AU2017364106A1 - Prevention of muscular dystrophy by CRISPR/Cpfl-mediated gene editing - Google Patents

Prevention of muscular dystrophy by CRISPR/Cpfl-mediated gene editing Download PDF

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AU2017364106A1
AU2017364106A1 AU2017364106A AU2017364106A AU2017364106A1 AU 2017364106 A1 AU2017364106 A1 AU 2017364106A1 AU 2017364106 A AU2017364106 A AU 2017364106A AU 2017364106 A AU2017364106 A AU 2017364106A AU 2017364106 A1 AU2017364106 A1 AU 2017364106A1
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exon
composition
human
promoter
sequence
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Rhonda Bassel-Duby
Chengzu LONG
Eric Olson
Yu Zhang
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University of Texas System
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University of Texas System
University of Texas at Austin
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    • C07K14/435Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof from animals; from humans
    • C07K14/46Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof from animals; from humans from vertebrates
    • C07K14/47Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof from animals; from humans from vertebrates from mammals
    • C07K14/4701Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof from animals; from humans from vertebrates from mammals not used
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AU2017364106A 2016-11-28 2017-11-28 Prevention of muscular dystrophy by CRISPR/Cpfl-mediated gene editing Abandoned AU2017364106A1 (en)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201662426853P 2016-11-28 2016-11-28
US62/426,853 2016-11-28
PCT/US2017/063468 WO2018098480A1 (en) 2016-11-28 2017-11-28 Prevention of muscular dystrophy by crispr/cpf1-mediated gene editing

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AU2017364106A1 true AU2017364106A1 (en) 2019-06-20

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US (1) US20200046854A1 (enExample)
EP (1) EP3545090A1 (enExample)
JP (1) JP2019536782A (enExample)
CN (1) CN110382695A (enExample)
AU (1) AU2017364106A1 (enExample)
CA (1) CA3044531A1 (enExample)
MX (1) MX2019006157A (enExample)
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