JP2021529519A5 - - Google Patents
Info
- Publication number
- JP2021529519A5 JP2021529519A5 JP2020572414A JP2020572414A JP2021529519A5 JP 2021529519 A5 JP2021529519 A5 JP 2021529519A5 JP 2020572414 A JP2020572414 A JP 2020572414A JP 2020572414 A JP2020572414 A JP 2020572414A JP 2021529519 A5 JP2021529519 A5 JP 2021529519A5
- Authority
- JP
- Japan
- Prior art keywords
- composition according
- composition
- nucleic acid
- single nucleic
- clrn1
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Priority Applications (2)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2023135405A JP2023153320A (ja) | 2018-06-25 | 2023-08-23 | Ｃｌｒｎ１に関連する聴力喪失及び／または視力喪失を治療する方法 |
| JP2025112689A JP2025156349A (ja) | 2018-06-25 | 2025-07-03 | Ｃｌｒｎ１に関連する聴力喪失及び／または視力喪失を治療する方法 |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201862689660P | 2018-06-25 | 2018-06-25 | |
| US62/689,660 | 2018-06-25 | ||
| PCT/US2019/039030 WO2020005974A1 (en) | 2018-06-25 | 2019-06-25 | Methods of treating clrn1-associated hearing loss and/or vision loss |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023135405A Division JP2023153320A (ja) | 2018-06-25 | 2023-08-23 | Ｃｌｒｎ１に関連する聴力喪失及び／または視力喪失を治療する方法 |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2021529519A JP2021529519A (ja) | 2021-11-04 |
| JP2021529519A5 true JP2021529519A5 (enExample) | 2022-06-24 |
Family
ID=68985009
Family Applications (3)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2020572414A Pending JP2021529519A (ja) | 2018-06-25 | 2019-06-25 | Ｃｌｒｎ１に関連する聴力喪失及び／または視力喪失を治療する方法 |
| JP2023135405A Pending JP2023153320A (ja) | 2018-06-25 | 2023-08-23 | Ｃｌｒｎ１に関連する聴力喪失及び／または視力喪失を治療する方法 |
| JP2025112689A Pending JP2025156349A (ja) | 2018-06-25 | 2025-07-03 | Ｃｌｒｎ１に関連する聴力喪失及び／または視力喪失を治療する方法 |
Family Applications After (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023135405A Pending JP2023153320A (ja) | 2018-06-25 | 2023-08-23 | Ｃｌｒｎ１に関連する聴力喪失及び／または視力喪失を治療する方法 |
| JP2025112689A Pending JP2025156349A (ja) | 2018-06-25 | 2025-07-03 | Ｃｌｒｎ１に関連する聴力喪失及び／または視力喪失を治療する方法 |
Country Status (14)
| Country | Link |
|---|---|
| US (1) | US20210277417A1 (enExample) |
| EP (1) | EP3824090A4 (enExample) |
| JP (3) | JP2021529519A (enExample) |
| KR (2) | KR20210057720A (enExample) |
| CN (1) | CN112639107B (enExample) |
| AU (2) | AU2019294603B2 (enExample) |
| BR (1) | BR112020026606A2 (enExample) |
| CA (1) | CA3104330A1 (enExample) |
| CL (1) | CL2020003346A1 (enExample) |
| EA (1) | EA202190114A1 (enExample) |
| IL (1) | IL279551A (enExample) |
| MX (1) | MX2020013628A (enExample) |
| SG (1) | SG11202012710WA (enExample) |
| WO (1) | WO2020005974A1 (enExample) |
Families Citing this family (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US20230340038A1 (en) * | 2020-09-14 | 2023-10-26 | President And Fellows Of Harvard College | Recombinant adeno associated virus (raav) encoding gjb2 and uses thereof |
| CN117157108A (zh) * | 2020-12-29 | 2023-12-01 | 阿库斯股份有限公司 | 用于治疗clrn1相关听力损失和/或视力损失的组合物和方法 |
| JP2024537796A (ja) * | 2021-09-30 | 2024-10-16 | アコーオス インコーポレイテッド | 難聴を治療するための遺伝子療法送達組成物及び方法 |
Family Cites Families (13)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US8980952B2 (en) * | 2002-03-20 | 2015-03-17 | University Of Maryland, Baltimore | Methods for treating brain swelling with a compound that blocks a non-selective cation channel |
| JP2008529498A (ja) * | 2005-02-03 | 2008-08-07 | バイオテック インスティテュート フォー インターナショナル イノベーション，インク． | 糖尿病治療用組成物類および方法 |
| US20100160415A1 (en) * | 2005-10-05 | 2010-06-24 | Bayhill Therapeutics, Inc | Compositions and methods for treatment of autoimmune disease |
| US20090215178A1 (en) * | 2008-02-22 | 2009-08-27 | Zequn Tang | Methods to enhance the stability and homogeneity of transgene expression in clonal cell lines |
| US20130071881A1 (en) * | 2009-11-19 | 2013-03-21 | Immuno Tec Laboratory Co. Ltd | Methods for producing antibody-producing cells that produce desired polypeptides |
| RU2658490C2 (ru) * | 2012-03-27 | 2018-06-21 | Кьюрвак Аг | Искусственные молекулы нуклеиновых кислот для улучшенной экспрессии белков или пептидов |
| CN102978284A (zh) * | 2012-11-19 | 2013-03-20 | 金子兵 | 一种筛查各类眼科遗传性疾病的基因芯片及其制备和使用方法 |
| CN105209619B (zh) * | 2013-03-11 | 2018-10-12 | 泰莱托恩基金会 | miR-204和miR-211及其用途 |
| DK2986635T3 (en) * | 2013-04-18 | 2019-01-28 | Fond Telethon | EFFECTIVE DELIVERY OF BIG GENES THROUGH DUAL-AAV VECTORS |
| WO2016073900A1 (en) * | 2014-11-06 | 2016-05-12 | Case Western Reserve University | Compositions and methods of treating usher syndrome iii |
| WO2016198621A1 (en) * | 2015-06-12 | 2016-12-15 | Glaxosmithkline Biologicals Sa | Adenovirus polynucleotides and polypeptides |
| CA3007476A1 (en) * | 2015-12-11 | 2017-06-15 | Massachusetts Eye And Ear Infirmary | Materials and methods for delivering nucleic acids to cochlear and vestibular cells |
| WO2018039375A1 (en) * | 2016-08-23 | 2018-03-01 | Akouos, Inc. | Compositions and methods for treating non-age-associated hearing impairment in a human subject |
-
2019
- 2019-06-25 BR BR112020026606-0A patent/BR112020026606A2/pt unknown
- 2019-06-25 KR KR1020217002300A patent/KR20210057720A/ko not_active Ceased
- 2019-06-25 EP EP19827048.0A patent/EP3824090A4/en active Pending
- 2019-06-25 AU AU2019294603A patent/AU2019294603B2/en active Active
- 2019-06-25 WO PCT/US2019/039030 patent/WO2020005974A1/en not_active Ceased
- 2019-06-25 KR KR1020267013299A patent/KR20260073466A/ko active Pending
- 2019-06-25 SG SG11202012710WA patent/SG11202012710WA/en unknown
- 2019-06-25 EA EA202190114A patent/EA202190114A1/ru unknown
- 2019-06-25 MX MX2020013628A patent/MX2020013628A/es unknown
- 2019-06-25 JP JP2020572414A patent/JP2021529519A/ja active Pending
- 2019-06-25 CA CA3104330A patent/CA3104330A1/en active Pending
- 2019-06-25 US US17/253,658 patent/US20210277417A1/en active Pending
- 2019-06-25 CN CN201980055197.XA patent/CN112639107B/zh active Active
-
2020
- 2020-12-17 IL IL279551A patent/IL279551A/en unknown
- 2020-12-22 CL CL2020003346A patent/CL2020003346A1/es unknown
-
2023
- 2023-08-23 JP JP2023135405A patent/JP2023153320A/ja active Pending
-
2025
- 2025-07-03 JP JP2025112689A patent/JP2025156349A/ja active Pending
-
2026
- 2026-02-24 AU AU2026201371A patent/AU2026201371A1/en active Pending
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