JP2019536782A - ＣＲＩＳＰＲ／Ｃｐｆ１媒介性遺伝子編集による筋ジストロフィーの予防 - Google Patents

ＣＲＩＳＰＲ／Ｃｐｆ１媒介性遺伝子編集による筋ジストロフィーの予防 Download PDF

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JP2019536782A
JP2019536782A JP2019528478A JP2019528478A JP2019536782A JP 2019536782 A JP2019536782 A JP 2019536782A JP 2019528478 A JP2019528478 A JP 2019528478A JP 2019528478 A JP2019528478 A JP 2019528478A JP 2019536782 A JP2019536782 A JP 2019536782A
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composition
promoter
sequence
vector
muscle
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JP2019536782A5 (enExample
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ユ チャン
ユ チャン
チェンツ ロン
チェンツ ロン
ロンダ バセル−デュビー
ロンダ バセル−デュビー
エリック オルソン
エリック オルソン
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University of Texas System
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JP2019528478A 2016-11-28 2017-11-28 ＣＲＩＳＰＲ／Ｃｐｆ１媒介性遺伝子編集による筋ジストロフィーの予防 Pending JP2019536782A (ja)

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Application Number Priority Date Filing Date Title
US201662426853P 2016-11-28 2016-11-28
US62/426,853 2016-11-28
PCT/US2017/063468 WO2018098480A1 (en) 2016-11-28 2017-11-28 Prevention of muscular dystrophy by crispr/cpf1-mediated gene editing

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JP2019536782A true JP2019536782A (ja) 2019-12-19
JP2019536782A5 JP2019536782A5 (enExample) 2021-01-14

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US (1) US20200046854A1 (enExample)
EP (1) EP3545090A1 (enExample)
JP (1) JP2019536782A (enExample)
CN (1) CN110382695A (enExample)
AU (1) AU2017364106A1 (enExample)
CA (1) CA3044531A1 (enExample)
MX (1) MX2019006157A (enExample)
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