CN102947453A - 用于病毒载体纯化的可扩缩生产平台和用于基因治疗中的如此纯化的病毒载体 - Google Patents

用于病毒载体纯化的可扩缩生产平台和用于基因治疗中的如此纯化的病毒载体 Download PDF

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CN102947453A
CN102947453A CN2011800166162A CN201180016616A CN102947453A CN 102947453 A CN102947453 A CN 102947453A CN 2011800166162 A CN2011800166162 A CN 2011800166162A CN 201180016616 A CN201180016616 A CN 201180016616A CN 102947453 A CN102947453 A CN 102947453A
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aav
particles
factor
vector
vectors
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J.F.赖特
G.屈
B.豪克
K.海
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Childrens Hospital of Philadelphia CHOP
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CN2011800166162A 2010-01-28 2011-01-25 用于病毒载体纯化的可扩缩生产平台和用于基因治疗中的如此纯化的病毒载体 Pending CN102947453A (zh)

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CN109121421A (zh) * 2015-12-11 2019-01-01 宾夕法尼亚州大学信托人 用于治疗家族性高胆固醇血症的基因疗法
CN109152821A (zh) * 2016-03-31 2019-01-04 星火治疗有限公司 基于柱的完全可扩展的rAAV制造工艺
CN109790549A (zh) * 2016-07-21 2019-05-21 星火治疗有限公司 生产高产重组腺相关病毒(rAAV)载体可扩展高回收法及其产生的重组腺相关病毒(rAAV)载体
CN111566220A (zh) * 2017-11-08 2020-08-21 阿维克斯公司 制备病毒载体的手段和方法及其用途
US11554147B2 (en) 2017-02-20 2023-01-17 The Trustees Of The University Of Pennsylvania Gene therapy for treating familial hypercholesterolemia
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