JP2018519835A5 - - Google Patents

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JP2018519835A5
JP2018519835A5 JP2018500697A JP2018500697A JP2018519835A5 JP 2018519835 A5 JP2018519835 A5 JP 2018519835A5 JP 2018500697 A JP2018500697 A JP 2018500697A JP 2018500697 A JP2018500697 A JP 2018500697A JP 2018519835 A5 JP2018519835 A5 JP 2018519835A5
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seq
nucleic acid
acid molecule
stranded nucleic
isolated double
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JP2018500697A
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JP2018519835A (ja
JP6983752B2 (ja
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Priority claimed from PCT/US2016/041095 external-priority patent/WO2017007813A1/en
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JP2018500697A 2015-07-06 2016-07-06 スーパーオキシドディスムターゼ1(sod1)を標的とする核酸分子 Expired - Fee Related JP6983752B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201562189050P 2015-07-06 2015-07-06
US62/189,050 2015-07-06
PCT/US2016/041095 WO2017007813A1 (en) 2015-07-06 2016-07-06 Nucleic acid molecules targeting superoxide dismutase 1 (sod1)

Publications (3)

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JP2018519835A JP2018519835A (ja) 2018-07-26
JP2018519835A5 true JP2018519835A5 (cg-RX-API-DMAC7.html) 2019-08-15
JP6983752B2 JP6983752B2 (ja) 2021-12-17

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JP2018500697A Expired - Fee Related JP6983752B2 (ja) 2015-07-06 2016-07-06 スーパーオキシドディスムターゼ1(sod1)を標的とする核酸分子

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US (1) US11001845B2 (cg-RX-API-DMAC7.html)
EP (2) EP3862005A1 (cg-RX-API-DMAC7.html)
JP (1) JP6983752B2 (cg-RX-API-DMAC7.html)
KR (1) KR20180026739A (cg-RX-API-DMAC7.html)
CN (1) CN108135923B (cg-RX-API-DMAC7.html)
CA (1) CA2991598A1 (cg-RX-API-DMAC7.html)
WO (1) WO2017007813A1 (cg-RX-API-DMAC7.html)

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US10900039B2 (en) 2014-09-05 2021-01-26 Phio Pharmaceuticals Corp. Methods for treating aging and skin disorders using nucleic acids targeting Tyr or MMP1
US11001845B2 (en) 2015-07-06 2021-05-11 Phio Pharmaceuticals Corp. Nucleic acid molecules targeting superoxide dismutase 1 (SOD1)
WO2017007825A1 (en) 2015-07-06 2017-01-12 Rxi Pharmaceuticals Corporation Methods for treating neurological disorders using a synergistic small molecule and nucleic acids therapeutic approach
US11021707B2 (en) 2015-10-19 2021-06-01 Phio Pharmaceuticals Corp. Reduced size self-delivering nucleic acid compounds targeting long non-coding RNA
CN114945669B (zh) * 2019-11-06 2025-01-10 阿尔尼拉姆医药品有限公司 肝外递送
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US20250297258A1 (en) * 2021-07-07 2025-09-25 Ractigen Therapeutics Oligonucleotide-based delivery vehicle for oligonucleotides agents and methods of use thereof
WO2025045130A1 (zh) * 2023-08-29 2025-03-06 石药集团中奇制药技术(石家庄)有限公司 一种抑制sod1基因表达的dsrna分子及其应用

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