JP2020517268A5 - - Google Patents
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- JP2020517268A5 JP2020517268A5 JP2019557373A JP2019557373A JP2020517268A5 JP 2020517268 A5 JP2020517268 A5 JP 2020517268A5 JP 2019557373 A JP2019557373 A JP 2019557373A JP 2019557373 A JP2019557373 A JP 2019557373A JP 2020517268 A5 JP2020517268 A5 JP 2020517268A5
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- JP
- Japan
- Prior art keywords
- cell
- seq
- cells
- promoter
- subject
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
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Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2024063151A JP7696039B2 (ja) | 2017-04-21 | 2024-04-10 | Ｘｌａ遺伝子療法用の最適化されたレンチウイルスベクター |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201762488523P | 2017-04-21 | 2017-04-21 | |
| US62/488,523 | 2017-04-21 | ||
| PCT/US2018/028331 WO2018195297A1 (en) | 2017-04-21 | 2018-04-19 | Optimized lentiviral vector for xla gene therapy |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024063151A Division JP7696039B2 (ja) | 2017-04-21 | 2024-04-10 | Ｘｌａ遺伝子療法用の最適化されたレンチウイルスベクター |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2020517268A JP2020517268A (ja) | 2020-06-18 |
| JP2020517268A5 true JP2020517268A5 (https=) | 2021-06-10 |
| JP7471821B2 JP7471821B2 (ja) | 2024-04-22 |
Family
ID=63856377
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2019557373A Active JP7471821B2 (ja) | 2017-04-21 | 2018-04-19 | Ｘｌａ遺伝子療法用の最適化されたレンチウイルスベクター |
| JP2024063151A Active JP7696039B2 (ja) | 2017-04-21 | 2024-04-10 | Ｘｌａ遺伝子療法用の最適化されたレンチウイルスベクター |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024063151A Active JP7696039B2 (ja) | 2017-04-21 | 2024-04-10 | Ｘｌａ遺伝子療法用の最適化されたレンチウイルスベクター |
Country Status (6)
| Country | Link |
|---|---|
| US (1) | US20200325458A1 (https=) |
| EP (1) | EP3612238A4 (https=) |
| JP (2) | JP7471821B2 (https=) |
| CN (1) | CN110809627A (https=) |
| AU (1) | AU2018256412B2 (https=) |
| WO (1) | WO2018195297A1 (https=) |
Families Citing this family (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US20230158110A1 (en) | 2018-05-30 | 2023-05-25 | The Regents Of The University Of California | Gene editing of monogenic disorders in human hematopoietic stem cells -- correction of x-linked hyper-igm syndrome (xhim) |
| JP7470119B2 (ja) | 2018-08-24 | 2024-04-17 | シーエスエル ベーリング ジーン セラピー インコーポレイテッド | 無血清培地におけるベクター産生 |
| US11464872B2 (en) * | 2020-12-07 | 2022-10-11 | Noga Therapeutics Ltd. | Lentiviral vectors for therapeutic expression of BTK in haematopoietic cells |
| WO2025215591A1 (en) | 2024-04-12 | 2025-10-16 | Csl Behring L.L.C. | Modified vectors for xla gene therapy |
Family Cites Families (2)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US6974667B2 (en) * | 2000-06-14 | 2005-12-13 | Gene Logic, Inc. | Gene expression profiles in liver cancer |
| US20160004814A1 (en) * | 2012-09-05 | 2016-01-07 | University Of Washington Through Its Center For Commercialization | Methods and compositions related to regulation of nucleic acids |
-
2018
- 2018-04-19 US US16/605,740 patent/US20200325458A1/en active Pending
- 2018-04-19 JP JP2019557373A patent/JP7471821B2/ja active Active
- 2018-04-19 CN CN201880043435.0A patent/CN110809627A/zh active Pending
- 2018-04-19 AU AU2018256412A patent/AU2018256412B2/en active Active
- 2018-04-19 WO PCT/US2018/028331 patent/WO2018195297A1/en not_active Ceased
- 2018-04-19 EP EP18788504.1A patent/EP3612238A4/en active Pending
-
2024
- 2024-04-10 JP JP2024063151A patent/JP7696039B2/ja active Active
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