JP2018538261A5 - - Google Patents
Download PDFInfo
- Publication number
- JP2018538261A5 JP2018538261A5 JP2018524411A JP2018524411A JP2018538261A5 JP 2018538261 A5 JP2018538261 A5 JP 2018538261A5 JP 2018524411 A JP2018524411 A JP 2018524411A JP 2018524411 A JP2018524411 A JP 2018524411A JP 2018538261 A5 JP2018538261 A5 JP 2018538261A5
- Authority
- JP
- Japan
- Prior art keywords
- composition
- item
- subject
- seq
- recombinant aav
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2021086103A JP7307121B2 (ja) | 2015-11-12 | 2021-05-21 | 筋ジストロフィーの治療方法 |
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201562254539P | 2015-11-12 | 2015-11-12 | |
| US62/254,539 | 2015-11-12 | ||
| US201662419793P | 2016-11-09 | 2016-11-09 | |
| US62/419,793 | 2016-11-09 | ||
| PCT/US2016/061703 WO2017083776A1 (en) | 2015-11-12 | 2016-11-11 | Methods of treating muscular dystrophy |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021086103A Division JP7307121B2 (ja) | 2015-11-12 | 2021-05-21 | 筋ジストロフィーの治療方法 |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2018538261A JP2018538261A (ja) | 2018-12-27 |
| JP2018538261A5 true JP2018538261A5 (enExample) | 2019-12-19 |
| JP6889717B2 JP6889717B2 (ja) | 2021-06-18 |
Family
ID=58696162
Family Applications (3)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2018524411A Active JP6889717B2 (ja) | 2015-11-12 | 2016-11-11 | 筋ジストロフィーの治療方法 |
| JP2021086103A Active JP7307121B2 (ja) | 2015-11-12 | 2021-05-21 | 筋ジストロフィーの治療方法 |
| JP2023076538A Withdrawn JP2023099184A (ja) | 2015-11-12 | 2023-05-08 | 筋ジストロフィーの治療方法 |
Family Applications After (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021086103A Active JP7307121B2 (ja) | 2015-11-12 | 2021-05-21 | 筋ジストロフィーの治療方法 |
| JP2023076538A Withdrawn JP2023099184A (ja) | 2015-11-12 | 2023-05-08 | 筋ジストロフィーの治療方法 |
Country Status (20)
| Country | Link |
|---|---|
| US (2) | US11820972B2 (enExample) |
| EP (1) | EP3373980B1 (enExample) |
| JP (3) | JP6889717B2 (enExample) |
| KR (1) | KR102821290B1 (enExample) |
| CN (1) | CN108883200B (enExample) |
| AU (3) | AU2016354561B2 (enExample) |
| CA (1) | CA3005240A1 (enExample) |
| CO (1) | CO2018005928A2 (enExample) |
| DK (1) | DK3373980T3 (enExample) |
| EA (1) | EA201891134A1 (enExample) |
| ES (1) | ES3034857T3 (enExample) |
| FI (1) | FI3373980T3 (enExample) |
| HR (1) | HRP20250923T1 (enExample) |
| IL (1) | IL259178B (enExample) |
| MX (1) | MX2018005882A (enExample) |
| RU (1) | RU2761264C2 (enExample) |
| SG (1) | SG11201803971UA (enExample) |
| TN (2) | TN2018000163A1 (enExample) |
| WO (1) | WO2017083776A1 (enExample) |
| ZA (1) | ZA201803080B (enExample) |
Families Citing this family (8)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| MA47800A (fr) | 2017-03-17 | 2020-01-22 | Univ Newcastle | Délivrance par vecteur viral adéno-associé d'un fragment de micro-dystrophine pour traiter la dystrophie musculaire |
| JP7511469B2 (ja) | 2017-09-27 | 2024-07-05 | イノザイム ファーマ， インコーポレイテッド | 組換えエクトヌクレオチドピロホスファターゼ／ホスホジエステラーゼ（ｎｐｐ１）を使用して心血管機能を改善し、心血管疾患を処置するための方法。 |
| IL321310A (en) | 2017-10-20 | 2025-08-01 | Res Inst Nationwide Childrens Hospital | Methods and materials for NT-3 gene therapy |
| BR112020025995A2 (pt) | 2018-06-18 | 2021-03-23 | Research Institute At Nationwide Children's Hospital | administração de microdistrofina músculo-específica por vetor de vírus adeno-associado para tratar a distrofia muscular |
| AU2019419494B2 (en) * | 2018-12-31 | 2026-03-26 | Research Institute At Nationwide Children's Hospital | DUX4 RNA silencing using RNA targeting CRISPR-Cas13b |
| BR112022025586A2 (pt) | 2020-06-15 | 2023-03-07 | Res Inst Nationwide Childrens Hospital | Liberação de vetor de vírus adenoassociado para distrofias musculares |
| KR102732922B1 (ko) * | 2021-10-29 | 2024-11-20 | 충남대학교 산학협력단 | 과산화수소수 처리에 의해 유용성분 함량이 증진된 상추의 재배방법 |
| CN117223686B (zh) * | 2023-11-15 | 2024-01-23 | 四川省农业机械科学研究院 | 一种扩座除砂一体化蚕盘及养蚕方法 |
Family Cites Families (19)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| ATE78293T1 (de) | 1983-05-27 | 1992-08-15 | Texas A & M Univ Sys | Verfahren zur herstellung eines rekombinanten baculovirus-expressionsvektors. |
| DK518384A (da) | 1984-01-31 | 1985-07-01 | Idaho Res Found | Vektor til fremstilling af et gen-produkt i insektceller, fremgangsmaade til dens fremstilling samt dens anvendelse |
| US6204059B1 (en) | 1994-06-30 | 2001-03-20 | University Of Pittsburgh | AAV capsid vehicles for molecular transfer |
| WO2002053703A2 (en) | 2001-01-05 | 2002-07-11 | Children's Hospital, Inc. | Aav2 vectors and methods |
| WO2003074714A1 (en) | 2002-03-05 | 2003-09-12 | Stichting Voor De Technische Wetenschappen | Baculovirus expression system |
| JP2006121961A (ja) * | 2004-10-28 | 2006-05-18 | Univ Of Tokushima | 顎骨骨幹異形成症ｇｄｄの原因遺伝子ｇｄｄ１とその用途 |
| US20100120627A1 (en) * | 2006-08-02 | 2010-05-13 | Abdelmajid Belouchi | Genemap of the human genes associated with psoriasis |
| FR2919305B1 (fr) * | 2007-07-26 | 2009-09-18 | Genethon Ass Loi De 1901 | Vecteurs viraux adeno-associes pour l'expression de la dysferline. |
| GB0715087D0 (en) | 2007-08-03 | 2007-09-12 | Summit Corp Plc | Drug combinations for the treatment of duchenne muscular dystrophy |
| US20100026655A1 (en) | 2008-07-31 | 2010-02-04 | Avago Technologies Ecbu Ip (Singapore) Pte. Ltd. | Capacitive Touchscreen or Touchpad for Finger or Stylus |
| US8536618B2 (en) | 2009-11-03 | 2013-09-17 | The Regents Of The University Of California | Light emitting diode structure utilizing zinc oxide nanorod arrays on one or more surfaces, and a low cost method of producing such zinc oxide nanorod arrays |
| WO2011044138A1 (en) | 2009-10-05 | 2011-04-14 | Catabasis Pharmaceuticals, Inc. | Lipoic acid acylated salicylate derivatives and their uses |
| WO2013078316A1 (en) * | 2011-11-23 | 2013-05-30 | Nationwide Children's Hospital, Inc. | Recombinant adeno-associated virus delivery of alpha-sarcoglycan polynucleotides |
| WO2013151663A1 (en) | 2012-04-02 | 2013-10-10 | modeRNA Therapeutics | Modified polynucleotides for the production of membrane proteins |
| WO2014037526A1 (en) * | 2012-09-07 | 2014-03-13 | INSERM (Institut National de la Santé et de la Recherche Médicale) | In vitro genetic diagnostic of inherited neuromuscular disorders |
| US9624282B2 (en) | 2012-11-26 | 2017-04-18 | The Curators Of The University Of Missouri | Microdystrophin peptides and methods for treating muscular dystrophy using the same |
| ITTO20130669A1 (it) | 2013-08-05 | 2015-02-06 | Consiglio Nazionale Ricerche | Vettore adeno-associato ricombinante muscolo-specifico e suo impiego nel trattamento di patologie muscolari |
| ES2666322T3 (es) * | 2013-10-08 | 2018-05-04 | Ystem S.R.L. | Composiciones farmacéuticas para el tratamiento de trastornos musculares |
| US9850497B2 (en) | 2013-11-04 | 2017-12-26 | Regents Of The University Of Minnesota | Gene targeting methods and tools |
-
2016
- 2016-11-11 RU RU2018121289A patent/RU2761264C2/ru active
- 2016-11-11 IL IL259178A patent/IL259178B/en unknown
- 2016-11-11 ES ES16865168T patent/ES3034857T3/es active Active
- 2016-11-11 DK DK16865168.5T patent/DK3373980T3/da active
- 2016-11-11 MX MX2018005882A patent/MX2018005882A/es unknown
- 2016-11-11 TN TNP/2018/000163A patent/TN2018000163A1/en unknown
- 2016-11-11 JP JP2018524411A patent/JP6889717B2/ja active Active
- 2016-11-11 AU AU2016354561A patent/AU2016354561B2/en active Active
- 2016-11-11 CN CN201680079597.0A patent/CN108883200B/zh active Active
- 2016-11-11 EP EP16865168.5A patent/EP3373980B1/en active Active
- 2016-11-11 US US15/775,566 patent/US11820972B2/en active Active
- 2016-11-11 WO PCT/US2016/061703 patent/WO2017083776A1/en not_active Ceased
- 2016-11-11 TN TNP/2019/000279A patent/TN2019000279A1/en unknown
- 2016-11-11 KR KR1020187016152A patent/KR102821290B1/ko active Active
- 2016-11-11 CA CA3005240A patent/CA3005240A1/en active Pending
- 2016-11-11 FI FIEP16865168.5T patent/FI3373980T3/fi active
- 2016-11-11 SG SG11201803971UA patent/SG11201803971UA/en unknown
- 2016-11-11 HR HRP20250923TT patent/HRP20250923T1/hr unknown
- 2016-11-11 EA EA201891134A patent/EA201891134A1/ru unknown
-
2018
- 2018-05-10 ZA ZA2018/03080A patent/ZA201803080B/en unknown
- 2018-06-08 CO CONC2018/0005928A patent/CO2018005928A2/es unknown
-
2021
- 2021-05-21 JP JP2021086103A patent/JP7307121B2/ja active Active
-
2022
- 2022-03-02 AU AU2022201427A patent/AU2022201427B2/en active Active
-
2023
- 2023-05-08 JP JP2023076538A patent/JP2023099184A/ja not_active Withdrawn
- 2023-11-17 US US18/513,227 patent/US20240191250A1/en active Pending
-
2025
- 2025-07-22 AU AU2025206419A patent/AU2025206419A1/en active Pending
Similar Documents
| Publication | Publication Date | Title |
|---|---|---|
| JP2019513393A5 (enExample) | ||
| JP7607007B2 (ja) | 変異ａａｖ、及び、細胞、臓器並びに組織への遺伝子導入のための組成物、方法並びに使用法 | |
| JP2019513779A5 (enExample) | ||
| IL259178B (en) | A vector encoding ano5 for the treatment of muscular dystrophy | |
| JP2021512072A5 (enExample) | ||
| JP2020513811A5 (enExample) | ||
| JP2019513399A5 (enExample) | ||
| JP2019513389A5 (enExample) | ||
| Pryadkina et al. | A comparison of AAV strategies distinguishes overlapping vectors for efficient systemic delivery of the 6.2 kb Dysferlin coding sequence | |
| JP2020510447A5 (enExample) | ||
| FI3442600T3 (fi) | Adeno-assosioidulla virusvektorilla b-sarkoglykaanin ja mikro-rna-29:n toimittaminen ja lihasdystrofian hoito | |
| JP2021500352A5 (enExample) | ||
| WO2016077687A4 (en) | Compositions and methods of treating amyotrophic lateral sclerosis (als) | |
| IL320714A (en) | Gene therapy for limb-girdle muscular dystrophy type 2c | |
| JP2023544683A (ja) | ペプチド改変されたａａｖカプシド | |
| JP2021528983A5 (enExample) | ||
| JP2013531471A5 (enExample) | ||
| RU2018116076A (ru) | Модифицированные гены атаксии фридрейха и векторы для генной терапии | |
| BR112014025985A2 (pt) | composição e métodos para transferência de gene altamente eficaz com o uso de variantes de capsídeo de aav | |
| RU2020109343A (ru) | Полинуклеотиды aadc для лечения болезни паркинсона | |
| HRP20201200T1 (hr) | OLIGONUKLEOTIDNI SPOJEVI ZA CILJANJE HUNTINGTIN mRNK | |
| JP2017510298A5 (enExample) | ||
| FI3851537T3 (fi) | Hyperbilirubinemian hoito | |
| MX375360B (es) | Vectores de virus adeno-asociado para el tratamiento de la enfermedad de almacenamiento de glucógeno. | |
| HRP20231077T1 (hr) | Genska terapija za pigmentni retinitis |