ES2700048T3 - Terapia génica par la enfermedad de Niemann-Pick tipo A - Google Patents
Terapia génica par la enfermedad de Niemann-Pick tipo A Download PDFInfo
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- ES2700048T3 ES2700048T3 ES07763560T ES07763560T ES2700048T3 ES 2700048 T3 ES2700048 T3 ES 2700048T3 ES 07763560 T ES07763560 T ES 07763560T ES 07763560 T ES07763560 T ES 07763560T ES 2700048 T3 ES2700048 T3 ES 2700048T3
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Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
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| US77162806P | 2006-02-08 | 2006-02-08 | |
| US77236006P | 2006-02-09 | 2006-02-09 | |
| PCT/US2007/003388 WO2007092563A2 (en) | 2006-02-08 | 2007-02-08 | Gene therapy for niemann-pick disease type a |
Publications (1)
| Publication Number | Publication Date |
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| ES2700048T3 true ES2700048T3 (es) | 2019-02-13 |
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Family Applications (1)
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| ES07763560T Active ES2700048T3 (es) | 2006-02-08 | 2007-02-08 | Terapia génica par la enfermedad de Niemann-Pick tipo A |
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| JP (2) | JP5706602B2 (OSRAM) |
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| BR (1) | BRPI0707590A2 (OSRAM) |
| CY (1) | CY1121380T1 (OSRAM) |
| DK (1) | DK1986661T3 (OSRAM) |
| ES (1) | ES2700048T3 (OSRAM) |
| HU (1) | HUE041928T2 (OSRAM) |
| IL (2) | IL193165B (OSRAM) |
| LT (1) | LT1986661T (OSRAM) |
| MX (3) | MX360595B (OSRAM) |
| PL (1) | PL1986661T3 (OSRAM) |
| PT (1) | PT1986661T (OSRAM) |
| SI (1) | SI1986661T1 (OSRAM) |
| WO (1) | WO2007092563A2 (OSRAM) |
Families Citing this family (28)
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| CA2606490C (en) | 2005-05-02 | 2018-02-06 | Genzyme Corporation | Gene therapy for spinal cord disorders |
| ES2887076T3 (es) | 2005-05-02 | 2021-12-21 | Genzyme Corp | Terapia génica para trastornos neurometabólicos |
| PL3252161T3 (pl) * | 2007-06-06 | 2022-03-07 | Genzyme Corporation | Terapia genowa dla lizosomalnych chorób spichrzeniowych |
| WO2010138263A2 (en) | 2009-05-28 | 2010-12-02 | University Of Massachusetts | Novel aav 's and uses thereof |
| DK2826860T3 (en) * | 2010-04-23 | 2018-12-03 | Univ Massachusetts | CNS targeting AAV vectors and methods for their use |
| US20130090374A1 (en) * | 2011-04-20 | 2013-04-11 | Miguel Sena-Esteves | Methods for the treatment of tay-sachs disease, sandhoff disease, and gm1-gangliosidosis |
| EP3622821A1 (en) * | 2013-05-15 | 2020-03-18 | Regents of the University of Minnesota | Adeno-associated virus mediated gene transfer to the central nervous system |
| EP3209311B1 (en) | 2014-10-21 | 2024-03-06 | University of Massachusetts | Recombinant aav variants and uses thereof |
| CA2979495A1 (en) * | 2015-03-17 | 2016-09-22 | Vrije Universiteit Brussel | Optimized liver-specific expression systems for fviii and fix |
| GB201508025D0 (en) | 2015-05-11 | 2015-06-24 | Ucl Business Plc | Fabry disease gene therapy |
| IL262211B2 (en) | 2016-04-15 | 2024-01-01 | Univ Pennsylvania | Gene therapy for treating mucopolysaccharidosis type ii |
| EP3519431A1 (en) | 2016-09-28 | 2019-08-07 | Cohbar Inc. | Therapeutic mots-c related peptides |
| AU2017341849B2 (en) | 2016-10-13 | 2024-03-21 | University Of Massachusetts | AAV capsid designs |
| US20190269797A1 (en) * | 2016-11-04 | 2019-09-05 | The Children's Hospital Of Philadelphia | Gene transfer compositions, methods and uses for treating neurodegenerative diseases |
| WO2018156892A1 (en) | 2017-02-23 | 2018-08-30 | Adrx, Inc. | Peptide inhibitors of transcription factor aggregation |
| WO2018226992A1 (en) | 2017-06-07 | 2018-12-13 | Adrx, Inc. | Tau aggregation inhibitors |
| US12116577B2 (en) | 2017-06-20 | 2024-10-15 | The United States Of America, As Represented By The Secretary, Department Of Health And Human Services | Codon-optimized human NPC1 genes for the treatment of Niemann-Pick type C1 deficiency and related conditions |
| TWI835747B (zh) | 2017-09-22 | 2024-03-21 | 賓州大學委員會 | 用於治療黏多醣病 ii 型之基因治療 |
| JP2021519581A (ja) | 2018-04-03 | 2021-08-12 | ストライドバイオ，インコーポレイテッド | 抗体を回避するウイルスベクター |
| AU2019247191A1 (en) | 2018-04-03 | 2020-10-15 | Ginkgo Bioworks, Inc. | Virus vectors for targeting ophthalmic tissues |
| SG11202009452WA (en) | 2018-04-03 | 2020-10-29 | Stridebio Inc | Antibody-evading virus vectors |
| CA3127336A1 (en) | 2019-01-28 | 2020-08-06 | Cohbar, Inc. | Therapeutic peptides |
| AR118465A1 (es) | 2019-03-21 | 2021-10-06 | Stridebio Inc | Vectores de virus adenoasociados recombinantes |
| PH12021552661A1 (en) * | 2019-04-24 | 2023-02-27 | Univ Oregon Health & Science | Promoter sequence and related products and uses thereof |
| CA3157700A1 (en) | 2019-10-17 | 2021-04-22 | Stridebio, Inc. | Adeno-associated viral vectors for treatment of niemann-pick disease type c |
| JP2023532923A (ja) * | 2020-06-30 | 2023-08-01 | チルドレンズ ナショナル メディカル センター | 骨格筋線維の修復を改善するためのリコンビナントヒト酸性スフィンゴミエリナーゼの使用 |
| CA3189878A1 (en) | 2020-08-19 | 2022-02-24 | Colin O'BANION | Adeno-associated virus vectors for treatment of rett syndrome |
| CA3205351A1 (en) * | 2021-02-01 | 2022-08-04 | James M. Wilson | Compositions and methods for treatment of niemann pick type a disease |
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| NL154598B (nl) | 1970-11-10 | 1977-09-15 | Organon Nv | Werkwijze voor het aantonen en bepalen van laagmoleculire verbindingen en van eiwitten die deze verbindingen specifiek kunnen binden, alsmede testverpakking. |
| US3817837A (en) | 1971-05-14 | 1974-06-18 | Syva Corp | Enzyme amplification assay |
| US3939350A (en) | 1974-04-29 | 1976-02-17 | Board Of Trustees Of The Leland Stanford Junior University | Fluorescent immunoassay employing total reflection for activation |
| US3996345A (en) | 1974-08-12 | 1976-12-07 | Syva Company | Fluorescence quenching with immunological pairs in immunoassays |
| US4275149A (en) | 1978-11-24 | 1981-06-23 | Syva Company | Macromolecular environment control in specific receptor assays |
| US4277437A (en) | 1978-04-05 | 1981-07-07 | Syva Company | Kit for carrying out chemically induced fluorescence immunoassay |
| US4366241A (en) | 1980-08-07 | 1982-12-28 | Syva Company | Concentrating zone method in heterogeneous immunoassays |
| DE3424893A1 (de) | 1984-07-06 | 1986-02-06 | Agfa-Gevaert Ag, 5090 Leverkusen | Photographisches silberhalogenidaufzeichnungsmaterial |
| US5143854A (en) | 1989-06-07 | 1992-09-01 | Affymax Technologies N.V. | Large scale photolithographic solid phase synthesis of polypeptides and receptor binding screening thereof |
| US6040138A (en) | 1995-09-15 | 2000-03-21 | Affymetrix, Inc. | Expression monitoring by hybridization to high density oligonucleotide arrays |
| US5773278A (en) | 1991-05-03 | 1998-06-30 | Mount Sinai Medical Center | Acid sphingomyelinase gene |
| US5412087A (en) | 1992-04-24 | 1995-05-02 | Affymax Technologies N.V. | Spatially-addressable immobilization of oligonucleotides and other biological polymers on surfaces |
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| JP3532566B2 (ja) | 1993-06-24 | 2004-05-31 | エル． グラハム，フランク | 遺伝子治療のためのアデノウイルスベクター |
| CN1263864C (zh) | 1993-10-25 | 2006-07-12 | 坎吉公司 | 重组腺病毒载体及其使用方法 |
| DK0733103T3 (da) | 1993-11-09 | 2004-07-12 | Univ Johns Hopkins | Fremstilling af höje titre af rekombinante AAV vektorer |
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| US5631734A (en) | 1994-02-10 | 1997-05-20 | Affymetrix, Inc. | Method and apparatus for detection of fluorescently labeled materials |
| US7252989B1 (en) | 1994-04-04 | 2007-08-07 | Board Of Regents, The University Of Texas System | Adenovirus supervector system |
| ATE386131T1 (de) | 1994-04-13 | 2008-03-15 | Univ Rockefeller | Aav-vermittelte überbringung von dna in zellen des nervensystems |
| US5795716A (en) | 1994-10-21 | 1998-08-18 | Chee; Mark S. | Computer-aided visualization and analysis system for sequence evaluation |
| AU734290B2 (en) | 1997-10-29 | 2001-06-07 | Genzyme Corporation | Compositions and methods for treating lysosomal storage disease |
| US6544785B1 (en) | 1998-09-14 | 2003-04-08 | Mount Sinai School Of Medicine Of New York University | Helper-free rescue of recombinant negative strand RNA viruses |
| ATE360082T1 (de) | 1999-11-16 | 2007-05-15 | Genzyme Corp | Vektoren und transgene mit regulatorischen elementen zur genverabreichung in leber |
| US6582692B1 (en) * | 1999-11-17 | 2003-06-24 | Avigen, Inc. | Recombinant adeno-associated virus virions for the treatment of lysosomal disorders |
| JP2003533437A (ja) * | 2000-02-17 | 2003-11-11 | ジェンザイム・コーポレイション | 遺伝子デリバリーのための門戸としての肺の遺伝的修飾 |
| WO2001060377A2 (en) * | 2000-02-17 | 2001-08-23 | Genzyme Corporation | Methods for treatment of lysosomal storage diseases using biphosphonates |
| US20040204379A1 (en) * | 2000-06-19 | 2004-10-14 | Cheng Seng H. | Combination enzyme replacement, gene therapy and small molecule therapy for lysosomal storage diseases |
| CA2361462A1 (en) * | 2001-11-07 | 2003-05-08 | Katherine A. High | Induction of tolerance to a therapeutic polypeptide |
| JP2006503808A (ja) * | 2002-06-14 | 2006-02-02 | イエダ リサーチ アンド デベロップメント カンパニー リミテッド | 神経保護及び神経再生用の抗原提示細胞 |
| AU2003265855A1 (en) * | 2002-08-28 | 2004-03-19 | University Of Florida | Modified aav |
| US20040258666A1 (en) * | 2003-05-01 | 2004-12-23 | Passini Marco A. | Gene therapy for neurometabolic disorders |
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2007
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- 2007-02-08 PT PT07763560T patent/PT1986661T/pt unknown
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- 2007-02-08 WO PCT/US2007/003388 patent/WO2007092563A2/en not_active Ceased
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| US20090117156A1 (en) | 2009-05-07 |
| LT1986661T (lt) | 2018-12-10 |
| WO2007092563A2 (en) | 2007-08-16 |
| JP2009526067A (ja) | 2009-07-16 |
| US20230287366A1 (en) | 2023-09-14 |
| WO2007092563A3 (en) | 2007-11-22 |
| IL193165B (en) | 2018-04-30 |
| EP1986661A4 (en) | 2012-04-25 |
| US20200080066A1 (en) | 2020-03-12 |
| PL1986661T3 (pl) | 2019-02-28 |
| HUE041928T2 (hu) | 2019-06-28 |
| MX360595B (es) | 2018-11-09 |
| MX2018008355A (es) | 2021-06-15 |
| CY1121380T1 (el) | 2020-05-29 |
| EP3456331B1 (en) | 2021-05-26 |
| EP1986661B1 (en) | 2018-08-29 |
| BRPI0707590A2 (pt) | 2011-05-10 |
| JP5881641B2 (ja) | 2016-03-09 |
| AR059371A1 (es) | 2008-03-26 |
| PT1986661T (pt) | 2018-12-05 |
| MX2018013684A (es) | 2021-06-15 |
| SI1986661T1 (sl) | 2018-12-31 |
| JP2013166777A (ja) | 2013-08-29 |
| JP5706602B2 (ja) | 2015-04-22 |
| EP3456331A1 (en) | 2019-03-20 |
| IL258587A (en) | 2018-06-28 |
| EP1986661A2 (en) | 2008-11-05 |
| DK1986661T3 (da) | 2019-01-02 |
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