JP2018538261A5 - - Google Patents

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Publication number
JP2018538261A5
JP2018538261A5 JP2018524411A JP2018524411A JP2018538261A5 JP 2018538261 A5 JP2018538261 A5 JP 2018538261A5 JP 2018524411 A JP2018524411 A JP 2018524411A JP 2018524411 A JP2018524411 A JP 2018524411A JP 2018538261 A5 JP2018538261 A5 JP 2018538261A5
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JP
Japan
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composition
item
subject
seq
recombinant aav
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JP2018524411A
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English (en)
Japanese (ja)
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JP6889717B2 (ja
JP2018538261A (ja
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Priority claimed from PCT/US2016/061703 external-priority patent/WO2017083776A1/en
Publication of JP2018538261A publication Critical patent/JP2018538261A/ja
Publication of JP2018538261A5 publication Critical patent/JP2018538261A5/ja
Priority to JP2021086103A priority Critical patent/JP7307121B2/ja
Application granted granted Critical
Publication of JP6889717B2 publication Critical patent/JP6889717B2/ja
Active legal-status Critical Current
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JP2018524411A 2015-11-12 2016-11-11 筋ジストロフィーの治療方法 Active JP6889717B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2021086103A JP7307121B2 (ja) 2015-11-12 2021-05-21 筋ジストロフィーの治療方法

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201562254539P 2015-11-12 2015-11-12
US62/254,539 2015-11-12
US201662419793P 2016-11-09 2016-11-09
US62/419,793 2016-11-09
PCT/US2016/061703 WO2017083776A1 (en) 2015-11-12 2016-11-11 Methods of treating muscular dystrophy

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2021086103A Division JP7307121B2 (ja) 2015-11-12 2021-05-21 筋ジストロフィーの治療方法

Publications (3)

Publication Number Publication Date
JP2018538261A JP2018538261A (ja) 2018-12-27
JP2018538261A5 true JP2018538261A5 (enExample) 2019-12-19
JP6889717B2 JP6889717B2 (ja) 2021-06-18

Family

ID=58696162

Family Applications (3)

Application Number Title Priority Date Filing Date
JP2018524411A Active JP6889717B2 (ja) 2015-11-12 2016-11-11 筋ジストロフィーの治療方法
JP2021086103A Active JP7307121B2 (ja) 2015-11-12 2021-05-21 筋ジストロフィーの治療方法
JP2023076538A Withdrawn JP2023099184A (ja) 2015-11-12 2023-05-08 筋ジストロフィーの治療方法

Family Applications After (2)

Application Number Title Priority Date Filing Date
JP2021086103A Active JP7307121B2 (ja) 2015-11-12 2021-05-21 筋ジストロフィーの治療方法
JP2023076538A Withdrawn JP2023099184A (ja) 2015-11-12 2023-05-08 筋ジストロフィーの治療方法

Country Status (21)

Country Link
US (2) US11820972B2 (enExample)
EP (1) EP3373980B1 (enExample)
JP (3) JP6889717B2 (enExample)
KR (1) KR102821290B1 (enExample)
CN (1) CN108883200B (enExample)
AU (3) AU2016354561B2 (enExample)
BR (1) BR112018009657A2 (enExample)
CA (1) CA3005240A1 (enExample)
CO (1) CO2018005928A2 (enExample)
DK (1) DK3373980T3 (enExample)
EA (1) EA201891134A1 (enExample)
ES (1) ES3034857T3 (enExample)
FI (1) FI3373980T3 (enExample)
HR (1) HRP20250923T1 (enExample)
IL (1) IL259178B (enExample)
MX (1) MX2018005882A (enExample)
RU (1) RU2761264C2 (enExample)
SG (1) SG11201803971UA (enExample)
TN (2) TN2019000279A1 (enExample)
WO (1) WO2017083776A1 (enExample)
ZA (1) ZA201803080B (enExample)

Families Citing this family (8)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP3596112A2 (en) 2017-03-17 2020-01-22 Newcastle University Adeno-associated virus vector delivery of a fragment of micro-dystrophin to treat muscular dystrophy
US12134790B2 (en) 2017-09-27 2024-11-05 Inozyme Pharma, Inc. Methods of improving cardiovascular function and treating cardiovascular disease using a recombinant ectonucleotide pyrophosphatase phosphodiesterase (NPP1)
US11926653B2 (en) 2017-10-20 2024-03-12 Research Institute At Nationwide Children's Hospital Methods and materials for NT-3 gene therapy
MY208145A (en) 2018-06-18 2025-04-18 Res Inst Nationwide Childrens Hospital Adeno-associated virus vector delivery of muscle specific micro-dystrophin to treat muscular dystrophy
EP3906308A1 (en) * 2018-12-31 2021-11-10 Research Institute at Nationwide Children's Hospital Dux4 rna silencing using rna targeting crispr-cas13b
IL299094A (en) 2020-06-15 2023-02-01 Res Inst Nationwide Childrens Hospital Administration of an adeno-associated virus vector for muscular dystrophies
KR102732922B1 (ko) * 2021-10-29 2024-11-20 충남대학교 산학협력단 과산화수소수 처리에 의해 유용성분 함량이 증진된 상추의 재배방법
CN117223686B (zh) * 2023-11-15 2024-01-23 四川省农业机械科学研究院 一种扩座除砂一体化蚕盘及养蚕方法

Family Cites Families (19)

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Publication number Priority date Publication date Assignee Title
EP0127839B1 (en) 1983-05-27 1992-07-15 THE TEXAS A&M UNIVERSITY SYSTEM Method for producing a recombinant baculovirus expression vector
ZA848495B (en) 1984-01-31 1985-09-25 Idaho Res Found Production of polypeptides in insect cells
US6204059B1 (en) 1994-06-30 2001-03-20 University Of Pittsburgh AAV capsid vehicles for molecular transfer
WO2002053703A2 (en) 2001-01-05 2002-07-11 Children's Hospital, Inc. Aav2 vectors and methods
AU2003212708A1 (en) 2002-03-05 2003-09-16 Stichting Voor De Technische Wetenschappen Baculovirus expression system
JP2006121961A (ja) 2004-10-28 2006-05-18 Univ Of Tokushima 顎骨骨幹異形成症ｇｄｄの原因遺伝子ｇｄｄ１とその用途
EP2052088A2 (en) * 2006-08-02 2009-04-29 Genizon Biosciences Genemap of the human genes associated with psoriasis
FR2919305B1 (fr) 2007-07-26 2009-09-18 Genethon Ass Loi De 1901 Vecteurs viraux adeno-associes pour l'expression de la dysferline.
GB0715087D0 (en) 2007-08-03 2007-09-12 Summit Corp Plc Drug combinations for the treatment of duchenne muscular dystrophy
US20100026655A1 (en) 2008-07-31 2010-02-04 Avago Technologies Ecbu Ip (Singapore) Pte. Ltd. Capacitive Touchscreen or Touchpad for Finger or Stylus
WO2011044138A1 (en) * 2009-10-05 2011-04-14 Catabasis Pharmaceuticals, Inc. Lipoic acid acylated salicylate derivatives and their uses
KR101841752B1 (ko) 2009-11-03 2018-05-04 더 리전트 오브 더 유니버시티 오브 캘리포니아 저온 수용액 내에서 성장한 다중 표면들 상의 산화 아연 층들에 의해 커버되는 고휘도 발광 다이오드
US9434928B2 (en) 2011-11-23 2016-09-06 Nationwide Children's Hospital, Inc. Recombinant adeno-associated virus delivery of alpha-sarcoglycan polynucleotides
WO2013151665A2 (en) 2012-04-02 2013-10-10 modeRNA Therapeutics Modified polynucleotides for the production of proteins associated with human disease
WO2014037526A1 (en) * 2012-09-07 2014-03-13 INSERM (Institut National de la Santé et de la Recherche Médicale) In vitro genetic diagnostic of inherited neuromuscular disorders
US9624282B2 (en) 2012-11-26 2017-04-18 The Curators Of The University Of Missouri Microdystrophin peptides and methods for treating muscular dystrophy using the same
ITTO20130669A1 (it) 2013-08-05 2015-02-06 Consiglio Nazionale Ricerche Vettore adeno-associato ricombinante muscolo-specifico e suo impiego nel trattamento di patologie muscolari
ES2666322T3 (es) * 2013-10-08 2018-05-04 Ystem S.R.L. Composiciones farmacéuticas para el tratamiento de trastornos musculares
US9850497B2 (en) 2013-11-04 2017-12-26 Regents Of The University Of Minnesota Gene targeting methods and tools

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