JP2022508835A5 - - Google Patents

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Publication number
JP2022508835A5
JP2022508835A5 JP2021546400A JP2021546400A JP2022508835A5 JP 2022508835 A5 JP2022508835 A5 JP 2022508835A5 JP 2021546400 A JP2021546400 A JP 2021546400A JP 2021546400 A JP2021546400 A JP 2021546400A JP 2022508835 A5 JP2022508835 A5 JP 2022508835A5
Authority
JP
Japan
Prior art keywords
sequence
effector
shmir
complementary
sequence defined
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2021546400A
Other languages
English (en)
Japanese (ja)
Other versions
JP2022508835A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/AU2019/051134 external-priority patent/WO2020077412A1/en
Publication of JP2022508835A publication Critical patent/JP2022508835A/ja
Publication of JP2022508835A5 publication Critical patent/JP2022508835A5/ja
Pending legal-status Critical Current

Links

JP2021546400A 2018-10-17 2019-10-17 眼咽頭筋ジストロフィー（ｏｐｍｄ）を治療するための方法 Pending JP2022508835A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201862747089P 2018-10-17 2018-10-17
US62/747,089 2018-10-17
PCT/AU2019/051134 WO2020077412A1 (en) 2018-10-17 2019-10-17 Methods for treating oculopharyngeal muscular dystrophy (opmd)

Publications (2)

Publication Number Publication Date
JP2022508835A JP2022508835A (ja) 2022-01-19
JP2022508835A5 true JP2022508835A5 (https=) 2022-10-24

Family

ID=70282838

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2021546400A Pending JP2022508835A (ja) 2018-10-17 2019-10-17 眼咽頭筋ジストロフィー（ｏｐｍｄ）を治療するための方法

Country Status (12)

Country Link
US (1) US20220106594A1 (https=)
EP (1) EP3866859A4 (https=)
JP (1) JP2022508835A (https=)
KR (1) KR20210081361A (https=)
CN (1) CN112867511A (https=)
AU (1) AU2019362925A1 (https=)
BR (1) BR112021007256A2 (https=)
CA (1) CA3114945A1 (https=)
IL (1) IL282323A (https=)
MX (1) MX2021004225A (https=)
SG (1) SG11202102185RA (https=)
WO (1) WO2020077412A1 (https=)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN115838725B (zh) * 2022-12-30 2023-09-08 广州派真生物技术有限公司 在哺乳动物心脏中特异性启动基因的启动子序列及其应用

Family Cites Families (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2014117050A2 (en) * 2013-01-26 2014-07-31 Mirimus, Inc. Modified mirna as a scaffold for shrna
NZ747314A (en) * 2016-04-14 2022-07-29 Benitec Ip Holdings Inc Reagents for treatment of oculopharyngeal muscular dystrophy (opmd) and use thereof
JP7233149B2 (ja) * 2016-12-14 2023-03-06 ベニテック アイピー ホールディングス インコーポレーテッド 眼咽頭型筋ジストロフィー（ｏｐｍｄ）を治療するための試薬及びその使用
CN113631706A (zh) * 2019-02-28 2021-11-09 贝尼泰克知识产权控股股份有限公司 用于治疗眼咽肌营养不良(opmd)的组合物和方法

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