CN113454222B - 淀粉样前体蛋白(APP)RNAi剂组成物及其使用方法 - Google Patents

淀粉样前体蛋白(APP)RNAi剂组成物及其使用方法 Download PDF

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CN113454222B
CN113454222B CN201980092566.2A CN201980092566A CN113454222B CN 113454222 B CN113454222 B CN 113454222B CN 201980092566 A CN201980092566 A CN 201980092566A CN 113454222 B CN113454222 B CN 113454222B
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nucleotides
strand
app
rnai agent
nucleotide
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CN113454222A (zh
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斯图尔特·米尔斯坦
柯克·布朗
贾亚普拉卡什·奈尔
马丁·迈尔
瓦桑特·贾达夫
马克·基廷
亚当·卡斯托雷诺
帕特里克·哈斯莱特
曼加拉·M·桑达拉潘迪安
凯文·菲茨杰拉德
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Anila Pharmaceuticals
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US201862781774P 2018-12-19 2018-12-19
US62/781,774 2018-12-19
US201962862472P 2019-06-17 2019-06-17
US62/862,472 2019-06-17
US201962928795P 2019-10-31 2019-10-31
US62/928,795 2019-10-31
PCT/US2019/067449 WO2020132227A2 (en) 2018-12-19 2019-12-19 AMYLOID PRECURSOR PROTEIN (APP) RNAi AGENT COMPOSITIONS AND METHODS OF USE THEREOF

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