CN110352007A - 用于调节rna剪接的方法 - Google Patents

用于调节rna剪接的方法 Download PDF

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Publication number
CN110352007A
CN110352007A CN201780084649.8A CN201780084649A CN110352007A CN 110352007 A CN110352007 A CN 110352007A CN 201780084649 A CN201780084649 A CN 201780084649A CN 110352007 A CN110352007 A CN 110352007A
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alkyl
amino
radical
alkoxy
hydroxy
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Chinese (zh)
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阿努拉哈·巴特查里亚
阿迈尔·达卡
克斯廷·埃芬贝格尔
维加亚拉克什米·加贝塔
李文成
尼柯莱·纳雷什金
克里斯多佛·特罗塔
卡利·韦丁格
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Ptc Medical Co
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Ptc Medical Co
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CN201780084649.8A 2016-11-28 2017-11-27 用于调节rna剪接的方法 Pending CN110352007A (zh)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201662426619P 2016-11-28 2016-11-28
US62/426,619 2016-11-28
PCT/US2017/063323 WO2018098446A1 (en) 2016-11-28 2017-11-27 Methods for modulating rna splicing

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CN110352007A true CN110352007A (zh) 2019-10-18

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US (2) US11702646B2 (enExample)
EP (1) EP3544435A4 (enExample)
JP (2) JP2019535789A (enExample)
CN (1) CN110352007A (enExample)
AU (1) AU2017363369A1 (enExample)
CA (1) CA3043755A1 (enExample)
EA (1) EA201991309A1 (enExample)
MX (1) MX2019005588A (enExample)
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Cited By (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN113604566A (zh) * 2021-07-13 2021-11-05 中山大学孙逸仙纪念医院 lncRNA BCYRN1在膀胱癌预后、治疗中的应用
WO2023143425A1 (zh) * 2022-01-25 2023-08-03 上海魁特迪生物科技有限公司 改善认知障碍的方法

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* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP3310169B1 (en) 2015-05-30 2023-05-17 PTC Therapeutics, Inc. Methods for modulating rna splicing
AU2017363369A1 (en) 2016-11-28 2019-05-30 Ptc Therapeutics, Inc Methods for modulating RNA splicing
US11608501B2 (en) 2017-06-14 2023-03-21 Ptc Therapeutics, Inc. Methods for modifying RNA splicing
MX2020001425A (es) 2017-08-04 2020-08-06 Skyhawk Therapeutics Inc Metodos y composiciones para modular el empalme.
US20210355509A1 (en) * 2018-08-07 2021-11-18 The Children's Hospital Of Philadelphia Alternative splicing regulation of gene expression and therapeutic methods
CA3113817A1 (en) * 2018-10-09 2020-04-16 The University Of North Carolina At Chapel Hill Regulated gene editing system
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