MX2019005588A - Metodos para modular corte y empalme de arn. - Google Patents

Metodos para modular corte y empalme de arn.

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Publication number
MX2019005588A
MX2019005588A MX2019005588A MX2019005588A MX2019005588A MX 2019005588 A MX2019005588 A MX 2019005588A MX 2019005588 A MX2019005588 A MX 2019005588A MX 2019005588 A MX2019005588 A MX 2019005588A MX 2019005588 A MX2019005588 A MX 2019005588A
Authority
MX
Mexico
Prior art keywords
methods
gene
another aspect
intronic
rna transcript
Prior art date
Application number
MX2019005588A
Other languages
English (en)
Spanish (es)
Inventor
Dakka Amal
Bhattacharyya Anuradha
EFFENBERGER Kerstin
Gabbeta Vijayalakshmi
Li Wencheng
Naryshkin Nikolai
Trotta Christopher
WIEDINGER Kari
Original Assignee
Ptc Therapeutics Inc
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Ptc Therapeutics Inc filed Critical Ptc Therapeutics Inc
Publication of MX2019005588A publication Critical patent/MX2019005588A/es

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MX2019005588A 2016-11-28 2017-11-27 Metodos para modular corte y empalme de arn. MX2019005588A (es)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
US201662426619P 2016-11-28 2016-11-28
PCT/US2017/063323 WO2018098446A1 (en) 2016-11-28 2017-11-27 Methods for modulating rna splicing

Publications (1)

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MX2019005588A true MX2019005588A (es) 2019-10-15

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MX2019005588A MX2019005588A (es) 2016-11-28 2017-11-27 Metodos para modular corte y empalme de arn.

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US (2) US11702646B2 (enExample)
EP (1) EP3544435A4 (enExample)
JP (2) JP2019535789A (enExample)
CN (1) CN110352007A (enExample)
AU (1) AU2017363369A1 (enExample)
CA (1) CA3043755A1 (enExample)
EA (1) EA201991309A1 (enExample)
MX (1) MX2019005588A (enExample)
WO (1) WO2018098446A1 (enExample)

Families Citing this family (44)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP3310169B1 (en) 2015-05-30 2023-05-17 PTC Therapeutics, Inc. Methods for modulating rna splicing
JP2019535789A (ja) 2016-11-28 2019-12-12 ピーティーシー セラピューティクス，インコーポレーテッド Ｒｎａスプライシングを調節する方法
CN111372611A (zh) 2017-06-14 2020-07-03 Ptc医疗公司 修饰rna剪接的方法
MX2020001425A (es) 2017-08-04 2020-08-06 Skyhawk Therapeutics Inc Metodos y composiciones para modular el empalme.
US20210355509A1 (en) * 2018-08-07 2021-11-18 The Children's Hospital Of Philadelphia Alternative splicing regulation of gene expression and therapeutic methods
AU2019359276A1 (en) * 2018-10-09 2021-04-29 The University Of North Carolina At Chapel Hill Regulated gene editing system
WO2020163248A1 (en) 2019-02-04 2020-08-13 Skyhawk Therapeutics, Inc. Methods and compositions for modulating splicing
WO2020163541A1 (en) 2019-02-05 2020-08-13 Skyhawk Therapeutics, Inc. Methods and compositions for modulating splicing
KR102913697B1 (ko) 2019-02-05 2026-01-15 스카이호크 테라퓨틱스, 인코포레이티드 스플라이싱을 조절하는 방법 및 조성물
JP7603594B2 (ja) 2019-02-06 2024-12-20 スカイホーク・セラピューティクス・インコーポレーテッド スプライシングを調節するための方法および組成物
KR102925385B1 (ko) 2019-02-06 2026-02-11 스카이호크 테라퓨틱스, 인코포레이티드 스플라이싱을 조절하는 방법 및 조성물
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