CN113423725A - 遗传工程化造血干细胞及其用途 - Google Patents

遗传工程化造血干细胞及其用途 Download PDF

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CN113423725A
CN113423725A CN201980070933.9A CN201980070933A CN113423725A CN 113423725 A CN113423725 A CN 113423725A CN 201980070933 A CN201980070933 A CN 201980070933A CN 113423725 A CN113423725 A CN 113423725A
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cell surface
cells
specific cell
lineage
surface antigen
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J.博伦
A.F.拉多维奇-莫雷诺
J.利迪尔德
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Vor Biopharma Inc
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Vor Biopharma Inc
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CN201980070933.9A 2018-08-28 2019-08-28 遗传工程化造血干细胞及其用途 Pending CN113423725A (zh)

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US201862723993P 2018-08-28 2018-08-28
US62/723,993 2018-08-28
US201862728061P 2018-09-06 2018-09-06
US62/728,061 2018-09-06
US201962789440P 2019-01-07 2019-01-07
US62/789,440 2019-01-07
US201962809202P 2019-02-22 2019-02-22
US62/809,202 2019-02-22
PCT/US2019/048662 WO2020047164A1 (en) 2018-08-28 2019-08-28 Genetically engineered hematopoietic stem cells and uses thereof

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Cited By (2)

* Cited by examiner, † Cited by third party
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CN114743598A (zh) * 2022-06-14 2022-07-12 湖南大学 一种基于信息论检测新冠病毒谱系间重组的方法
CN116850210A (zh) * 2023-01-17 2023-10-10 武汉大学 用于治疗急性髓系白血病的成分和方法

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SG11201907870VA (en) 2017-02-28 2019-09-27 Vor Biopharma Inc Compositions and methods for inhibition of lineage specific proteins
CA3110837A1 (en) * 2018-08-28 2020-03-05 Vor Biopharma Inc. Genetically engineered hematopoietic stem cells and uses thereof
CN114423865A (zh) * 2019-05-23 2022-04-29 Vor生物制药股份有限公司 Cd33修饰的组合物和方法
AU2020336211A1 (en) * 2019-08-28 2022-03-10 Vor Biopharma Inc. Compositions and methods for CD123 modification
US20220290160A1 (en) * 2019-08-28 2022-09-15 Vor Biopharma Inc. Compositions and methods for cll1 modification
WO2021081244A1 (en) * 2019-10-22 2021-04-29 Fred Hutchinson Cancer Research Center Base editor-mediated cd33 reduction to selectively protect therapeutic cells
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