JP2019529385A5 - - Google Patents
Download PDFInfo
- Publication number
- JP2019529385A5 JP2019529385A5 JP2019512292A JP2019512292A JP2019529385A5 JP 2019529385 A5 JP2019529385 A5 JP 2019529385A5 JP 2019512292 A JP2019512292 A JP 2019512292A JP 2019512292 A JP2019512292 A JP 2019512292A JP 2019529385 A5 JP2019529385 A5 JP 2019529385A5
- Authority
- JP
- Japan
- Prior art keywords
- use according
- mammal
- cells
- cns
- therapeutic protein
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2022002163A JP2022050574A (ja) | 2016-09-02 | 2022-01-11 | Ｃｎｓ障害を治療するための方法及びベクター |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201662383274P | 2016-09-02 | 2016-09-02 | |
| US62/383,274 | 2016-09-02 | ||
| PCT/US2017/049959 WO2018045347A1 (en) | 2016-09-02 | 2017-09-01 | Methods and vectors for treating cns disorders |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022002163A Division JP2022050574A (ja) | 2016-09-02 | 2022-01-11 | Ｃｎｓ障害を治療するための方法及びベクター |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2019529385A JP2019529385A (ja) | 2019-10-17 |
| JP2019529385A5 true JP2019529385A5 (enExample) | 2020-09-17 |
| JP7610923B2 JP7610923B2 (ja) | 2025-01-09 |
Family
ID=61309371
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2019512292A Active JP7610923B2 (ja) | 2016-09-02 | 2017-09-01 | Ｃｎｓ障害を治療するための方法及びベクター |
| JP2022002163A Pending JP2022050574A (ja) | 2016-09-02 | 2022-01-11 | Ｃｎｓ障害を治療するための方法及びベクター |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022002163A Pending JP2022050574A (ja) | 2016-09-02 | 2022-01-11 | Ｃｎｓ障害を治療するための方法及びベクター |
Country Status (9)
| Country | Link |
|---|---|
| US (1) | US20190192693A1 (enExample) |
| EP (1) | EP3506930A4 (enExample) |
| JP (2) | JP7610923B2 (enExample) |
| CN (1) | CN110121356A (enExample) |
| AU (2) | AU2017318717B2 (enExample) |
| BR (1) | BR112019004353A2 (enExample) |
| CA (1) | CA3035628A1 (enExample) |
| MX (1) | MX2019002518A (enExample) |
| WO (1) | WO2018045347A1 (enExample) |
Families Citing this family (12)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| GB201508026D0 (en) | 2015-05-11 | 2015-06-24 | Ucl Business Plc | Capsid |
| EP3655001A4 (en) * | 2017-07-17 | 2021-04-28 | Spark Therapeutics, Inc. | Apheresis methods and uses |
| US12275948B2 (en) | 2018-06-28 | 2025-04-15 | The University Of North Carolina At Chapel Hill | Optimized CLN5 genes and expression cassettes and their use |
| CN113966399A (zh) | 2018-09-26 | 2022-01-21 | 加州理工学院 | 用于靶向基因疗法的腺相关病毒组合物 |
| SG11202104295UA (en) * | 2018-11-14 | 2021-06-29 | Regenxbio Inc | Gene therapy for neuronal ceroid lipofuscinoses |
| WO2020112802A1 (en) * | 2018-11-28 | 2020-06-04 | Prevail Therapeutics, Inc. | Gene therapies for neurodegenerative disease |
| BR112021015817A2 (pt) | 2019-02-22 | 2021-10-13 | The Trustees Of The University Of Pennsylvania | Vírus adeno-associado recombinante para tratamento de neurodegeneração com início na idade adulta associado a grn |
| US20220348638A1 (en) * | 2019-09-24 | 2022-11-03 | The J. David Gladstone Institutes, a testamentary trust estabilished under the Will of J. David Glad | Method of targeting neuronal apoe to treat a neurocognitive disorder |
| EP4045653A1 (en) * | 2019-10-16 | 2022-08-24 | Cornell University | Gene therapy for alzheimer's disease |
| US20230384310A1 (en) * | 2020-10-01 | 2023-11-30 | Sangamo Therapeutics, Inc. | Methods of detecting anti-aav antibodies |
| CN112852881B (zh) * | 2021-02-09 | 2023-08-15 | 南京贝思奥生物科技有限公司 | 利用细胞穿膜肽增强腺相关病毒在中枢神经系统转导效率的方法 |
| TW202426479A (zh) * | 2022-10-10 | 2024-07-01 | 美商星火治療公司 | Apoe基因療法 |
Family Cites Families (6)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US7135339B2 (en) * | 2003-11-20 | 2006-11-14 | University Of Iowa Research Foundation | Methods for producing and using in vivo pseudotyped retroviruses using envelope glycoproteins from lymphocytic choriomeningitis virus (LCMV) |
| EP2634253B1 (en) | 2010-10-27 | 2016-05-11 | Jichi Medical University | Adeno-associated virus virions for transferring genes into neural cells |
| CA2873890C (en) * | 2012-05-18 | 2022-12-06 | University Of Iowa Research Foundation | Methods and compositions for treating amyloid deposits |
| BR112016001592A2 (pt) * | 2013-07-26 | 2017-11-28 | Univ Iowa Res Found | métodos e composições para o tratamento de doenças cerebrais |
| ES2874704T3 (es) | 2013-11-20 | 2021-11-05 | Univ Iowa Res Found | Procedimiento para monitorizar la eficacia de un tratamiento de la enfermedad de Alzheimer con una isoforma de ApoE |
| CN108347932B (zh) * | 2015-02-20 | 2022-09-13 | 衣阿华大学研究基金会 | 用于治疗遗传性眼病的方法和组合物 |
-
2017
- 2017-09-01 JP JP2019512292A patent/JP7610923B2/ja active Active
- 2017-09-01 CA CA3035628A patent/CA3035628A1/en active Pending
- 2017-09-01 MX MX2019002518A patent/MX2019002518A/es unknown
- 2017-09-01 CN CN201780067677.9A patent/CN110121356A/zh active Pending
- 2017-09-01 US US16/329,697 patent/US20190192693A1/en not_active Abandoned
- 2017-09-01 BR BR112019004353A patent/BR112019004353A2/pt unknown
- 2017-09-01 WO PCT/US2017/049959 patent/WO2018045347A1/en not_active Ceased
- 2017-09-01 EP EP17847658.6A patent/EP3506930A4/en active Pending
- 2017-09-01 AU AU2017318717A patent/AU2017318717B2/en active Active
-
2022
- 2022-01-11 JP JP2022002163A patent/JP2022050574A/ja active Pending
-
2024
- 2024-10-06 AU AU2024227138A patent/AU2024227138A1/en not_active Abandoned
Similar Documents
| Publication | Publication Date | Title |
|---|---|---|
| JP2019529385A5 (enExample) | ||
| ES2897508T3 (es) | Variantes de virus adenoasociados y métodos de uso de las mismas | |
| JP2020527333A5 (enExample) | ||
| ES2903127T3 (es) | Terapia génica para trastornos neurodegenerativos | |
| JP2016503405A5 (enExample) | ||
| RU2018116076A (ru) | Модифицированные гены атаксии фридрейха и векторы для генной терапии | |
| HRP20192141T1 (hr) | Genska terapija za retinitis pigmentosa | |
| JP2017509632A5 (enExample) | ||
| RU2017125234A (ru) | Конструкции нуклеиновой кислоты и векторы для генотерапии для применения для лечения болезни вильсона и других состояний | |
| JP2017529395A5 (enExample) | ||
| JP2020519629A5 (enExample) | ||
| JP7616668B2 (ja) | Ｕｂｅ３ａ遺伝子および発現カセットならびにそれらの使用 | |
| JPWO2020106916A5 (enExample) | ||
| CA3158518A1 (en) | Triple function adeno-associated virus (aav)vectors for the treatment of c9orf72 associated diseases | |
| JP2020509786A5 (enExample) | ||
| IL292264B1 (en) | Aav transfer cassette | |
| JPWO2019152609A5 (enExample) | ||
| CN114144518A (zh) | 用于基因疗法的双亮氨酸拉链激酶抑制剂 | |
| JPWO2021053222A5 (enExample) | ||
| HRP20220199T1 (hr) | Postupak genetskog liječenja korištenjem virusa aav-xbp1s/gfp i njegova uporaba u prevenciji i liječenju amiotrofične lateralne skleroze | |
| JPWO2021076911A5 (enExample) | ||
| US12516301B2 (en) | Optimized SUMF1 genes and expression cassettes and their use | |
| US20250269066A1 (en) | Gene therapy | |
| US12480098B1 (en) | Adeno-associated virus variant | |
| KR102874560B1 (ko) | 아데노연관바이러스 변이체 |