JP2021534154A5 - - Google Patents

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Publication number
JP2021534154A5
JP2021534154A5 JP2021507686A JP2021507686A JP2021534154A5 JP 2021534154 A5 JP2021534154 A5 JP 2021534154A5 JP 2021507686 A JP2021507686 A JP 2021507686A JP 2021507686 A JP2021507686 A JP 2021507686A JP 2021534154 A5 JP2021534154 A5 JP 2021534154A5
Authority
JP
Japan
Prior art keywords
aso
administered
combination according
subject
raav
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Withdrawn
Application number
JP2021507686A
Other languages
English (en)
Japanese (ja)
Other versions
JP2021534154A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2019/046720 external-priority patent/WO2020037161A1/en
Publication of JP2021534154A publication Critical patent/JP2021534154A/ja
Publication of JP2021534154A5 publication Critical patent/JP2021534154A5/ja
Priority to JP2024096579A priority Critical patent/JP2024111074A/ja
Priority to JP2025187453A priority patent/JP2026009384A/ja
Withdrawn legal-status Critical Current

Links

JP2021507686A 2018-08-15 2019-08-15 脊髄性筋萎縮症のための併用療法 Withdrawn JP2021534154A (ja)

Priority Applications (2)

Application Number Priority Date Filing Date Title
JP2024096579A JP2024111074A (ja) 2018-08-15 2024-06-14 脊髄性筋萎縮症のための併用療法
JP2025187453A JP2026009384A (ja) 2018-08-15 2025-11-06 脊髄性筋萎縮症のための併用療法

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201862764893P 2018-08-15 2018-08-15
US62/764,893 2018-08-15
US201862783189P 2018-12-20 2018-12-20
US62/783,189 2018-12-20
PCT/US2019/046720 WO2020037161A1 (en) 2018-08-15 2019-08-15 Combination therapy for spinal muscular atrophy

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2024096579A Division JP2024111074A (ja) 2018-08-15 2024-06-14 脊髄性筋萎縮症のための併用療法

Publications (2)

Publication Number Publication Date
JP2021534154A JP2021534154A (ja) 2021-12-09
JP2021534154A5 true JP2021534154A5 (enExample) 2022-08-22

Family

ID=69525927

Family Applications (3)

Application Number Title Priority Date Filing Date
JP2021507686A Withdrawn JP2021534154A (ja) 2018-08-15 2019-08-15 脊髄性筋萎縮症のための併用療法
JP2024096579A Pending JP2024111074A (ja) 2018-08-15 2024-06-14 脊髄性筋萎縮症のための併用療法
JP2025187453A Pending JP2026009384A (ja) 2018-08-15 2025-11-06 脊髄性筋萎縮症のための併用療法

Family Applications After (2)

Application Number Title Priority Date Filing Date
JP2024096579A Pending JP2024111074A (ja) 2018-08-15 2024-06-14 脊髄性筋萎縮症のための併用療法
JP2025187453A Pending JP2026009384A (ja) 2018-08-15 2025-11-06 脊髄性筋萎縮症のための併用療法

Country Status (4)

Country Link
US (1) US20210308281A1 (enExample)
EP (1) EP3837374A4 (enExample)
JP (3) JP2021534154A (enExample)
WO (1) WO2020037161A1 (enExample)

Families Citing this family (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
PT3999643T (pt) * 2019-07-19 2023-12-11 Biogen Ma Inc Métodos de tratamento da atrofia muscular espinhal
EP4013387A4 (en) * 2019-08-15 2023-09-27 Biogen MA Inc. COMBINATION THERAPY FOR SPINAL MUSCLE ATROPHY
WO2022022617A1 (en) * 2020-07-31 2022-02-03 Ractigen Therapeutics Combinatory treatment of sma with sarna and mrna modulators
WO2023168427A1 (en) 2022-03-03 2023-09-07 Yale University Compositions and methods for delivering therapeutic polynucleotides for exon skipping
WO2023240236A1 (en) 2022-06-10 2023-12-14 Voyager Therapeutics, Inc. Compositions and methods for the treatment of spinal muscular atrophy related disorders
IL326390A (en) 2023-08-10 2026-04-01 Univ Pennsylvania Compositions and methods for treating spinal muscular atrophy

Family Cites Families (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
ES2699827T3 (es) * 2009-06-17 2019-02-13 Biogen Ma Inc Composiciones y métodos para la modulación de corte y empalme de SMN2 en un sujeto
MX2018007234A (es) * 2015-12-14 2018-11-09 Univ Pennsylvania Vectores virales adenoasociados utiles en el tratamiento de atrofia muscular espinal.
WO2019094253A1 (en) * 2017-11-08 2019-05-16 Avexis Inc. Means and method for preparing viral vectors and uses of same
EP3801638A1 (en) * 2018-06-08 2021-04-14 Novartis AG Cell-based assay for measuring drug product potency
CN120860258A (zh) * 2018-11-30 2025-10-31 北京诺华制药有限公司 Aav病毒载体及其用途

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