CN116064539A - 用于诱导父本ube3a表达的寡核苷酸 - Google Patents

用于诱导父本ube3a表达的寡核苷酸 Download PDF

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CN116064539A
CN116064539A CN202211275954.4A CN202211275954A CN116064539A CN 116064539 A CN116064539 A CN 116064539A CN 202211275954 A CN202211275954 A CN 202211275954A CN 116064539 A CN116064539 A CN 116064539A
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oligonucleotide
nucleosides
ube3a
oligonucleotides
lna
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Chinese (zh)
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韦罗妮卡·科斯塔
马伊·黑特耶恩
马里乌斯·赫纳
拉维·姚高希亚
马斯·奥波尔·詹森
克里斯托弗·帕奇
吕克·彼泽森
索伦·韦斯特高·拉斯穆森
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F Hoffmann La Roche AG
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F Hoffmann La Roche AG
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