CA3022611A1 - Genetically engineered cells and methods of making the same - Google Patents

Genetically engineered cells and methods of making the same Download PDF

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Publication number
CA3022611A1
CA3022611A1 CA3022611A CA3022611A CA3022611A1 CA 3022611 A1 CA3022611 A1 CA 3022611A1 CA 3022611 A CA3022611 A CA 3022611A CA 3022611 A CA3022611 A CA 3022611A CA 3022611 A1 CA3022611 A1 CA 3022611A1
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Canada
Prior art keywords
seq
domain
cells
composition
grna molecule
Prior art date
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Application number
CA3022611A
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English (en)
French (fr)
Inventor
Blythe SATHER
G. Grant Welstead
David A. Bumcrot
Ari E. FRIEDLAND
Jon Jones
Morgan L. Maeder
Chris NYE
Eugenio Marco Rubio
Ruth SALMON
Current Assignee (The listed assignees may be inaccurate. Google has not performed a legal analysis and makes no representation or warranty as to the accuracy of the list.)
Juno Therapeutics Inc
Editas Medicine Inc
Original Assignee
Juno Therapeutics Inc
Editas Medicine Inc
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Application filed by Juno Therapeutics Inc, Editas Medicine Inc filed Critical Juno Therapeutics Inc
Publication of CA3022611A1 publication Critical patent/CA3022611A1/en
Pending legal-status Critical Current

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    • A61K48/005—Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy characterised by an aspect of the 'active' part of the composition delivered, i.e. the nucleic acid delivered
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