-14 | Asimov Inc. | Promoters and uses thereof |
Family Cites Families (24)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US5173414A (en) | 1990-10-30 | 1992-12-22 | Applied Immune Sciences, Inc. | Production of recombinant adeno-associated virus vectors |
| WO1995013365A1 (en) | 1993-11-09 | 1995-05-18 | Targeted Genetics Corporation | Generation of high titers of recombinant aav vectors |
| PT728214E (pt) | 1993-11-09 | 2004-11-30 | Ohio Med College | Linhas celulares estaveis capazes de expressar o gene de replicacao do virus adeno-associado |
| US5658785A (en) | 1994-06-06 | 1997-08-19 | Children's Hospital, Inc. | Adeno-associated virus materials and methods |
| US5856152A (en) | 1994-10-28 | 1999-01-05 | The Trustees Of The University Of Pennsylvania | Hybrid adenovirus-AAV vector and methods of use therefor |
| CA2207927A1 (en) | 1994-12-06 | 1996-06-13 | Targeted Genetics Corporation | Packaging cell lines for generation of high titers of recombinant aav vectors |
| FR2737730B1 (fr) | 1995-08-10 | 1997-09-05 | Pasteur Merieux Serums Vacc | Procede de purification de virus par chromatographie |
| WO1997008298A1 (en) | 1995-08-30 | 1997-03-06 | Genzyme Corporation | Chromatographic purification of adenovirus and aav |
| US6632670B1 (en) | 1995-09-08 | 2003-10-14 | Genzyme Corporation | AAV vectors for gene therapy |
| US5910434A (en) | 1995-12-15 | 1999-06-08 | Systemix, Inc. | Method for obtaining retroviral packaging cell lines producing high transducing efficiency retroviral supernatant |
| JP2001500497A (ja) | 1996-09-06 | 2001-01-16 | トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア | 組換えアデノ随伴ウイルスに指図される遺伝子治療の方法 |
| DK1009808T3 (da) | 1997-09-05 | 2013-01-21 | Genzyme Corp | Fremgangsmåder til generering af hjælper-frie præparater af rekombinante aav-vektorer med høj titer |
| US6566118B1 (en) | 1997-09-05 | 2003-05-20 | Targeted Genetics Corporation | Methods for generating high titer helper-free preparations of released recombinant AAV vectors |
| US6258595B1 (en) | 1999-03-18 | 2001-07-10 | The Trustees Of The University Of Pennsylvania | Compositions and methods for helper-free production of recombinant adeno-associated viruses |
| US7056502B2 (en) | 2000-04-28 | 2006-06-06 | The Trustees Of The University Of Pennsylvania | Recombinant aav vectors with AAV5 capsids and AAV5 vectors pseudotyped in heterologous capsids |
| WO2002053703A2 (en) | 2001-01-05 | 2002-07-11 | Children's Hospital, Inc. | Aav2 vectors and methods |
| DE102012007232B4 (de) | 2012-04-07 | 2014-03-13 | Susanne Weller | Verfahren zur Herstellung von rotierenden elektrischen Maschinen |
| JP2015092462A (ja) | 2013-09-30 | 2015-05-14 | Tdk株式会社 | 正極及びそれを用いたリチウムイオン二次電池 |
| WO2015141521A1 (ja) | 2014-03-21 | 2015-09-24 | 株式会社日立国際電気 | 基板処理装置、半導体装置の製造方法及び記録媒体 |
| JP6197169B2 (ja) | 2014-09-29 | 2017-09-20 | 東芝メモリ株式会社 | 半導体装置の製造方法 |
| AR114350A1 (es) * | 2018-01-31 | 2020-08-26 | Res Institute At Nationwide ChildrenS Hospital | Terapia genética para la distrofia muscular de cinturas del tipo 2c |
| AU2020229340A1 (en) * | 2019-02-26 | 2021-09-16 | Research Institute At Nationwide Children's Hospital | Adeno-associated virus vector delivery of B-sarcoglycan and the treatment of muscular dystrophy |
| WO2021126880A1 (en) * | 2019-12-16 | 2021-06-24 | Research Institute At Nationwide Children's Hospital | Compositions and methods for restoring and maintaining the dystrophin-associated protein complex (dapc) |
| US20230256117A1 (en) * | 2020-06-19 | 2023-08-17 | Genethon | Gene therapy expression system allowing an adequate expression in the muscles and in the heart of sgcg |
-
2021
- 2021-08-30 TW TW110132144A patent/TWI887479B/zh active
- 2021-08-30 TW TW114126376A patent/TW202541851A/zh unknown
- 2021-09-03 JP JP2023514417A patent/JP2023540095A/ja active Pending
- 2021-09-03 CA CA3189647A patent/CA3189647A1/en active Pending
- 2021-09-03 CN CN202180053937.3A patent/CN116134047A/zh active Pending
- 2021-09-03 BR BR112023003736A patent/BR112023003736A2/pt unknown
- 2021-09-03 AU AU2021340584A patent/AU2021340584A1/en active Pending
- 2021-09-03 KR KR1020237011162A patent/KR20230066021A/ko active Pending
- 2021-09-03 IL IL300986A patent/IL300986A/en unknown
- 2021-09-03 MX MX2023002569A patent/MX2023002569A/es unknown
- 2021-09-03 EP EP21790297.2A patent/EP4204088A1/en active Pending
- 2021-09-03 WO PCT/US2021/048957 patent/WO2022055791A1/en not_active Ceased
- 2021-09-07 US US17/468,086 patent/US11925675B2/en active Active
- 2021-09-07 AR ARP210102484A patent/AR123445A1/es unknown
-
2023
- 2023-03-29 CO CONC2023/0004031A patent/CO2023004031A2/es unknown
-
2024
- 2024-02-16 US US18/444,018 patent/US20240374684A1/en active Pending
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