CN116194154A - 使用aav载体的plakophilin-2(pkp2)基因疗法 - Google Patents

使用aav载体的plakophilin-2(pkp2)基因疗法 Download PDF

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Publication number
CN116194154A
CN116194154A CN202180058096.5A CN202180058096A CN116194154A CN 116194154 A CN116194154 A CN 116194154A CN 202180058096 A CN202180058096 A CN 202180058096A CN 116194154 A CN116194154 A CN 116194154A
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vector
polynucleotide
ser
gly
leu
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C·D·赫尔佐格
C·B·萨克拉门多
R·普拉巴卡尔
D·里克斯
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Spaceship Seven LLC
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CN202180058096.5A 2020-08-07 2021-08-09 使用aav载体的plakophilin-2(pkp2)基因疗法 Pending CN116194154A (zh)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063063032P 2020-08-07 2020-08-07
US63/063,032 2020-08-07
PCT/US2021/045220 WO2022032226A1 (en) 2020-08-07 2021-08-09 Plakophilin-2 (pkp2) gene therapy using aav vector

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CN116194154A true CN116194154A (zh) 2023-05-30

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US (4) US20220168447A1 (https=)
EP (1) EP4192487A4 (https=)
JP (1) JP2023538519A (https=)
KR (1) KR20230043869A (https=)
CN (1) CN116194154A (https=)
AU (1) AU2021320902A1 (https=)
BR (1) BR112023001852A2 (https=)
CA (1) CA3185267A1 (https=)
IL (1) IL300263A (https=)
MX (1) MX2023001615A (https=)
WO (1) WO2022032226A1 (https=)

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