JP2020505317A5 - - Google Patents
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- JP2020505317A5 JP2020505317A5 JP2019522742A JP2019522742A JP2020505317A5 JP 2020505317 A5 JP2020505317 A5 JP 2020505317A5 JP 2019522742 A JP2019522742 A JP 2019522742A JP 2019522742 A JP2019522742 A JP 2019522742A JP 2020505317 A5 JP2020505317 A5 JP 2020505317A5
- Authority
- JP
- Japan
- Prior art keywords
- subject
- nucleic acid
- acid molecule
- administering
- combination according
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
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Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2023016007A JP2023041950A (ja) | 2017-01-20 | 2023-02-06 | 臍帯血移植（ｕｃｂｔ）および増加したガラクトセレブロシダーゼの発現によるクラッベ病の処置 |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201762448433P | 2017-01-20 | 2017-01-20 | |
| US62/448,433 | 2017-01-20 | ||
| PCT/US2018/014370 WO2018136710A1 (en) | 2017-01-20 | 2018-01-19 | Treatment of krabbe disease with umbilical cord blood transplantion (ucbt) and increased galactocerebrosidase (galc) expression |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023016007A Division JP2023041950A (ja) | 2017-01-20 | 2023-02-06 | 臍帯血移植（ｕｃｂｔ）および増加したガラクトセレブロシダーゼの発現によるクラッベ病の処置 |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2020505317A JP2020505317A (ja) | 2020-02-20 |
| JP2020505317A5 true JP2020505317A5 (https=) | 2021-02-25 |
Family
ID=62908818
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2019522742A Withdrawn JP2020505317A (ja) | 2017-01-20 | 2018-01-19 | 臍帯血移植（ｕｃｂｔ）および増加したガラクトセレブロシダーゼの発現によるクラッベ病の処置 |
| JP2023016007A Pending JP2023041950A (ja) | 2017-01-20 | 2023-02-06 | 臍帯血移植（ｕｃｂｔ）および増加したガラクトセレブロシダーゼの発現によるクラッベ病の処置 |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023016007A Pending JP2023041950A (ja) | 2017-01-20 | 2023-02-06 | 臍帯血移植（ｕｃｂｔ）および増加したガラクトセレブロシダーゼの発現によるクラッベ病の処置 |
Country Status (9)
| Country | Link |
|---|---|
| US (1) | US12599636B2 (https=) |
| EP (1) | EP3571298B1 (https=) |
| JP (2) | JP2020505317A (https=) |
| KR (1) | KR20190106990A (https=) |
| CN (2) | CN118078860A (https=) |
| AU (1) | AU2018210326B9 (https=) |
| CA (1) | CA3042467A1 (https=) |
| IL (1) | IL266287A (https=) |
| WO (1) | WO2018136710A1 (https=) |
Families Citing this family (5)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2020132385A1 (en) * | 2018-12-21 | 2020-06-25 | The University Of North Carolina At Chapel Hill | Optimized galc genes and expression cassettes and their use |
| EP3931337A1 (en) * | 2019-02-26 | 2022-01-05 | The Trustees of The University of Pennsylvania | Compositions useful in treatment of krabbe disease |
| CA3132379A1 (en) * | 2019-03-22 | 2020-10-01 | Rush University Medical Center | Combination of nasal gene delivery and oral cinnamic acid, oleamide or gemfibrozil for lysosomal storage disorders |
| CA3177924A1 (en) * | 2020-05-12 | 2021-11-18 | The Trustees Of The University Of Pennsylvania | Compositions useful in treatment of krabbe disease |
| US20230210911A1 (en) * | 2020-06-26 | 2023-07-06 | University Of Pittsburgh- Of The Commonwealth System Of Higher Education | Methods and materials for treating non-malignant disorders or diseases with cord blood |
Family Cites Families (5)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US4458066A (en) | 1980-02-29 | 1984-07-03 | University Patents, Inc. | Process for preparing polynucleotides |
| US6730297B1 (en) | 1999-05-28 | 2004-05-04 | Chiron Corporation | Use of recombinant gene delivery vectors for treating or preventing lysosomal storage disorders |
| MX359371B (es) | 2001-11-13 | 2018-09-25 | Univ Pennsylvania | Un metodo para detectar y/o identificar secuencias del virus adeno-asociado y aislamiento de secuencias novedosas identificadas de ese modo. |
| WO2004042033A2 (en) | 2002-11-01 | 2004-05-21 | The Board Of Trustees Of The Leland Stanford Junior University | Circulating stem cells and uses related thereto |
| US9986722B2 (en) * | 2012-08-07 | 2018-06-05 | Chiesi Farmaceutici S.P.A. | Animal model of Krabbe's disease |
-
2018
- 2018-01-19 CN CN202410102735.9A patent/CN118078860A/zh active Pending
- 2018-01-19 JP JP2019522742A patent/JP2020505317A/ja not_active Withdrawn
- 2018-01-19 KR KR1020197012608A patent/KR20190106990A/ko not_active Ceased
- 2018-01-19 WO PCT/US2018/014370 patent/WO2018136710A1/en not_active Ceased
- 2018-01-19 CN CN201880004477.3A patent/CN110168085A/zh active Pending
- 2018-01-19 AU AU2018210326A patent/AU2018210326B9/en active Active
- 2018-01-19 US US16/349,514 patent/US12599636B2/en active Active
- 2018-01-19 EP EP18741529.4A patent/EP3571298B1/en active Active
- 2018-01-19 CA CA3042467A patent/CA3042467A1/en active Pending
-
2019
- 2019-04-28 IL IL266287A patent/IL266287A/en unknown
-
2023
- 2023-02-06 JP JP2023016007A patent/JP2023041950A/ja active Pending
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