JP2021503933A5 - - Google Patents

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Publication number
JP2021503933A5
JP2021503933A5 JP2020529473A JP2020529473A JP2021503933A5 JP 2021503933 A5 JP2021503933 A5 JP 2021503933A5 JP 2020529473 A JP2020529473 A JP 2020529473A JP 2020529473 A JP2020529473 A JP 2020529473A JP 2021503933 A5 JP2021503933 A5 JP 2021503933A5
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JP
Japan
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nucleic acid
isolated nucleic
acid molecule
acid sequence
pharmaceutical composition
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JP2020529473A
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English (en)
Japanese (ja)
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JP2021503933A (ja
JP7390290B2 (ja
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Priority claimed from PCT/EP2018/082872 external-priority patent/WO2019106027A1/en
Publication of JP2021503933A publication Critical patent/JP2021503933A/ja
Publication of JP2021503933A5 publication Critical patent/JP2021503933A5/ja
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JP2020529473A 2017-11-30 2018-11-28 霊長類網膜色素上皮細胞特異的プロモーターSynP61 Active JP7390290B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
EP17204746 2017-11-30
EP17204746.6 2017-11-30
PCT/EP2018/082872 WO2019106027A1 (en) 2017-11-30 2018-11-28 SynP61, A PRIMATE RETINAL PIGMENT EPITHELIUM CELL-SPECIFIC PROMOTER

Publications (3)

Publication Number Publication Date
JP2021503933A JP2021503933A (ja) 2021-02-15
JP2021503933A5 true JP2021503933A5 (https=) 2022-01-06
JP7390290B2 JP7390290B2 (ja) 2023-12-01

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ID=60543414

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Application Number Title Priority Date Filing Date
JP2020529473A Active JP7390290B2 (ja) 2017-11-30 2018-11-28 霊長類網膜色素上皮細胞特異的プロモーターSynP61

Country Status (15)

Country Link
US (1) US20230193314A1 (https=)
EP (1) EP3717509A1 (https=)
JP (1) JP7390290B2 (https=)
KR (1) KR20200091435A (https=)
CN (1) CN111527102A (https=)
AU (1) AU2018376544B2 (https=)
BR (1) BR112020010775A2 (https=)
CA (1) CA3083404A1 (https=)
CR (1) CR20200235A (https=)
IL (1) IL274885A (https=)
MX (1) MX2020005648A (https=)
PH (1) PH12020550766A1 (https=)
RU (1) RU2020121390A (https=)
SG (1) SG11202005002QA (https=)
WO (1) WO2019106027A1 (https=)

Families Citing this family (13)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
JP2011516091A (ja) 2008-04-18 2011-05-26 ノバルティス・フォルシュングスシュティフトゥング・ツヴァイクニーダーラッスング・フリードリッヒ・ミーシェー・インスティトゥート・フォー・バイオメディカル・リサーチ 失明の治療のための新規な治療用ツールおよび方法
ES2747433T3 (es) 2015-04-30 2020-03-10 Friedrich Miescher Institute For Biomedical Res Promotor para la expresión específica de genes en células de Müller
WO2017046084A1 (en) 2015-09-15 2017-03-23 Friedrich Miescher Institute For Biomedical Research Novel therapeutical tools and methods for treating blindness by targeting photoreceptors
EP3362101B1 (en) 2015-10-14 2021-05-19 Friedrich Miescher Institute for Biomedical Research Promoter for the specific expression of genes in retinal endothelial cells
US10995344B2 (en) 2015-12-03 2021-05-04 Friedrich Miescher Institute For Biomedical Research SYNP159, a promoter for the specific expression of genes in rod photoreceptors
BR112018011059A2 (pt) 2015-12-03 2018-11-21 Friedrich Miescher Institute For Biomedical Research synp161, um promotor para a expressão específica de genes em fotoreceptores de haste
JP7075341B2 (ja) 2015-12-03 2022-05-25 フリードリッヒ ミーシェー インスティトゥート フォー バイオメディカル リサーチ SynP162、桿体光受容器における遺伝子の特異的発現のためのプロモーター
WO2017093934A1 (en) 2015-12-03 2017-06-08 Friedrich Miescher Institute For Biomedical Research Synp160, a promoter for the specific expression of genes in rod photoreceptors
CA3042197A1 (en) 2016-11-02 2018-05-11 Friedrich Miescher Institute For Biomedical Research Synp198, a promoter for the specific expression of genes in direction selective retinal ganglion cells
JP7112414B2 (ja) 2017-02-08 2022-08-03 フリードリッヒ ミーシェー インスティトゥート フォー バイオメディカル リサーチ 網膜神経節細胞中の遺伝子の特異的発現のためのプロモーターsynp88
CN111726985B (zh) 2017-11-15 2022-06-10 弗里德里克·米谢尔生物医学研究所 灵长类动物视网膜色素上皮细胞特异性启动子
JP2021503934A (ja) 2017-11-30 2021-02-15 フリードリッヒ ミーシェー インスティトゥート フォー バイオメディカル リサーチ 網膜色素上皮中の遺伝子の特異的発現のためのプロモーターSynPIII
JP2022520875A (ja) * 2019-02-25 2022-04-01 ノバルティス アーゲー Biettiクリスタリン網膜症を治療するための組成物及び方法

Family Cites Families (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US7309487B2 (en) * 2004-02-09 2007-12-18 George Inana Methods and compositions for detecting and treating retinal diseases
WO2015121793A1 (en) * 2014-02-11 2015-08-20 Friedrich Miescher Institute For Biomedical Research Müller cell-specific promoter
CN111726985B (zh) * 2017-11-15 2022-06-10 弗里德里克·米谢尔生物医学研究所 灵长类动物视网膜色素上皮细胞特异性启动子

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