JP2024119830A5 - - Google Patents
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- Publication number
- JP2024119830A5 JP2024119830A5 JP2024081593A JP2024081593A JP2024119830A5 JP 2024119830 A5 JP2024119830 A5 JP 2024119830A5 JP 2024081593 A JP2024081593 A JP 2024081593A JP 2024081593 A JP2024081593 A JP 2024081593A JP 2024119830 A5 JP2024119830 A5 JP 2024119830A5
- Authority
- JP
- Japan
- Prior art keywords
- seq
- vector
- shrna
- nucleotide sequence
- composition
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (8)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201862726184P | 2018-08-31 | 2018-08-31 | |
| US62/726,184 | 2018-08-31 | ||
| US201862749622P | 2018-10-23 | 2018-10-23 | |
| US62/749,622 | 2018-10-23 | ||
| US201862754530P | 2018-11-01 | 2018-11-01 | |
| US62/754,530 | 2018-11-01 | ||
| PCT/US2019/049163 WO2020047476A1 (en) | 2018-08-31 | 2019-08-30 | Adeno-associated viral vectors for the treatment of best disease |
| JP2021511541A JP2021534796A (ja) | 2018-08-31 | 2019-08-30 | ベスト病の処置のためのアデノ随伴ウイルスベクター |
Related Parent Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021511541A Division JP2021534796A (ja) | 2018-08-31 | 2019-08-30 | ベスト病の処置のためのアデノ随伴ウイルスベクター |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2025266930A Division JP2026067864A (ja) | 2018-08-31 | 2025-12-19 | ベスト病の処置のためのアデノ随伴ウイルスベクター |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2024119830A JP2024119830A (ja) | 2024-09-03 |
| JP2024119830A5 true JP2024119830A5 (https=) | 2024-12-23 |
Family
ID=69644668
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021511541A Pending JP2021534796A (ja) | 2018-08-31 | 2019-08-30 | ベスト病の処置のためのアデノ随伴ウイルスベクター |
| JP2024081593A Pending JP2024119830A (ja) | 2018-08-31 | 2024-05-20 | ベスト病の処置のためのアデノ随伴ウイルスベクター |
Family Applications Before (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021511541A Pending JP2021534796A (ja) | 2018-08-31 | 2019-08-30 | ベスト病の処置のためのアデノ随伴ウイルスベクター |
Country Status (8)
| Country | Link |
|---|---|
| US (1) | US20220033826A1 (https=) |
| EP (1) | EP3843791A4 (https=) |
| JP (2) | JP2021534796A (https=) |
| CN (2) | CN112839682B (https=) |
| AU (1) | AU2019328577A1 (https=) |
| CA (1) | CA3110563A1 (https=) |
| IL (2) | IL321380A (https=) |
| WO (1) | WO2020047476A1 (https=) |
Families Citing this family (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CA3110563A1 (en) * | 2018-08-31 | 2020-03-05 | University Of Florida Research Foundation, Incorporated | Adeno-associated viral vectors for the treatment of best disease |
| KR20220106742A (ko) * | 2019-09-25 | 2022-07-29 | 유니버시티 오브 유타 리서치 파운데이션 | Vmd2 프로모터로부터 구성적으로 활성인 rap1a의 발현을 위한 방법 및 조성물 |
| US20230112568A1 (en) * | 2020-02-28 | 2023-04-13 | The Trustees Of The University Of Pennsylvania | Treating autosomal recessive bestrophinopathies and methods for evaluating same |
| EP4590841A2 (en) * | 2022-09-20 | 2025-07-30 | Aldevron, LLC | Best1 vectors and uses thereof |
Family Cites Families (17)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| JP2005507398A (ja) * | 2001-10-09 | 2005-03-17 | デヴェロゲン アクチエンゲゼルシャフト フュア エントヴィックルングスビオローギッシェ フォルシュング | エネルギー恒常性の調節に関与するＢｅｓｔｒｏｐｈｉｎおよびＢｅｓｔｒｏｐｈｉｎ相同性タンパク質 |
| EP2305812A3 (en) * | 2002-11-14 | 2012-06-06 | Dharmacon, Inc. | Fuctional and hyperfunctional sirna |
| US20050266552A1 (en) * | 2003-12-05 | 2005-12-01 | Doench John G | Reagents and methods for identification of RNAi pathway genes and chemical modulators of RNAi |
| JP4543188B2 (ja) * | 2004-03-10 | 2010-09-15 | 学校法人日本医科大学 | ヒトチミジル酸合成酵素に対するＲＮＡｉとして作用するＲＮＡ配列 |
| CN101538569B (zh) * | 2008-08-19 | 2011-07-06 | 香港理工大学深圳研究院 | 抑制人dmt1蛋白的rna、重组体及应用 |
| KR101154538B1 (ko) * | 2009-08-24 | 2012-06-13 | 한국과학기술연구원 | 소뇌에서의 ｇａｂａ 방출 조절제 |
| CN102277434B (zh) * | 2011-07-28 | 2015-11-18 | 上海吉凯基因化学技术有限公司 | 人zfx基因的用途及其相关药物 |
| CN102533982B (zh) * | 2011-12-19 | 2016-01-06 | 上海吉凯基因化学技术有限公司 | 人klf8基因在肿瘤治疗中的新用途 |
| JP6283652B2 (ja) * | 2012-03-16 | 2018-02-21 | ザ リージェンツ オブ ザ ユニバーシティ オブ カリフォルニア | 単一のｓｉＲＮＡおよびｓｈＲＮＡナノカプセルに基づいた新規ＲＮＡｉ分子送達プラットホーム |
| AU2013243948A1 (en) * | 2012-04-02 | 2014-10-30 | Moderna Therapeutics, Inc. | Modified polynucleotides for the production of proteins associated with human disease |
| US9546366B2 (en) * | 2013-03-14 | 2017-01-17 | Raadysan Biotech, Inc. | Replication factor C-40 (RFC40/RFC2) as a prognostic marker and target in estrogen positive and negative and triple negative breast cancer |
| EP4674963A3 (en) * | 2013-12-09 | 2026-04-29 | Baylor College of Medicine | Hippo and dystrophin complex signaling in cardiomyocyte renewal |
| GB201322798D0 (en) * | 2013-12-20 | 2014-02-05 | Oxford Biomedica Ltd | Production system |
| WO2016081885A2 (en) * | 2014-11-20 | 2016-05-26 | Massachusetts Eye And Ear Infirmary | Panel-based genetic diagnostic testing for inherited eye diseases |
| CN114533761A (zh) * | 2014-12-30 | 2022-05-27 | 细胞治疗神经科学有限公司 | 治疗视网膜疾病的方法 |
| CN107287238B (zh) * | 2016-04-11 | 2020-10-16 | 厦门继景生物技术有限责任公司 | 一种基因载体及其用于治疗雷柏氏先天性黑矇2型疾病的基因治疗药物 |
| CA3110563A1 (en) * | 2018-08-31 | 2020-03-05 | University Of Florida Research Foundation, Incorporated | Adeno-associated viral vectors for the treatment of best disease |
-
2019
- 2019-08-30 CA CA3110563A patent/CA3110563A1/en active Pending
- 2019-08-30 JP JP2021511541A patent/JP2021534796A/ja active Pending
- 2019-08-30 CN CN201980067514.XA patent/CN112839682B/zh active Active
- 2019-08-30 IL IL321380A patent/IL321380A/en unknown
- 2019-08-30 CN CN202510424401.8A patent/CN120350002A/zh active Pending
- 2019-08-30 WO PCT/US2019/049163 patent/WO2020047476A1/en not_active Ceased
- 2019-08-30 AU AU2019328577A patent/AU2019328577A1/en active Pending
- 2019-08-30 EP EP19854295.3A patent/EP3843791A4/en active Pending
- 2019-08-30 US US17/272,203 patent/US20220033826A1/en active Pending
-
2021
- 2021-02-24 IL IL281083A patent/IL281083A/en unknown
-
2024
- 2024-05-20 JP JP2024081593A patent/JP2024119830A/ja active Pending
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