AU2017363369A1 - Methods for modulating RNA splicing - Google Patents

Methods for modulating RNA splicing Download PDF

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Publication number
AU2017363369A1
AU2017363369A1 AU2017363369A AU2017363369A AU2017363369A1 AU 2017363369 A1 AU2017363369 A1 AU 2017363369A1 AU 2017363369 A AU2017363369 A AU 2017363369A AU 2017363369 A AU2017363369 A AU 2017363369A AU 2017363369 A1 AU2017363369 A1 AU 2017363369A1
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AU
Australia
Prior art keywords
amino
8alkyl
salkyl
hydroxy
heterocyclyl
Prior art date
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Abandoned
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AU2017363369A
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Inventor
Anuradha Bhattacharyya
Amal DAKKA
Kerstin EFFENBERGER
Vijayalakshmi GABBETA
Wencheng Li
Nikolai Naryshkin
Christopher Trotta
Kari WIEDINGER
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PTC Therapeutics Inc
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PTC Therapeutics Inc
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Publication of AU2017363369A1 publication Critical patent/AU2017363369A1/en
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AU2017363369A 2016-11-28 2017-11-27 Methods for modulating RNA splicing Abandoned AU2017363369A1 (en)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201662426619P 2016-11-28 2016-11-28
US62/426,619 2016-11-28
PCT/US2017/063323 WO2018098446A1 (en) 2016-11-28 2017-11-27 Methods for modulating rna splicing

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AU2017363369A1 true AU2017363369A1 (en) 2019-05-30

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AU2017363369A Abandoned AU2017363369A1 (en) 2016-11-28 2017-11-27 Methods for modulating RNA splicing

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US (2) US11702646B2 (enExample)
EP (1) EP3544435A4 (enExample)
JP (2) JP2019535789A (enExample)
CN (1) CN110352007A (enExample)
AU (1) AU2017363369A1 (enExample)
CA (1) CA3043755A1 (enExample)
EA (1) EA201991309A1 (enExample)
MX (1) MX2019005588A (enExample)
WO (1) WO2018098446A1 (enExample)

Families Citing this family (44)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP3310169B1 (en) 2015-05-30 2023-05-17 PTC Therapeutics, Inc. Methods for modulating rna splicing
JP2019535789A (ja) 2016-11-28 2019-12-12 ピーティーシー セラピューティクス，インコーポレーテッド Ｒｎａスプライシングを調節する方法
CN111372611A (zh) 2017-06-14 2020-07-03 Ptc医疗公司 修饰rna剪接的方法
MX2020001425A (es) 2017-08-04 2020-08-06 Skyhawk Therapeutics Inc Metodos y composiciones para modular el empalme.
US20210355509A1 (en) * 2018-08-07 2021-11-18 The Children's Hospital Of Philadelphia Alternative splicing regulation of gene expression and therapeutic methods
AU2019359276A1 (en) * 2018-10-09 2021-04-29 The University Of North Carolina At Chapel Hill Regulated gene editing system
WO2020163248A1 (en) 2019-02-04 2020-08-13 Skyhawk Therapeutics, Inc. Methods and compositions for modulating splicing
WO2020163541A1 (en) 2019-02-05 2020-08-13 Skyhawk Therapeutics, Inc. Methods and compositions for modulating splicing
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