JP2020527329A5 - - Google Patents

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Publication number
JP2020527329A5
JP2020527329A5 JP2019567349A JP2019567349A JP2020527329A5 JP 2020527329 A5 JP2020527329 A5 JP 2020527329A5 JP 2019567349 A JP2019567349 A JP 2019567349A JP 2019567349 A JP2019567349 A JP 2019567349A JP 2020527329 A5 JP2020527329 A5 JP 2020527329A5
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JP
Japan
Prior art keywords
b4galt1
nucleic acid
seq
sequence
pharmaceutical composition
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JP2019567349A
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English (en)
Japanese (ja)
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JP7661009B2 (ja
JP2020527329A (ja
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Priority claimed from PCT/US2018/035806 external-priority patent/WO2018226560A1/en
Publication of JP2020527329A publication Critical patent/JP2020527329A/ja
Publication of JP2020527329A5 publication Critical patent/JP2020527329A5/ja
Priority to JP2023078115A priority Critical patent/JP2023113657A/ja
Application granted granted Critical
Publication of JP7661009B2 publication Critical patent/JP7661009B2/ja
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JP2019567349A 2017-06-05 2018-06-04 B4galt1バリアント及びその使用 Active JP7661009B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2023078115A JP2023113657A (ja) 2017-06-05 2023-05-10 B4galt1バリアント及びその使用

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US201762515140P 2017-06-05 2017-06-05
US62/515,140 2017-06-05
US201762550161P 2017-08-25 2017-08-25
US62/550,161 2017-08-25
US201862659344P 2018-04-18 2018-04-18
US62/659,344 2018-04-18
PCT/US2018/035806 WO2018226560A1 (en) 2017-06-05 2018-06-04 B4galt1 variants and uses thereof

Related Child Applications (1)

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JP2023078115A Division JP2023113657A (ja) 2017-06-05 2023-05-10 B4galt1バリアント及びその使用

Publications (3)

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JP2020527329A JP2020527329A (ja) 2020-09-10
JP2020527329A5 true JP2020527329A5 (cg-RX-API-DMAC7.html) 2021-07-26
JP7661009B2 JP7661009B2 (ja) 2025-04-14

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JP2019567349A Active JP7661009B2 (ja) 2017-06-05 2018-06-04 B4galt1バリアント及びその使用
JP2023078115A Pending JP2023113657A (ja) 2017-06-05 2023-05-10 B4galt1バリアント及びその使用

Family Applications After (1)

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JP2023078115A Pending JP2023113657A (ja) 2017-06-05 2023-05-10 B4galt1バリアント及びその使用

Country Status (14)

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US (2) US10738284B2 (cg-RX-API-DMAC7.html)
EP (1) EP3635102B1 (cg-RX-API-DMAC7.html)
JP (2) JP7661009B2 (cg-RX-API-DMAC7.html)
KR (1) KR102624979B1 (cg-RX-API-DMAC7.html)
CN (1) CN110997906B (cg-RX-API-DMAC7.html)
AU (1) AU2018282072B2 (cg-RX-API-DMAC7.html)
CA (1) CA3065938A1 (cg-RX-API-DMAC7.html)
DK (1) DK3635102T3 (cg-RX-API-DMAC7.html)
ES (1) ES3049196T3 (cg-RX-API-DMAC7.html)
FI (1) FI3635102T3 (cg-RX-API-DMAC7.html)
IL (1) IL271073B2 (cg-RX-API-DMAC7.html)
MX (1) MX2019014661A (cg-RX-API-DMAC7.html)
SG (1) SG11201911597YA (cg-RX-API-DMAC7.html)
WO (1) WO2018226560A1 (cg-RX-API-DMAC7.html)

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CA3065938A1 (en) 2017-06-05 2018-12-13 Regeneron Pharmaceuticals, Inc. B4galt1 variants and uses thereof
JP2023516052A (ja) * 2020-03-04 2023-04-17 リジェネロン・ファーマシューティカルズ・インコーポレイテッド B4galt1媒介性機能の齧歯類モデル
CN120225673A (zh) 2022-06-01 2025-06-27 e-生物有限公司 表达和/或功能抑制剂
WO2024121373A1 (en) * 2022-12-09 2024-06-13 Proqr Therapeutics Ii B.V. Antisense oligonucleotides for the treatment of cardiovascular disease
CN115960926A (zh) * 2022-12-30 2023-04-14 南方科技大学 一种mRNA及含有mRNA的药物
EP4562159A1 (en) * 2023-07-27 2025-06-04 e-therapeutics PLC Inhibitors of expression and/or function

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