JP2022502046A5 - - Google Patents

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Publication number
JP2022502046A5
JP2022502046A5 JP2021517037A JP2021517037A JP2022502046A5 JP 2022502046 A5 JP2022502046 A5 JP 2022502046A5 JP 2021517037 A JP2021517037 A JP 2021517037A JP 2021517037 A JP2021517037 A JP 2021517037A JP 2022502046 A5 JP2022502046 A5 JP 2022502046A5
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JP
Japan
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amino acid
seq
aav9
aav capsid
raav
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JP2021517037A
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English (en)
Japanese (ja)
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JP7624724B2 (ja
JPWO2020068990A5 (https=
JP2022502046A (ja
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Priority claimed from PCT/US2019/052969 external-priority patent/WO2020068990A1/en
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Publication of JPWO2020068990A5 publication Critical patent/JPWO2020068990A5/ja
Priority to JP2024134976A priority Critical patent/JP2024161454A/ja
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JP2021517037A 2018-09-26 2019-09-25 標的遺伝子療法のためのアデノ随伴ウイルス組成物 Active JP7624724B2 (ja)

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JP2024134976A JP2024161454A (ja) 2018-09-26 2024-08-13 標的遺伝子療法のためのアデノ随伴ウイルス組成物

Applications Claiming Priority (5)

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US201862736904P 2018-09-26 2018-09-26
US62/736,904 2018-09-26
US201962832812P 2019-04-11 2019-04-11
US62/832,812 2019-04-11
PCT/US2019/052969 WO2020068990A1 (en) 2018-09-26 2019-09-25 Adeno-associated virus compositions for targeted gene therapy

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JP2022502046A JP2022502046A (ja) 2022-01-11
JP2022502046A5 true JP2022502046A5 (https=) 2022-10-03
JPWO2020068990A5 JPWO2020068990A5 (https=) 2022-10-03
JP7624724B2 JP7624724B2 (ja) 2025-01-31

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JP2024134976A Pending JP2024161454A (ja) 2018-09-26 2024-08-13 標的遺伝子療法のためのアデノ随伴ウイルス組成物

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US (3) US11149256B2 (https=)
EP (1) EP3856913A4 (https=)
JP (2) JP7624724B2 (https=)
KR (1) KR20210084459A (https=)
CN (1) CN113966399A (https=)
AU (1) AU2019346447A1 (https=)
CA (1) CA3114199A1 (https=)
SG (1) SG11202103102WA (https=)
WO (1) WO2020068990A1 (https=)

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