JP2014517694A5 - - Google Patents

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Publication number
JP2014517694A5
JP2014517694A5 JP2014512189A JP2014512189A JP2014517694A5 JP 2014517694 A5 JP2014517694 A5 JP 2014517694A5 JP 2014512189 A JP2014512189 A JP 2014512189A JP 2014512189 A JP2014512189 A JP 2014512189A JP 2014517694 A5 JP2014517694 A5 JP 2014517694A5
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JP
Japan
Prior art keywords
pharmaceutical composition
nucleic acid
acid sequence
vector
viral vector
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JP2014512189A
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English (en)
Japanese (ja)
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JP2014517694A (ja
JP6162104B2 (ja
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Priority claimed from PCT/US2012/039897 external-priority patent/WO2012162705A2/en
Publication of JP2014517694A publication Critical patent/JP2014517694A/ja
Publication of JP2014517694A5 publication Critical patent/JP2014517694A5/ja
Application granted granted Critical
Publication of JP6162104B2 publication Critical patent/JP6162104B2/ja
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JP2014512189A 2011-05-26 2012-05-29 細胞及び遺伝子に基づく心臓機能改善方法 Active JP6162104B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201161490450P 2011-05-26 2011-05-26
US61/490,450 2011-05-26
PCT/US2012/039897 WO2012162705A2 (en) 2011-05-26 2012-05-29 Cell and gene based methods to improve cardiac function

Publications (3)

Publication Number Publication Date
JP2014517694A JP2014517694A (ja) 2014-07-24
JP2014517694A5 true JP2014517694A5 (enExample) 2015-07-16
JP6162104B2 JP6162104B2 (ja) 2017-07-12

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ID=47218136

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2014512189A Active JP6162104B2 (ja) 2011-05-26 2012-05-29 細胞及び遺伝子に基づく心臓機能改善方法

Country Status (10)

Country Link
US (1) US9868937B2 (enExample)
EP (1) EP2714709B1 (enExample)
JP (1) JP6162104B2 (enExample)
KR (1) KR20140035967A (enExample)
CN (1) CN103946230B (enExample)
AU (1) AU2012258525B2 (enExample)
BR (1) BR112013030209A2 (enExample)
CA (1) CA2837322C (enExample)
RU (1) RU2608957C2 (enExample)
WO (1) WO2012162705A2 (enExample)

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Publication number Priority date Publication date Assignee Title
BR112013030209A2 (pt) 2011-05-26 2017-06-13 Univ Washington métodos baseados em célula e gene para melhorar função cardíaca
EP2792742A1 (en) * 2013-04-17 2014-10-22 Universitätsklinikum Hamburg-Eppendorf (UKE) Gene-therapy vectors for treating cardiomyopathy
WO2015153357A1 (en) * 2014-03-29 2015-10-08 Beat Biotherapeutics Corp. Compositions and methods for improving cardiac function
US10479821B2 (en) 2015-01-16 2019-11-19 University Of Washington Micro-dystrophins and related methods of use
US10646588B2 (en) 2015-03-11 2020-05-12 The United States Of America, As Represented By The Secretary, Department Of Health And Human Services RP2 and RPGR vectors for treating X-linked retinitis pigmentosa
US10118034B2 (en) * 2015-08-18 2018-11-06 Boston Scientific Scimed, Inc. Methods for producing cardiomyocyte cells
WO2018144770A1 (en) * 2017-02-04 2018-08-09 AnaBios Corporation System and methods for predicting drug-induced inotropic and pro-arrhythmia risk
CN108913655B (zh) * 2018-07-16 2022-07-15 浙江大学 基于多能干细胞技术建立“人源性”心肌肥大模型的方法
CN112218877B (zh) 2018-08-27 2025-07-25 瑞泽恩制药公司 拉曼光谱在下游纯化中的应用
KR20210102870A (ko) 2018-08-30 2021-08-20 테나야 테라퓨틱스, 인코포레이티드 미오카르딘 및 ascl1을 사용한 심장 세포 재프로그래밍
US20200405824A1 (en) * 2019-06-26 2020-12-31 University Of Washington Use of ribonucleotide reductase alone or in combination with micro-dystrophin to treat duchenne muscular dystrophy striated muscle disease
CN110384800B (zh) * 2019-07-19 2021-06-08 广东省实验动物监测所 LncRNA XLOC_075168在制备促进血管新生的药物中的应用
BR112022015979A2 (pt) 2020-02-13 2022-10-11 Tenaya Therapeutics Inc Vetores de terapia genética para tratamento de doenças cardíacas
US20240189481A1 (en) * 2021-04-06 2024-06-13 University Of Washington Non-contractile cardiomyocytes for cardiac repair
JP2024545507A (ja) * 2021-12-10 2024-12-09 スペースクラフト セブン リミテッド ライアビリティ カンパニー Aavベクターを用いたトロポニンc(tnnc1)遺伝子治療
WO2025207745A1 (en) * 2024-03-27 2025-10-02 The Board Of Trustees Of The Leland Stanford Junior University Methods of inducing dilated cardiomyopathy phenotype in cardiomyocytes and applications thereof
CN120758566B (zh) * 2025-09-10 2025-11-21 瓯江实验室 一种在心肌细胞中特异性过表达zer1的病毒载体的构建及在心衰治疗中的应用

Family Cites Families (14)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
JPH02240440A (ja) 1989-03-14 1990-09-25 Shiigeru:Kk 慣性ダンパ
GB9022543D0 (en) 1990-10-17 1990-11-28 Wellcome Found Antibody production
US6151525A (en) * 1997-11-07 2000-11-21 Medtronic, Inc. Method and system for myocardial identifier repair
WO1999062940A2 (en) 1998-05-30 1999-12-09 Collateral Therapeutics, Inc. Methods of altering cardiac cell phenotype
CA2342283C (en) * 1998-09-11 2004-05-25 The Regents Of The University Of California Recombinant adenovirus for tissue specific expression in heart
EP1139751A4 (en) * 1998-12-28 2003-03-19 Arch Dev Corp EFFICIENT AND STABLE -I (IN VIVO) GENE TRANSFER TO CARDIOMYCETS USING RECOMBINANT ADENO-ASSOCIATED VIRUS VECTORS
AU2002230999A1 (en) * 2000-12-21 2002-07-01 Medtronic, Inc. Electrically responsive promoter system
AU2003234520A1 (en) * 2002-05-08 2003-11-11 The Regents Of The University Of California Methods and compositions for correction of cardiac conduction disturbances
US20040161847A1 (en) 2002-09-11 2004-08-19 Phillips Michael Ian Vigilant vector system
EP1654366A1 (en) 2003-08-11 2006-05-10 University Of South Florida Stem cell beacon
ATE532863T1 (de) 2003-11-21 2011-11-15 Daiichi Sankyo Co Ltd Verfahren zur anzucht von myokardzellen
WO2005094485A2 (en) 2004-03-25 2005-10-13 Yun Yen Drug screening
DE102011018586A1 (de) 2011-04-26 2012-10-31 Oliver Müller Vektorsystem zur spezifischen Genexpression im Herzmuskel
BR112013030209A2 (pt) 2011-05-26 2017-06-13 Univ Washington métodos baseados em célula e gene para melhorar função cardíaca

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