MX2019005588A - Metodos para modular corte y empalme de arn. - Google Patents

Metodos para modular corte y empalme de arn.

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Publication number
MX2019005588A
MX2019005588A MX2019005588A MX2019005588A MX2019005588A MX 2019005588 A MX2019005588 A MX 2019005588A MX 2019005588 A MX2019005588 A MX 2019005588A MX 2019005588 A MX2019005588 A MX 2019005588A MX 2019005588 A MX2019005588 A MX 2019005588A
Authority
MX
Mexico
Prior art keywords
methods
gene
another aspect
intronic
rna transcript
Prior art date
Application number
MX2019005588A
Other languages
English (en)
Spanish (es)
Inventor
Dakka Amal
Bhattacharyya Anuradha
EFFENBERGER Kerstin
Gabbeta Vijayalakshmi
Li Wencheng
Naryshkin Nikolai
Trotta Christopher
WIEDINGER Kari
Original Assignee
Ptc Therapeutics Inc
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Ptc Therapeutics Inc filed Critical Ptc Therapeutics Inc
Publication of MX2019005588A publication Critical patent/MX2019005588A/es

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MX2019005588A 2016-11-28 2017-11-27 Metodos para modular corte y empalme de arn. MX2019005588A (es)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
US201662426619P 2016-11-28 2016-11-28
PCT/US2017/063323 WO2018098446A1 (en) 2016-11-28 2017-11-27 Methods for modulating rna splicing

Publications (1)

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MX2019005588A true MX2019005588A (es) 2019-10-15

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MX2019005588A MX2019005588A (es) 2016-11-28 2017-11-27 Metodos para modular corte y empalme de arn.

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US (2) US11702646B2 (enExample)
EP (1) EP3544435A4 (enExample)
JP (2) JP2019535789A (enExample)
CN (1) CN110352007A (enExample)
AU (1) AU2017363369A1 (enExample)
CA (1) CA3043755A1 (enExample)
EA (1) EA201991309A1 (enExample)
MX (1) MX2019005588A (enExample)
WO (1) WO2018098446A1 (enExample)

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EP3310169B1 (en) 2015-05-30 2023-05-17 PTC Therapeutics, Inc. Methods for modulating rna splicing
AU2017363369A1 (en) 2016-11-28 2019-05-30 Ptc Therapeutics, Inc Methods for modulating RNA splicing
US11608501B2 (en) 2017-06-14 2023-03-21 Ptc Therapeutics, Inc. Methods for modifying RNA splicing
MX2020001425A (es) 2017-08-04 2020-08-06 Skyhawk Therapeutics Inc Metodos y composiciones para modular el empalme.
US20210355509A1 (en) * 2018-08-07 2021-11-18 The Children's Hospital Of Philadelphia Alternative splicing regulation of gene expression and therapeutic methods
CA3113817A1 (en) * 2018-10-09 2020-04-16 The University Of North Carolina At Chapel Hill Regulated gene editing system
CN114007613A (zh) 2019-02-05 2022-02-01 斯基霍克疗法公司 用于调节剪接的方法和组合物
JP7603595B2 (ja) 2019-02-06 2024-12-20 スカイホーク・セラピューティクス・インコーポレーテッド スプライシングを調節するための方法および組成物
US11129829B2 (en) 2019-06-17 2021-09-28 Skyhawk Therapeutics, Inc. Methods for modulating splicing
EP4004213A1 (en) 2019-07-25 2022-06-01 Novartis AG Regulatable expression systems
CN114746550A (zh) * 2019-08-19 2022-07-12 斯托克制药公司 用于调节剪接和蛋白质表达的组合物和方法
AU2020394867A1 (en) 2019-12-02 2022-05-26 Storm Therapeutics Limited Polyheterocyclic compounds as METTL3 inhibitors
IL295542A (en) * 2020-02-12 2022-10-01 Childrens Hospital Philadelphia Compositions and methods for inducible alternative splicing regulation of gene expression
CA3169676A1 (en) 2020-02-28 2021-09-02 Dominic Reynolds Compounds and methods for modulating splicing
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