JP2021503933A5 - - Google Patents

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Publication number
JP2021503933A5
JP2021503933A5 JP2020529473A JP2020529473A JP2021503933A5 JP 2021503933 A5 JP2021503933 A5 JP 2021503933A5 JP 2020529473 A JP2020529473 A JP 2020529473A JP 2020529473 A JP2020529473 A JP 2020529473A JP 2021503933 A5 JP2021503933 A5 JP 2021503933A5
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JP
Japan
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nucleic acid
isolated nucleic
acid molecule
acid sequence
pharmaceutical composition
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JP2020529473A
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English (en)
Japanese (ja)
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JP2021503933A (ja
JP7390290B2 (ja
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Priority claimed from PCT/EP2018/082872 external-priority patent/WO2019106027A1/en
Publication of JP2021503933A publication Critical patent/JP2021503933A/ja
Publication of JP2021503933A5 publication Critical patent/JP2021503933A5/ja
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Publication of JP7390290B2 publication Critical patent/JP7390290B2/ja
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JP2020529473A 2017-11-30 2018-11-28 霊長類網膜色素上皮細胞特異的プロモーターSynP61 Active JP7390290B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
EP17204746.6 2017-11-30
EP17204746 2017-11-30
PCT/EP2018/082872 WO2019106027A1 (en) 2017-11-30 2018-11-28 SynP61, A PRIMATE RETINAL PIGMENT EPITHELIUM CELL-SPECIFIC PROMOTER

Publications (3)

Publication Number Publication Date
JP2021503933A JP2021503933A (ja) 2021-02-15
JP2021503933A5 true JP2021503933A5 (https=) 2022-01-06
JP7390290B2 JP7390290B2 (ja) 2023-12-01

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ID=60543414

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2020529473A Active JP7390290B2 (ja) 2017-11-30 2018-11-28 霊長類網膜色素上皮細胞特異的プロモーターSynP61

Country Status (15)

Country Link
US (1) US20230193314A1 (https=)
EP (1) EP3717509A1 (https=)
JP (1) JP7390290B2 (https=)
KR (1) KR20200091435A (https=)
CN (1) CN111527102A (https=)
AU (1) AU2018376544B2 (https=)
BR (1) BR112020010775A2 (https=)
CA (1) CA3083404A1 (https=)
CR (1) CR20200235A (https=)
IL (1) IL274885A (https=)
MX (1) MX2020005648A (https=)
PH (1) PH12020550766A1 (https=)
RU (1) RU2020121390A (https=)
SG (1) SG11202005002QA (https=)
WO (1) WO2019106027A1 (https=)

Families Citing this family (13)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
MX2010011467A (es) 2008-04-18 2011-02-15 Novartis Forschungsstiftung Novedosas herramientas y metodos terapeuticos para tratar la ceguera.
US10941417B2 (en) 2015-04-30 2021-03-09 Friedrich Miescher Institute For Biomedical Research Promoter for the specific expression of genes in Müller cells
US10857241B2 (en) 2015-09-15 2020-12-08 Friedrich Miescher Institute For Biomedical Research Therapeutical tools and methods for treating blindness by targeting photoreceptors
WO2017064642A1 (en) 2015-10-14 2017-04-20 Fredrich Miescher Institute For Biomedical Research Promoter for the specific expression of genes in retinal endothelial cells
EP3383440B1 (en) 2015-12-03 2021-06-30 Friedrich Miescher Institute for Biomedical Research Synp162, a promoter for the specific expression of genes in rod photoreceptors
EP3383439B1 (en) 2015-12-03 2019-09-25 Friedrich Miescher Institute for Biomedical Research Synp161, a promoter for the specific expression of genes in rod photoreceptors
ES2909444T3 (es) 2015-12-03 2022-05-06 Friedrich Miescher Institute For Biomedical Res Synp159, un promotor para la expresión específica de genes en los fotorreceptores de los bastones
WO2017093934A1 (en) 2015-12-03 2017-06-08 Friedrich Miescher Institute For Biomedical Research Synp160, a promoter for the specific expression of genes in rod photoreceptors
RU2766353C2 (ru) 2016-11-02 2022-03-15 Фридрих Мишер Инститьют Фор Байомедикал Рисерч Synp198, промотор для специфической экспрессии генов в ганглионарных клетках сетчатки, избирательных в отношении направления
WO2018146588A1 (en) 2017-02-08 2018-08-16 Friedrich Miescher Institute For Biomedical Research Synp88, a promoter for the specific expression of genes in retinal ganglion cells
MX2020005033A (es) 2017-11-15 2020-10-28 Friedrich Miescher Institute For Biomedical Res Promotor especifico de las celulas del epitelio pigmentario retinal en primates.
SG11202005024QA (en) 2017-11-30 2020-06-29 Friedrich Miescher Institute For Biomedical Res Synpiii, a promoter for the specific expression of genes in retinal pigment epithelium
US20220154211A1 (en) * 2019-02-25 2022-05-19 Novartis Ag Compositions and methods to treat bietti crystalline dystrophy

Family Cites Families (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US7309487B2 (en) * 2004-02-09 2007-12-18 George Inana Methods and compositions for detecting and treating retinal diseases
EP3105334B1 (en) * 2014-02-11 2019-07-03 Friedrich Miescher Institute for Biomedical Research Müller cell-specific promoter
MX2020005033A (es) * 2017-11-15 2020-10-28 Friedrich Miescher Institute For Biomedical Res Promotor especifico de las celulas del epitelio pigmentario retinal en primates.

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