JP2012143233A5 - - Google Patents

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JP2012143233A5
JP2012143233A5 JP2012040561A JP2012040561A JP2012143233A5 JP 2012143233 A5 JP2012143233 A5 JP 2012143233A5 JP 2012040561 A JP2012040561 A JP 2012040561A JP 2012040561 A JP2012040561 A JP 2012040561A JP 2012143233 A5 JP2012143233 A5 JP 2012143233A5
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JP5769650B2 (ja
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JP2012040561A 2004-06-01 2012-02-27 Aavベクターの凝集を防ぐための組成物およびその方法 Expired - Lifetime JP5769650B2 (ja)

Applications Claiming Priority (4)

Application Number Priority Date Filing Date Title
US57599704P 2004-06-01 2004-06-01
US60/575,997 2004-06-01
US63922204P 2004-12-22 2004-12-22
US60/639,222 2004-12-22

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JP2007515525A Division JP2008501339A (ja) 2004-06-01 2005-06-01 Aavベクターの凝集を防ぐための組成物およびその方法

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JP2014014070A Division JP2014111625A (ja) 2004-06-01 2014-01-29 Aavベクターの凝集を防ぐための組成物およびその方法

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JP2012143233A JP2012143233A (ja) 2012-08-02
JP2012143233A5 true JP2012143233A5 (enExample) 2013-05-09
JP5769650B2 JP5769650B2 (ja) 2015-08-26

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JP2007515525A Pending JP2008501339A (ja) 2004-06-01 2005-06-01 Aavベクターの凝集を防ぐための組成物およびその方法
JP2012040561A Expired - Lifetime JP5769650B2 (ja) 2004-06-01 2012-02-27 Aavベクターの凝集を防ぐための組成物およびその方法
JP2014014070A Pending JP2014111625A (ja) 2004-06-01 2014-01-29 Aavベクターの凝集を防ぐための組成物およびその方法
JP2016058761A Pending JP2016195587A (ja) 2004-06-01 2016-03-23 Aavベクターの凝集を防ぐための組成物およびその方法
JP2018218970A Pending JP2019058177A (ja) 2004-06-01 2018-11-22 Aavベクターの凝集を防ぐための組成物およびその方法

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JP2007515525A Pending JP2008501339A (ja) 2004-06-01 2005-06-01 Aavベクターの凝集を防ぐための組成物およびその方法

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JP2014014070A Pending JP2014111625A (ja) 2004-06-01 2014-01-29 Aavベクターの凝集を防ぐための組成物およびその方法
JP2016058761A Pending JP2016195587A (ja) 2004-06-01 2016-03-23 Aavベクターの凝集を防ぐための組成物およびその方法
JP2018218970A Pending JP2019058177A (ja) 2004-06-01 2018-11-22 Aavベクターの凝集を防ぐための組成物およびその方法

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US (4) US7704721B2 (enExample)
EP (3) EP3290513B1 (enExample)
JP (5) JP2008501339A (enExample)
BR (1) BRPI0511764B8 (enExample)
CA (1) CA2569244C (enExample)
DK (2) DK1751275T3 (enExample)
ES (2) ES2647477T3 (enExample)
HU (2) HUE035418T2 (enExample)
MX (3) MXPA06014030A (enExample)
WO (1) WO2005118792A1 (enExample)

Families Citing this family (112)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
ES2673823T3 (es) * 2006-11-03 2018-06-25 Alphavax, Inc. Formulaciones de alfavirus y de partículas de replicones de alfavirus y métodos relacionados
US20090111099A1 (en) * 2007-10-27 2009-04-30 Yongsheng Ma Promoter Detection and Analysis
US8067241B2 (en) * 2009-08-26 2011-11-29 General Electric Company Method and apparatus for antigen retrieval process
CA2787827C (en) 2010-01-28 2020-11-10 The Children's Hospital Of Philadelphia A scalable manufacturing platform for viral vector purification and viral vectors so purified for use in gene therapy
BR112012026095A2 (pt) 2010-04-14 2015-09-15 Emd Millipore Corp métodos de produção de estoques de vírus de alta pureza e altos títulos e métodos de uso dos mesmos.
WO2012018628A1 (en) 2010-07-26 2012-02-09 Board Of Regents, The University Of Texas System Methods for inducing an immune response via buccal and/or sublingual administration of a vaccine
EP2686423A4 (en) * 2011-03-14 2015-01-28 Nat Res Council Canada METHOD FOR PRODUCING VIRUSES IN CELLS
EP2782596A4 (en) 2011-11-22 2015-07-29 Philadelphia Children Hospital VIRUS VECTORS FOR HIGHLY EFFICIENT TRANSGENIC ADMINISTRATION
EP2790737B1 (en) * 2011-12-12 2018-11-21 The Children's Hospital of Philadelphia Large commercial scale lentiviral vector production system and vectors produced thereby
US9974850B2 (en) 2013-01-25 2018-05-22 Board Of Regents, The University Of Texas System Immunogenic compositions and uses thereof
ES2689150T3 (es) * 2013-06-17 2018-11-08 De Staat Der Nederlanden, Vert. Door De Minister Van Vws, Ministerie Van Volksgezondheid, Welzijn En Sport Métodos para la prevención de agregación de componentes víricos
JP6567974B2 (ja) * 2013-11-29 2019-08-28 タカラバイオ株式会社 アデノ随伴ウイルスの定量方法
CA2942451A1 (en) 2014-04-25 2015-10-29 Genethon Treatment of hyperbilirubinemia
US10577627B2 (en) 2014-06-09 2020-03-03 Voyager Therapeutics, Inc. Chimeric capsids
WO2016004319A1 (en) * 2014-07-02 2016-01-07 University Of Florida Research Foundation, Inc. Compositions and methods for purifying recombinant adeno-associated virus
CA2966620A1 (en) 2014-11-05 2016-05-12 Voyager Therapeutics, Inc. Aadc polynucleotides for the treatment of parkinson's disease
CA2975583A1 (en) 2014-11-14 2016-05-19 Voyager Therapeutics, Inc. Modulatory polynucleotides
CA2967367C (en) 2014-11-14 2023-05-16 Voyager Therapeutics, Inc. Compositions and methods of treating amyotrophic lateral sclerosis (als)
HK1245326A1 (zh) 2014-12-12 2018-08-24 Voyager Therapeutics, Inc. 用於生产scaav的组合物和方法
WO2016114992A2 (en) * 2015-01-13 2016-07-21 Alfa Wassermann, Inc. Methods of purifying adeno-associated virus (aav) and/or recombinant adeno-associated virus (raav) and gradients and flow-through buffers therefore
EP3054007A1 (en) 2015-02-09 2016-08-10 Institut National De La Sante Et De La Recherche Medicale (Inserm) Recombinant adeno-associated virus particle purification comprising an immuno-affinity purification step
US20180230489A1 (en) 2015-10-28 2018-08-16 Voyager Therapeutics, Inc. Regulatable expression using adeno-associated virus (aav)
JP7418957B2 (ja) 2015-11-16 2024-01-22 リサーチ インスティチュート アット ネイションワイド チルドレンズ ホスピタル タイチン系ミオパチー及び他のタイチノパチーの治療のための材料及び方法
WO2017100676A1 (en) * 2015-12-11 2017-06-15 The Trustees Of The University Of Pennsylvania Scalable purification method for aav8
LT3436593T (lt) * 2016-03-28 2023-03-10 Ultragenyx Pharmaceutical Inc. Adenoviruso šiluminio inaktyvavimo būdai
WO2017189959A1 (en) 2016-04-29 2017-11-02 Voyager Therapeutics, Inc. Compositions for the treatment of disease
US11299751B2 (en) 2016-04-29 2022-04-12 Voyager Therapeutics, Inc. Compositions for the treatment of disease
KR20240056729A (ko) 2016-05-18 2024-04-30 보이저 테라퓨틱스, 인크. 조절성 폴리뉴클레오티드
KR20220108216A (ko) 2016-05-18 2022-08-02 보이저 테라퓨틱스, 인크. 헌팅톤 질환을 치료하기 위한 조성물 및 방법
PT3488007T (pt) * 2016-07-21 2024-03-14 Spark Therapeutics Inc Métodos escaláveis de recuperação elevada para produzir vetor viral adenoassociado recombinante (raav) de alto rendimento e vetores virais adenoassociados recombinantes (raav) produzidos pelos mesmos
US20190185864A1 (en) 2016-08-23 2019-06-20 Akouos, Inc. Compositions and methods for treating non-age-associated hearing impairment in a human subject
AU2017321488B2 (en) 2016-08-30 2022-10-20 The Regents Of The University Of California Methods for biomedical targeting and delivery and devices and systems for practicing the same
EP3293259A1 (en) 2016-09-12 2018-03-14 Genethon Acid-alpha glucosidase variants and uses thereof
PE20191203A1 (es) 2016-09-12 2019-09-10 Genethon Variantes de alfa-glucosidasa acida y usos de las mismas
EP3293260A1 (en) 2016-09-12 2018-03-14 Genethon Acid-alpha glucosidase variants and uses thereof
EP3293203A1 (en) 2016-09-12 2018-03-14 Genethon Acid-alpha glucosidase variants and uses thereof
EP3512939A1 (en) 2016-09-16 2019-07-24 Leukocare AG A novel method for obtaining efficient viral vector-based compositions for vaccination or gene therapy
KR102574849B1 (ko) * 2016-11-04 2023-09-06 다케다 야쿠힌 고교 가부시키가이샤 아데노-연관 바이러스 제형
US10626376B2 (en) 2016-11-14 2020-04-21 St. Jude Children's Research Hospital Method for isolating and purifying adeno-associated virus particles using salt
US10294452B2 (en) * 2016-11-22 2019-05-21 Dao-Yao He Lysis, extraction and purification of adeno-associated virus and adenovirus from host cells
EP3576796A1 (en) 2017-02-01 2019-12-11 Centre National De La Recherche Scientifique Particles and compositions comprising the same for transfection
MA47820A (fr) 2017-03-10 2020-01-15 Genethon Traitement de la glycogénose de type iii
EP3618839A4 (en) 2017-05-05 2021-06-09 Voyager Therapeutics, Inc. Compositions and methods of treating amyotrophic lateral sclerosis (als)
SG11201909868YA (en) 2017-05-05 2019-11-28 Voyager Therapeutics Inc Compositions and methods of treating huntington's disease
JOP20190269A1 (ar) 2017-06-15 2019-11-20 Voyager Therapeutics Inc بولي نوكليوتيدات aadc لعلاج مرض باركنسون
WO2019018342A1 (en) 2017-07-17 2019-01-24 Voyager Therapeutics, Inc. NETWORK EQUIPMENT TRACK GUIDE SYSTEM
WO2019028306A2 (en) 2017-08-03 2019-02-07 Voyager Therapeutics, Inc. COMPOSITIONS AND METHODS FOR ADMINISTRATION OF ADENO-ASSOCIATED VIRUSES
AU2018338728B2 (en) 2017-09-29 2025-01-02 Centre National De La Recherche Scientifique (Cnrs) Rescue of central and peripheral neurological phenotype of Friedreich's Ataxia by intravenous delivery
EP3697908A1 (en) 2017-10-16 2020-08-26 Voyager Therapeutics, Inc. Treatment of amyotrophic lateral sclerosis (als)
WO2019079240A1 (en) 2017-10-16 2019-04-25 Voyager Therapeutics, Inc. TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)
BR112019013268A2 (pt) * 2017-11-08 2019-12-17 Avexis Inc. meios e métodos para a preparação de vetores virais e usos dos mesmos
JP2021505610A (ja) * 2017-12-05 2021-02-18 アプライド ジェネティック テクノロジーズ コーポレイション ウイルス粒子のための製剤最適化
BR112020015173A2 (pt) 2018-01-31 2020-12-29 Research Institute At Nationwide Children's Hospital Terapia gênica para distrofia muscular da cintura e membros do tipo 2c
CN120665951A (zh) 2018-02-07 2025-09-19 吉尼松公司 杂合调控元件
US20210010028A1 (en) 2018-03-06 2021-01-14 Voyager Therapeutics, Inc. Insect cell manufactured partial self-complementary aav genomes
CN112313331A (zh) 2018-04-27 2021-02-02 沃雅戈治疗公司 用于测量aadc病毒载体效力的方法
MX2020012077A (es) 2018-05-15 2021-03-09 Voyager Therapeutics Inc Composiciones y metodos para el tratamiento de la enfermedad de parkinson.
WO2019222441A1 (en) 2018-05-16 2019-11-21 Voyager Therapeutics, Inc. Aav serotypes for brain specific payload delivery
US20210214749A1 (en) 2018-05-16 2021-07-15 Voyager Therapeutics, Inc. Directed evolution
US12228571B2 (en) 2018-06-08 2025-02-18 Novartis Ag Cell-based assay for measuring drug product potency
KR20210028162A (ko) 2018-06-29 2021-03-11 더 리서치 인스티튜트 앳 네이션와이드 칠드런스 하스피탈 지대근 이영양증 2a형을 치료하기 위한 재조합 아데노 연관 바이러스 생성물 및 방법
AU2019296451B2 (en) 2018-06-29 2021-04-29 Wuhan Neurophth Biotechnology Limited Company Compositions and methods for treating leber's hereditary optic neuropathy
WO2020010042A1 (en) 2018-07-02 2020-01-09 Voyager Therapeutics, Inc. Treatment of amyotrophic lateral sclerosis and disorders associated with the spinal cord
BR112021000327A2 (pt) * 2018-07-11 2021-04-06 Baxalta Incorporated Composições de aav
WO2020023612A1 (en) 2018-07-24 2020-01-30 Voyager Therapeutics, Inc. Systems and methods for producing gene therapy formulations
EP3833746B1 (en) 2018-08-08 2023-03-29 Genethon Mini-gde for the treatment of glycogen storage disease iii
US20210163991A1 (en) * 2018-08-10 2021-06-03 Regenxbio Inc. Scalable method for recombinant aav production
AU2019323434A1 (en) 2018-08-20 2021-02-25 Wuhan Neurophth Biotechnology Limited Company Compositions and methods for treating leber's hereditary optic neuropathy
EP3856762A1 (en) 2018-09-28 2021-08-04 Voyager Therapeutics, Inc. Frataxin expression constructs having engineered promoters and methods of use thereof
TW202035689A (zh) 2018-10-04 2020-10-01 美商航海家醫療公司 測量病毒載體粒子的效價及強度之方法
CN113631225A (zh) 2019-01-18 2021-11-09 沃雅戈治疗公司 用于生产aav颗粒的方法和系统
SG11202109113TA (en) 2019-02-26 2021-09-29 Res Inst Nationwide Childrens Hospital Adeno-associated virus vector delivery of b-sarcoglycan and the treatment of muscular dystrophy
KR20210148273A (ko) 2019-04-08 2021-12-07 제네똥 근육 발현을 위한 하이브리드 프로모터
AU2020257570A1 (en) 2019-04-19 2021-10-28 Genethon Gene therapy of fibroblast growth factor 23 related hypophosphatemic diseases
WO2020214929A1 (en) * 2019-04-19 2020-10-22 Regenxbio Inc. Adeno-associated virus vector formulations and methods
US20220243225A1 (en) 2019-04-29 2022-08-04 Voyager Therapeutics, Inc. SYSTEMS AND METHODS FOR PRODUCING BACULOVIRAL INFECTED INSECT CELLS (BIICs) IN BIOREACTORS
CN120137971A (zh) 2019-07-25 2025-06-13 诺华股份有限公司 可调节的表达系统
EP4010465A1 (en) 2019-08-09 2022-06-15 Voyager Therapeutics, Inc. Cell culture medium for use in producing gene therapy products in bioreactors
US20220325250A1 (en) 2019-08-14 2022-10-13 Leukocare Ag Method for obtaining efficient compositions comprising viral vectors for vaccination or gene therapy
US11155835B2 (en) 2019-08-19 2021-10-26 The Catholic University Of America Prokaryotic-eukaryotic hybrid viral vector for delivery of large cargos of genes and proteins into human cells
US11401530B2 (en) 2019-08-19 2022-08-02 The Catholic University Of America Bacteriophage-based artificial viruses for human genome remodeling
PL4017871T3 (pl) 2019-08-21 2024-07-08 Research Institute At Nationwide Children's Hospital Dostarczanie alfa-sarkoglikanu za pomocą wektora wirusa związanego z adenowirusami i leczenie dystrofii mięśniowej
EP4022070A1 (en) 2019-08-26 2022-07-06 Voyager Therapeutics, Inc. Controlled expression of viral proteins
EP4041292A1 (en) 2019-10-07 2022-08-17 RegenxBio Inc. Adeno-associated virus vector pharmaceutical composition and methods
WO2021078834A1 (en) 2019-10-22 2021-04-29 Genethon Chimeric acid-alpha glucosidase polypeptides and uses thereof
CA3151442A1 (en) 2019-10-22 2021-04-29 Pasqualina COLELLA Sortilin receptor ligand based chimeric polypeptides and uses thereof
CN113025633B (zh) 2019-12-09 2024-08-27 武汉纽福斯生物科技有限公司 编码人nadh脱氢酶亚单位1蛋白的核酸及其应用
KR102167829B1 (ko) * 2020-02-10 2020-10-20 주식회사 이노테라피 아데노연관바이러스용 안정화제 및 이를 이용한 아데노연관바이러스의 안정화 방법
WO2021168362A1 (en) 2020-02-21 2021-08-26 Akouos, Inc. Compositions and methods for treating non-age-associated hearing impairment in a human subject
WO2021236908A2 (en) 2020-05-20 2021-11-25 Biomarin Pharmaceutical Inc. Use of regulatory proteins for the production of adeno-associated virus
EP3913060A1 (en) 2020-05-22 2021-11-24 Genethon Vectors encoding a glucose-6-phosphatase (g6pase-a) for gene therapy
CN116096867A (zh) * 2020-06-02 2023-05-09 詹森生物科技公司 用于病毒纯化的材料和方法
EP4192514A1 (en) 2020-08-06 2023-06-14 Voyager Therapeutics, Inc. Cell culture medium for use in producing gene therapy products in bioreactors
IL300323A (en) * 2020-08-07 2023-04-01 Janssen Biotech Inc Formulations for viral particles with a high degree of purity
WO2022043280A1 (en) 2020-08-24 2022-03-03 Genethon C-terminal truncated gde for the treatment of glycogen storage disease iii
IL302128A (en) 2020-11-02 2023-06-01 Biomarin Pharm Inc A process for the enrichment of adeno-associated virus
WO2022122883A1 (en) 2020-12-09 2022-06-16 Genethon Lysosomal acid lipase variants and uses thereof
EP4301768A2 (en) 2021-03-03 2024-01-10 Voyager Therapeutics, Inc. Controlled expression of viral proteins
US20240141378A1 (en) 2021-03-03 2024-05-02 Voyager Therapeutics, Inc. Controlled expression of viral proteins
WO2022236008A1 (en) * 2021-05-07 2022-11-10 Board Of Regents, The University Of Texas System Methods and compositions for transport, storage, and delivery of adeno-associated viral vector and other molecules
WO2023012313A1 (en) 2021-08-04 2023-02-09 Genethon Hybrid promoters for gene expression in muscles and in the cns
EP4402265A1 (en) 2021-09-16 2024-07-24 Novartis AG Novel transcription factors
US12285497B2 (en) 2021-10-15 2025-04-29 Research Institute At Nationwide Children's Hospital Self-complementary adeno-associated virus vector and its use in treatment of muscular dystrophy
EP4422613A1 (en) 2021-10-25 2024-09-04 Novartis AG Methods for improving adeno-associated virus (aav) delivery
WO2023175584A1 (en) 2022-03-17 2023-09-21 Innoskel Polynucleotides encoding the alpha-1 chain of human type ii collagen and methods of their use
WO2023175585A1 (en) 2022-03-17 2023-09-21 Innoskel Hybrid promoters and their use in osteolysis syndrome
US20250353883A1 (en) 2022-05-06 2025-11-20 Novartis Ag Novel recombinant aav vp2 fusion polypeptides
CA3252764A1 (en) 2022-06-09 2023-12-14 Inst Nat Sante Rech Med GDE truncated at the N-terminal level for the treatment of type III glycogen storage disease
WO2024054983A1 (en) 2022-09-08 2024-03-14 Voyager Therapeutics, Inc. Controlled expression of viral proteins
TW202426017A (zh) * 2022-11-24 2024-07-01 俄羅斯聯邦商拜奧卡德聯合股份公司 非包膜病毒的藥物組合物
WO2025003477A1 (en) 2023-06-29 2025-01-02 Genethon N-terminal truncated glycogen debranching enzymes for the treatment of glycogen storage disease iii
EP4606892A1 (en) 2024-02-23 2025-08-27 Merck Patent GmbH Methods for the production of viral particles

Family Cites Families (8)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
SE420977B (sv) * 1976-03-18 1981-11-16 Kabi Ab Forfarande for rening och isolering av hepatitvirus for vaccinframstellning
DE69737107T2 (de) * 1996-11-20 2007-07-12 Introgen Therapeutics Inc., Austin Ein verbessertes verfahren zur produktion und reinigung von adenoviralen vektoren
US7732129B1 (en) * 1998-12-01 2010-06-08 Crucell Holland B.V. Method for the production and purification of adenoviral vectors
US6566118B1 (en) * 1997-09-05 2003-05-20 Targeted Genetics Corporation Methods for generating high titer helper-free preparations of released recombinant AAV vectors
EP1080218A1 (en) * 1998-05-27 2001-03-07 University of Florida Method of preparing recombinant adeno-associated virus compositions by using an iodixanol gradient
EP2420247A1 (en) * 2000-03-07 2012-02-22 Merck Sharp & Dohme Corp. Adenovirus formulations
US6593123B1 (en) 2000-08-07 2003-07-15 Avigen, Inc. Large-scale recombinant adeno-associated virus (rAAV) production and purification
ATE360683T1 (de) * 2002-05-14 2007-05-15 Merck & Co Inc Verfahren zur reinigung von adenovirus

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