JP2021503934A5 - - Google Patents

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Publication number
JP2021503934A5
JP2021503934A5 JP2020529489A JP2020529489A JP2021503934A5 JP 2021503934 A5 JP2021503934 A5 JP 2021503934A5 JP 2020529489 A JP2020529489 A JP 2020529489A JP 2020529489 A JP2020529489 A JP 2020529489A JP 2021503934 A5 JP2021503934 A5 JP 2021503934A5
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JP
Japan
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nucleic acid
acid sequence
acid molecule
isolated nucleic
seq
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Ceased
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JP2020529489A
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English (en)
Japanese (ja)
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JP2021503934A (ja
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Priority claimed from PCT/EP2018/082880 external-priority patent/WO2019106035A1/en
Publication of JP2021503934A publication Critical patent/JP2021503934A/ja
Publication of JP2021503934A5 publication Critical patent/JP2021503934A5/ja
Ceased legal-status Critical Current

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JP2020529489A 2017-11-30 2018-11-28 網膜色素上皮中の遺伝子の特異的発現のためのプロモーターSynPIII Ceased JP2021503934A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
EP17204750.8 2017-11-30
EP17204750 2017-11-30
PCT/EP2018/082880 WO2019106035A1 (en) 2017-11-30 2018-11-28 Synpiii, a promoter for the specific expression of genes in retinal pigment epithelium

Publications (2)

Publication Number Publication Date
JP2021503934A JP2021503934A (ja) 2021-02-15
JP2021503934A5 true JP2021503934A5 (https=) 2022-01-06

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ID=60543416

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JP2020529489A Ceased JP2021503934A (ja) 2017-11-30 2018-11-28 網膜色素上皮中の遺伝子の特異的発現のためのプロモーターSynPIII

Country Status (15)

Country Link
US (1) US11591615B2 (https=)
EP (1) EP3717651A1 (https=)
JP (1) JP2021503934A (https=)
KR (1) KR20200091432A (https=)
CN (1) CN111542611A (https=)
AU (1) AU2018376259A1 (https=)
BR (1) BR112020010928A2 (https=)
CA (1) CA3083682A1 (https=)
CR (1) CR20200236A (https=)
IL (1) IL274957A (https=)
MX (1) MX2020005649A (https=)
PH (1) PH12020550748A1 (https=)
RU (1) RU2020121408A (https=)
SG (1) SG11202005024QA (https=)
WO (1) WO2019106035A1 (https=)

Families Citing this family (14)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
MX2010011467A (es) 2008-04-18 2011-02-15 Novartis Forschungsstiftung Novedosas herramientas y metodos terapeuticos para tratar la ceguera.
US10941417B2 (en) 2015-04-30 2021-03-09 Friedrich Miescher Institute For Biomedical Research Promoter for the specific expression of genes in Müller cells
US10857241B2 (en) 2015-09-15 2020-12-08 Friedrich Miescher Institute For Biomedical Research Therapeutical tools and methods for treating blindness by targeting photoreceptors
WO2017064642A1 (en) 2015-10-14 2017-04-20 Fredrich Miescher Institute For Biomedical Research Promoter for the specific expression of genes in retinal endothelial cells
EP3383440B1 (en) 2015-12-03 2021-06-30 Friedrich Miescher Institute for Biomedical Research Synp162, a promoter for the specific expression of genes in rod photoreceptors
EP3383439B1 (en) 2015-12-03 2019-09-25 Friedrich Miescher Institute for Biomedical Research Synp161, a promoter for the specific expression of genes in rod photoreceptors
WO2017093934A1 (en) 2015-12-03 2017-06-08 Friedrich Miescher Institute For Biomedical Research Synp160, a promoter for the specific expression of genes in rod photoreceptors
ES2909444T3 (es) 2015-12-03 2022-05-06 Friedrich Miescher Institute For Biomedical Res Synp159, un promotor para la expresión específica de genes en los fotorreceptores de los bastones
RU2766353C2 (ru) 2016-11-02 2022-03-15 Фридрих Мишер Инститьют Фор Байомедикал Рисерч Synp198, промотор для специфической экспрессии генов в ганглионарных клетках сетчатки, избирательных в отношении направления
WO2018146588A1 (en) 2017-02-08 2018-08-16 Friedrich Miescher Institute For Biomedical Research Synp88, a promoter for the specific expression of genes in retinal ganglion cells
MX2020005033A (es) 2017-11-15 2020-10-28 Friedrich Miescher Institute For Biomedical Res Promotor especifico de las celulas del epitelio pigmentario retinal en primates.
SG11202005024QA (en) 2017-11-30 2020-06-29 Friedrich Miescher Institute For Biomedical Res Synpiii, a promoter for the specific expression of genes in retinal pigment epithelium
WO2024110770A1 (en) * 2022-11-22 2024-05-30 INSERM (Institut National de la Santé et de la Recherche Médicale) A new promoter for retinal pigment epithelium (rpe) targeted gene therapy
AU2024260900A1 (en) * 2023-04-27 2025-11-13 Korea Research Institute Of Bioscience And Biotechnology Promoter for gene expression in retinal cells, and vector system comprising same

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Publication number Priority date Publication date Assignee Title
GB9206874D0 (en) 1992-03-30 1992-05-13 Connaught Lab Generation of improved inducible mammalian expression vectors
CA2346262A1 (en) * 1998-09-17 2000-03-23 University Of Florida Methods for treatment of degenerative retinal diseases
CN101484005A (zh) 2006-05-04 2009-07-15 韦恩州立大学 通过向体内递送视紫红质核酸恢复视觉响应
EP1891976A1 (en) 2006-08-23 2008-02-27 Novartis Forschungsstiftung, Zweigniederlassung Friedrich Miescher Institute for Biomedical Research Use of light sensitive genes
WO2009112448A1 (en) 2008-03-11 2009-09-17 Novartis Forschungsstiftung, Zweigniederlassung Novel tool for the analysis of neural circuits
MX2010011467A (es) 2008-04-18 2011-02-15 Novartis Forschungsstiftung Novedosas herramientas y metodos terapeuticos para tratar la ceguera.
CN103608455B (zh) 2011-01-07 2019-01-15 应用遗传科技公司 用于治疗色盲和其它疾病的启动子、表达盒、载体、药盒和方法
WO2014033095A1 (en) * 2012-08-27 2014-03-06 Friedrich Miescher Institute For Biomedical Research Retinal off circuit-specific promoter
EP3104895A1 (en) 2014-02-10 2016-12-21 Friedrich Miescher Institute for Biomedical Research Aii retinal amacrine cell-specific promoter
EP3105334B1 (en) 2014-02-11 2019-07-03 Friedrich Miescher Institute for Biomedical Research Müller cell-specific promoter
GB201502137D0 (en) * 2015-02-09 2015-03-25 Ucl Business Plc Treatment
US10941417B2 (en) 2015-04-30 2021-03-09 Friedrich Miescher Institute For Biomedical Research Promoter for the specific expression of genes in Müller cells
US10857241B2 (en) 2015-09-15 2020-12-08 Friedrich Miescher Institute For Biomedical Research Therapeutical tools and methods for treating blindness by targeting photoreceptors
WO2017064642A1 (en) 2015-10-14 2017-04-20 Fredrich Miescher Institute For Biomedical Research Promoter for the specific expression of genes in retinal endothelial cells
EP3383440B1 (en) 2015-12-03 2021-06-30 Friedrich Miescher Institute for Biomedical Research Synp162, a promoter for the specific expression of genes in rod photoreceptors
ES2909444T3 (es) 2015-12-03 2022-05-06 Friedrich Miescher Institute For Biomedical Res Synp159, un promotor para la expresión específica de genes en los fotorreceptores de los bastones
EP3383439B1 (en) 2015-12-03 2019-09-25 Friedrich Miescher Institute for Biomedical Research Synp161, a promoter for the specific expression of genes in rod photoreceptors
WO2017093934A1 (en) 2015-12-03 2017-06-08 Friedrich Miescher Institute For Biomedical Research Synp160, a promoter for the specific expression of genes in rod photoreceptors
WO2017093566A1 (en) * 2015-12-04 2017-06-08 Universite Pierre Et Marie Curie (Paris 6) Promoters and uses thereof
US20190209708A1 (en) 2016-05-17 2019-07-11 Friedrich Miescher Institute For Biomedical Research Novel therapeutic tools and methods for treating blindness
RU2766353C2 (ru) 2016-11-02 2022-03-15 Фридрих Мишер Инститьют Фор Байомедикал Рисерч Synp198, промотор для специфической экспрессии генов в ганглионарных клетках сетчатки, избирательных в отношении направления
EP3548093A1 (en) 2016-12-01 2019-10-09 Friedrich Miescher Institute for Biomedical Research Synp107, a promoter for the specific expression of genes in interneurons
US20190376083A1 (en) 2016-12-01 2019-12-12 Friedrich Miescher Institute For Biomedical Research Synp1, a promoter for the specific expression of genes in interneurons
WO2018146588A1 (en) 2017-02-08 2018-08-16 Friedrich Miescher Institute For Biomedical Research Synp88, a promoter for the specific expression of genes in retinal ganglion cells
MX2020005033A (es) 2017-11-15 2020-10-28 Friedrich Miescher Institute For Biomedical Res Promotor especifico de las celulas del epitelio pigmentario retinal en primates.
SG11202005024QA (en) 2017-11-30 2020-06-29 Friedrich Miescher Institute For Biomedical Res Synpiii, a promoter for the specific expression of genes in retinal pigment epithelium
CN111527102A (zh) 2017-11-30 2020-08-11 弗里德里克·米谢尔生物医学研究所 灵长类动物视网膜色素上皮细胞特异性启动子SynP61
EP3870240A1 (en) 2018-10-25 2021-09-01 Friedrich Miescher Institute for Biomedical Research Synp78 (proa27), a promoter for the specific expression of genes in retinal ganglion cells
US20210353773A1 (en) 2018-10-25 2021-11-18 Friedrich Miescher Institute For Biomedical Research Synp194 (prob15), a promoter for the specific expression of genes in retinal ganglion cells
EP3870239A1 (en) 2018-10-25 2021-09-01 Friedrich Miescher Institute for Biomedical Research Synp57 (proa14), a promoter for the specific expression of genes in photoreceptors
EP3870709A1 (en) 2018-10-25 2021-09-01 Friedrich Miescher Institute for Biomedical Research Synp27 (prob12), a promoter for the specific expression of genes in protoplasmic astrocytes
JP2022505517A (ja) 2018-10-25 2022-01-14 フリードリッヒ ミーシェー インスティトゥート フォー バイオメディカル リサーチ 網膜神経節細胞中の遺伝子の特異的発現のためのプロモーターSynP151(ProC29)
WO2020084537A1 (en) 2018-10-25 2020-04-30 Friedrich Miescher Institute For Biomedical Research Synp17 (prob1), a promoter for the specific expression of genes in retinal ganglion cells
US20220119807A1 (en) 2019-01-24 2022-04-21 Friedrich Miescher Institute For Biomedical Research Synp35 (proc8), a promoter for the specific expression of genes in retinal ganglion cells
US20220119841A1 (en) 2019-01-24 2022-04-21 Friedrich Miescher Instit for Biomedical Research Synp5 (proa9), a promoter for the specific expression of genes in retinal ganglion cells
WO2020152626A1 (en) 2019-01-24 2020-07-30 Friedrich Miescher Institute For Biomedical Research Synp166 (proa36), a promoter for the specific expression of genes in photoreceptors
EP3914300A1 (en) 2019-01-24 2021-12-01 Friedrich Miescher Institute for Biomedical Research Synp66 (proa21), a promoter for the specific expression of genes in retinal ganglion cells
SG11202108044YA (en) 2019-02-25 2021-09-29 Novartis Ag Compositions and methods to treat bietti crystalline dystrophy
US20220154211A1 (en) 2019-02-25 2022-05-19 Novartis Ag Compositions and methods to treat bietti crystalline dystrophy

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