JP2021529519A5 - - Google Patents
Info
- Publication number
- JP2021529519A5 JP2021529519A5 JP2020572414A JP2020572414A JP2021529519A5 JP 2021529519 A5 JP2021529519 A5 JP 2021529519A5 JP 2020572414 A JP2020572414 A JP 2020572414A JP 2020572414 A JP2020572414 A JP 2020572414A JP 2021529519 A5 JP2021529519 A5 JP 2021529519A5
- Authority
- JP
- Japan
- Prior art keywords
- composition according
- composition
- nucleic acid
- single nucleic
- clrn1
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Priority Applications (2)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2023135405A JP2023153320A (ja) | 2018-06-25 | 2023-08-23 | Ｃｌｒｎ１に関連する聴力喪失及び／または視力喪失を治療する方法 |
| JP2025112689A JP2025156349A (ja) | 2018-06-25 | 2025-07-03 | Ｃｌｒｎ１に関連する聴力喪失及び／または視力喪失を治療する方法 |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201862689660P | 2018-06-25 | 2018-06-25 | |
| US62/689,660 | 2018-06-25 | ||
| PCT/US2019/039030 WO2020005974A1 (en) | 2018-06-25 | 2019-06-25 | Methods of treating clrn1-associated hearing loss and/or vision loss |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023135405A Division JP2023153320A (ja) | 2018-06-25 | 2023-08-23 | Ｃｌｒｎ１に関連する聴力喪失及び／または視力喪失を治療する方法 |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2021529519A JP2021529519A (ja) | 2021-11-04 |
| JP2021529519A5 true JP2021529519A5 (enExample) | 2022-06-24 |
Family
ID=68985009
Family Applications (3)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2020572414A Pending JP2021529519A (ja) | 2018-06-25 | 2019-06-25 | Ｃｌｒｎ１に関連する聴力喪失及び／または視力喪失を治療する方法 |
| JP2023135405A Pending JP2023153320A (ja) | 2018-06-25 | 2023-08-23 | Ｃｌｒｎ１に関連する聴力喪失及び／または視力喪失を治療する方法 |
| JP2025112689A Pending JP2025156349A (ja) | 2018-06-25 | 2025-07-03 | Ｃｌｒｎ１に関連する聴力喪失及び／または視力喪失を治療する方法 |
Family Applications After (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023135405A Pending JP2023153320A (ja) | 2018-06-25 | 2023-08-23 | Ｃｌｒｎ１に関連する聴力喪失及び／または視力喪失を治療する方法 |
| JP2025112689A Pending JP2025156349A (ja) | 2018-06-25 | 2025-07-03 | Ｃｌｒｎ１に関連する聴力喪失及び／または視力喪失を治療する方法 |
Country Status (14)
| Country | Link |
|---|---|
| US (1) | US20210277417A1 (enExample) |
| EP (1) | EP3824090A4 (enExample) |
| JP (3) | JP2021529519A (enExample) |
| KR (1) | KR20210057720A (enExample) |
| CN (1) | CN112639107B (enExample) |
| AU (2) | AU2019294603B2 (enExample) |
| BR (1) | BR112020026606A2 (enExample) |
| CA (1) | CA3104330A1 (enExample) |
| CL (1) | CL2020003346A1 (enExample) |
| EA (1) | EA202190114A1 (enExample) |
| IL (1) | IL279551A (enExample) |
| MX (1) | MX2020013628A (enExample) |
| SG (1) | SG11202012710WA (enExample) |
| WO (1) | WO2020005974A1 (enExample) |
Families Citing this family (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US20230340038A1 (en) * | 2020-09-14 | 2023-10-26 | President And Fellows Of Harvard College | Recombinant adeno associated virus (raav) encoding gjb2 and uses thereof |
| IL304006A (en) * | 2020-12-29 | 2023-08-01 | Akouos Inc | Compositions and methods for treating hearing loss and/or vision loss associated with CLRN1 |
| EP4409009A4 (en) * | 2021-09-30 | 2025-12-17 | Akouos Inc | Compositions for administering gene therapy and methods for treating hearing loss |
Family Cites Families (13)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US8980952B2 (en) * | 2002-03-20 | 2015-03-17 | University Of Maryland, Baltimore | Methods for treating brain swelling with a compound that blocks a non-selective cation channel |
| WO2006084243A2 (en) * | 2005-02-03 | 2006-08-10 | Biotech Institute For International Innovation, Inc. | Compositions and methods for the therapeutic treatment of diabetes |
| CA2624615A1 (en) * | 2005-10-05 | 2007-04-19 | Bayhill Therapeutics, Inc. | Compositions and methods for treatment of autoimmune disease |
| US20090215178A1 (en) * | 2008-02-22 | 2009-08-27 | Zequn Tang | Methods to enhance the stability and homogeneity of transgene expression in clonal cell lines |
| JP2013511258A (ja) * | 2009-11-19 | 2013-04-04 | 株式会社免疫工学研究所 | 所望のポリペプチドを産生する抗体産生細胞の製造方法 |
| MX362981B (es) * | 2012-03-27 | 2019-02-28 | Curevac Ag | Moleculas artificiales de acido nucleico para la expresion mejorada de proteina o peptido. |
| CN102978284A (zh) * | 2012-11-19 | 2013-03-20 | 金子兵 | 一种筛查各类眼科遗传性疾病的基因芯片及其制备和使用方法 |
| EP2970972B1 (en) * | 2013-03-11 | 2018-08-15 | Fondazione Telethon | Mir-204 and mir-211 and uses thereof |
| AU2014255665B2 (en) * | 2013-04-18 | 2018-08-02 | Fondazione Telethon | Effective delivery of large genes by dual AAV vectors |
| US11827680B2 (en) * | 2014-11-06 | 2023-11-28 | Case Western Reserve University | Compounds and methods of treating usher syndrome III |
| BR112017026523A2 (pt) * | 2015-06-12 | 2018-08-14 | Glaxosmithkline Biologicals Sa | vetor recombinante, adenovírus recombinante, composição, uso de um vetor recombinante, de um adenovírus recombinante ou de uma composição, método para induzir uma resposta imune em um indivíduo, e, polinucleotídeo isolado. |
| SG10201913266UA (en) * | 2015-12-11 | 2020-02-27 | Massachusetts Eye & Ear Infirmary | Materials and methods for delivering nucleic acids to cochlear and vestibular cells |
| EP3510161A4 (en) * | 2016-08-23 | 2020-04-22 | Akouos, Inc. | COMPOSITIONS AND METHODS FOR TREATING PERSONAL HEARING LOSS IN A PERSON |
-
2019
- 2019-06-25 US US17/253,658 patent/US20210277417A1/en active Pending
- 2019-06-25 KR KR1020217002300A patent/KR20210057720A/ko not_active Ceased
- 2019-06-25 WO PCT/US2019/039030 patent/WO2020005974A1/en not_active Ceased
- 2019-06-25 EP EP19827048.0A patent/EP3824090A4/en active Pending
- 2019-06-25 CA CA3104330A patent/CA3104330A1/en active Pending
- 2019-06-25 AU AU2019294603A patent/AU2019294603B2/en active Active
- 2019-06-25 SG SG11202012710WA patent/SG11202012710WA/en unknown
- 2019-06-25 BR BR112020026606-0A patent/BR112020026606A2/pt unknown
- 2019-06-25 MX MX2020013628A patent/MX2020013628A/es unknown
- 2019-06-25 CN CN201980055197.XA patent/CN112639107B/zh active Active
- 2019-06-25 JP JP2020572414A patent/JP2021529519A/ja active Pending
- 2019-06-25 EA EA202190114A patent/EA202190114A1/ru unknown
-
2020
- 2020-12-17 IL IL279551A patent/IL279551A/en unknown
- 2020-12-22 CL CL2020003346A patent/CL2020003346A1/es unknown
-
2023
- 2023-08-23 JP JP2023135405A patent/JP2023153320A/ja active Pending
-
2025
- 2025-07-03 JP JP2025112689A patent/JP2025156349A/ja active Pending
-
2026
- 2026-02-24 AU AU2026201371A patent/AU2026201371A1/en active Pending
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