BRPI0707590A2 - terapia gÊnica para a doenÇa de niemann-pick do tipo a - Google Patents
terapia gÊnica para a doenÇa de niemann-pick do tipo a Download PDFInfo
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- BRPI0707590A2 BRPI0707590A2 BRPI0707590-1A BRPI0707590A BRPI0707590A2 BR PI0707590 A2 BRPI0707590 A2 BR PI0707590A2 BR PI0707590 A BRPI0707590 A BR PI0707590A BR PI0707590 A2 BRPI0707590 A2 BR PI0707590A2
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- brain
- aav2
- vector
- transgene
- mammalian
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Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
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| US77162806P | 2006-02-08 | 2006-02-08 | |
| US60/771,628 | 2006-02-08 | ||
| US77236006P | 2006-02-09 | 2006-02-09 | |
| US60/772,360 | 2006-02-09 | ||
| PCT/US2007/003388 WO2007092563A2 (en) | 2006-02-08 | 2007-02-08 | Gene therapy for niemann-pick disease type a |
Publications (1)
| Publication Number | Publication Date |
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| BRPI0707590A2 true BRPI0707590A2 (pt) | 2011-05-10 |
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| BRPI0707590-1A BRPI0707590A2 (pt) | 2006-02-08 | 2007-02-08 | terapia gÊnica para a doenÇa de niemann-pick do tipo a |
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| SI (1) | SI1986661T1 (OSRAM) |
| WO (1) | WO2007092563A2 (OSRAM) |
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| CA2606490C (en) | 2005-05-02 | 2018-02-06 | Genzyme Corporation | Gene therapy for spinal cord disorders |
| ES2887076T3 (es) | 2005-05-02 | 2021-12-21 | Genzyme Corp | Terapia génica para trastornos neurometabólicos |
| PL3252161T3 (pl) * | 2007-06-06 | 2022-03-07 | Genzyme Corporation | Terapia genowa dla lizosomalnych chorób spichrzeniowych |
| WO2010138263A2 (en) | 2009-05-28 | 2010-12-02 | University Of Massachusetts | Novel aav 's and uses thereof |
| DK2826860T3 (en) * | 2010-04-23 | 2018-12-03 | Univ Massachusetts | CNS targeting AAV vectors and methods for their use |
| US20130090374A1 (en) * | 2011-04-20 | 2013-04-11 | Miguel Sena-Esteves | Methods for the treatment of tay-sachs disease, sandhoff disease, and gm1-gangliosidosis |
| EP3622821A1 (en) * | 2013-05-15 | 2020-03-18 | Regents of the University of Minnesota | Adeno-associated virus mediated gene transfer to the central nervous system |
| EP3209311B1 (en) | 2014-10-21 | 2024-03-06 | University of Massachusetts | Recombinant aav variants and uses thereof |
| CA2979495A1 (en) * | 2015-03-17 | 2016-09-22 | Vrije Universiteit Brussel | Optimized liver-specific expression systems for fviii and fix |
| GB201508025D0 (en) | 2015-05-11 | 2015-06-24 | Ucl Business Plc | Fabry disease gene therapy |
| IL262211B2 (en) | 2016-04-15 | 2024-01-01 | Univ Pennsylvania | Gene therapy for treating mucopolysaccharidosis type ii |
| EP3519431A1 (en) | 2016-09-28 | 2019-08-07 | Cohbar Inc. | Therapeutic mots-c related peptides |
| AU2017341849B2 (en) | 2016-10-13 | 2024-03-21 | University Of Massachusetts | AAV capsid designs |
| US20190269797A1 (en) * | 2016-11-04 | 2019-09-05 | The Children's Hospital Of Philadelphia | Gene transfer compositions, methods and uses for treating neurodegenerative diseases |
| WO2018156892A1 (en) | 2017-02-23 | 2018-08-30 | Adrx, Inc. | Peptide inhibitors of transcription factor aggregation |
| WO2018226992A1 (en) | 2017-06-07 | 2018-12-13 | Adrx, Inc. | Tau aggregation inhibitors |
| US12116577B2 (en) | 2017-06-20 | 2024-10-15 | The United States Of America, As Represented By The Secretary, Department Of Health And Human Services | Codon-optimized human NPC1 genes for the treatment of Niemann-Pick type C1 deficiency and related conditions |
| TWI835747B (zh) | 2017-09-22 | 2024-03-21 | 賓州大學委員會 | 用於治療黏多醣病 ii 型之基因治療 |
| JP2021519581A (ja) | 2018-04-03 | 2021-08-12 | ストライドバイオ，インコーポレイテッド | 抗体を回避するウイルスベクター |
| AU2019247191A1 (en) | 2018-04-03 | 2020-10-15 | Ginkgo Bioworks, Inc. | Virus vectors for targeting ophthalmic tissues |
| SG11202009452WA (en) | 2018-04-03 | 2020-10-29 | Stridebio Inc | Antibody-evading virus vectors |
| CA3127336A1 (en) | 2019-01-28 | 2020-08-06 | Cohbar, Inc. | Therapeutic peptides |
| AR118465A1 (es) | 2019-03-21 | 2021-10-06 | Stridebio Inc | Vectores de virus adenoasociados recombinantes |
| PH12021552661A1 (en) * | 2019-04-24 | 2023-02-27 | Univ Oregon Health & Science | Promoter sequence and related products and uses thereof |
| CA3157700A1 (en) | 2019-10-17 | 2021-04-22 | Stridebio, Inc. | Adeno-associated viral vectors for treatment of niemann-pick disease type c |
| JP2023532923A (ja) * | 2020-06-30 | 2023-08-01 | チルドレンズ ナショナル メディカル センター | 骨格筋線維の修復を改善するためのリコンビナントヒト酸性スフィンゴミエリナーゼの使用 |
| CA3189878A1 (en) | 2020-08-19 | 2022-02-24 | Colin O'BANION | Adeno-associated virus vectors for treatment of rett syndrome |
| CA3205351A1 (en) * | 2021-02-01 | 2022-08-04 | James M. Wilson | Compositions and methods for treatment of niemann pick type a disease |
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| DE3424893A1 (de) | 1984-07-06 | 1986-02-06 | Agfa-Gevaert Ag, 5090 Leverkusen | Photographisches silberhalogenidaufzeichnungsmaterial |
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2007
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| LT1986661T (lt) | 2018-12-10 |
| WO2007092563A2 (en) | 2007-08-16 |
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| US20230287366A1 (en) | 2023-09-14 |
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| US20200080066A1 (en) | 2020-03-12 |
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| MX2018008355A (es) | 2021-06-15 |
| CY1121380T1 (el) | 2020-05-29 |
| EP3456331B1 (en) | 2021-05-26 |
| EP1986661B1 (en) | 2018-08-29 |
| JP5881641B2 (ja) | 2016-03-09 |
| AR059371A1 (es) | 2008-03-26 |
| PT1986661T (pt) | 2018-12-05 |
| MX2018013684A (es) | 2021-06-15 |
| SI1986661T1 (sl) | 2018-12-31 |
| JP2013166777A (ja) | 2013-08-29 |
| JP5706602B2 (ja) | 2015-04-22 |
| EP3456331A1 (en) | 2019-03-20 |
| IL258587A (en) | 2018-06-28 |
| EP1986661A2 (en) | 2008-11-05 |
| DK1986661T3 (da) | 2019-01-02 |
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