TW201740945A - 治療法布裡病之給藥方案 - Google Patents
治療法布裡病之給藥方案 Download PDFInfo
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- TW201740945A TW201740945A TW106126844A TW106126844A TW201740945A TW 201740945 A TW201740945 A TW 201740945A TW 106126844 A TW106126844 A TW 106126844A TW 106126844 A TW106126844 A TW 106126844A TW 201740945 A TW201740945 A TW 201740945A
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- gal
- agalsidase
- alpha
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- migalastat
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Classifications
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- A61K47/06—Organic compounds, e.g. natural or synthetic hydrocarbons, polyolefins, mineral oil, petrolatum or ozokerite
- A61K47/22—Heterocyclic compounds, e.g. ascorbic acid, tocopherol or pyrrolidones
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- A61K38/16—Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof
- A61K38/43—Enzymes; Proenzymes; Derivatives thereof
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- A61K31/33—Heterocyclic compounds
- A61K31/395—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins
- A61K31/435—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins having six-membered rings with one nitrogen as the only ring hetero atom
- A61K31/44—Non condensed pyridines; Hydrogenated derivatives thereof
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- A—HUMAN NECESSITIES
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- A61P3/00—Drugs for disorders of the metabolism
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- A—HUMAN NECESSITIES
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- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P9/00—Drugs for disorders of the cardiovascular system
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- C—CHEMISTRY; METALLURGY
- C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
- C12Y—ENZYMES
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- A—HUMAN NECESSITIES
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Landscapes
- Health & Medical Sciences (AREA)
- Life Sciences & Earth Sciences (AREA)
- Chemical & Material Sciences (AREA)
- General Health & Medical Sciences (AREA)
- Medicinal Chemistry (AREA)
- Veterinary Medicine (AREA)
- Public Health (AREA)
- Pharmacology & Pharmacy (AREA)
- Animal Behavior & Ethology (AREA)
- Epidemiology (AREA)
- Engineering & Computer Science (AREA)
- Bioinformatics & Cheminformatics (AREA)
- Chemical Kinetics & Catalysis (AREA)
- General Chemical & Material Sciences (AREA)
- Organic Chemistry (AREA)
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- Wood Science & Technology (AREA)
- Genetics & Genomics (AREA)
- Hematology (AREA)
- Zoology (AREA)
- Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
- Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
- Medicinal Preparation (AREA)
- Hydrogenated Pyridines (AREA)
Applications Claiming Priority (3)
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| US201161451798P | 2011-03-11 | 2011-03-11 | |
| US201161578201P | 2011-12-20 | 2011-12-20 | |
| US201261596165P | 2012-02-07 | 2012-02-07 |
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| TW201740945A true TW201740945A (zh) | 2017-12-01 |
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| TW101108345A TWI624258B (zh) | 2011-03-11 | 2012-03-12 | 治療法布裡病之給藥方案 |
| TW106126844A TW201740945A (zh) | 2011-03-11 | 2012-03-12 | 治療法布裡病之給藥方案 |
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| TW105118425A TWI624259B (zh) | 2011-03-11 | 2012-03-12 | 治療法布裡病之給藥方案 |
| TW101108345A TWI624258B (zh) | 2011-03-11 | 2012-03-12 | 治療法布裡病之給藥方案 |
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| EP (2) | EP2683382B1 (OSRAM) |
| JP (5) | JP2014528901A (OSRAM) |
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| CN (2) | CN107088225A (OSRAM) |
| AU (6) | AU2012229330B2 (OSRAM) |
| CA (1) | CA2829947C (OSRAM) |
| CL (1) | CL2013002601A1 (OSRAM) |
| EA (1) | EA031874B1 (OSRAM) |
| ES (1) | ES2807502T3 (OSRAM) |
| HK (1) | HK1242998A1 (OSRAM) |
| MX (1) | MX2013010446A (OSRAM) |
| SG (2) | SG10201604757RA (OSRAM) |
| TW (3) | TWI624259B (OSRAM) |
| WO (1) | WO2012125402A2 (OSRAM) |
| ZA (1) | ZA201306735B (OSRAM) |
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| FI3457135T3 (fi) | 2006-05-16 | 2025-03-08 | Amicus Therapeutics Inc | Fabryn taudin hoitovaihtoehtoja |
| HUE026543T2 (hu) | 2008-02-12 | 2016-06-28 | Amicus Therapeutics Inc | Eljárás betegségek gyógyászati chaperonnal történõ kezelésére adott válasz elõrejelzésére |
| UY34317A (es) | 2011-09-12 | 2013-02-28 | Genzyme Corp | Anticuerpo antireceptor de célula T (alfa)/ß |
| US9790268B2 (en) | 2012-09-12 | 2017-10-17 | Genzyme Corporation | Fc containing polypeptides with altered glycosylation and reduced effector function |
| AU2014249224B2 (en) | 2013-03-11 | 2019-01-17 | Genzyme Corporation | Site-specific antibody-drug conjugation through glycoengineering |
| AU2015216909B2 (en) * | 2014-02-17 | 2017-07-20 | Glaxosmithkline Intellectual Property Development Limited | Microbiological process |
| EP3129067B1 (en) | 2014-03-19 | 2023-01-04 | Genzyme Corporation | Site-specific glycoengineering of targeting moieties |
| US9675627B2 (en) * | 2014-04-14 | 2017-06-13 | Amicus Therapeutics, Inc. | Dosing regimens for treating and/or preventing cerebral amyloidoses |
| GB201508025D0 (en) * | 2015-05-11 | 2015-06-24 | Ucl Business Plc | Fabry disease gene therapy |
| EP3335126A4 (en) | 2015-08-11 | 2019-05-01 | Cognoa, Inc. | METHOD AND DEVICE FOR DETERMINING DEVELOPMENT PROGRESS WITH ARTIFICIAL INTELLIGENCE AND USER ENTRY |
| US11972336B2 (en) | 2015-12-18 | 2024-04-30 | Cognoa, Inc. | Machine learning platform and system for data analysis |
| WO2017165164A1 (en) * | 2016-03-22 | 2017-09-28 | Amicus Therapeutics, Inc. | Methods of treating fabry disease in patients having the g9331a mutation in the gla gene |
| CA3031249A1 (en) * | 2016-07-19 | 2018-01-25 | Amicus Therapeutics, Inc. | Treatment of fabry disease in ert-naive and ert-experienced patients |
| CN110192252A (zh) | 2016-11-14 | 2019-08-30 | 科格诺亚公司 | 用于评估发育状况并提供覆盖度和可靠性控制的方法和装置 |
| EP3580700A4 (en) * | 2017-02-09 | 2020-11-18 | Cognoa, Inc. | PLATFORM AND SYSTEM FOR DIGITAL PERSONALIZED MEDICINE |
| BR112019025083B1 (pt) | 2017-05-30 | 2022-08-09 | Amicus Therapeutics, Inc | Métodos de tratamento de pacientes portadores de fabry com insuficiência renal |
| TWI795408B (zh) * | 2017-05-30 | 2023-03-11 | 美商阿米庫斯醫療股份有限公司 | 治療有腎損傷的法布里患者的方法 |
| JP7066157B2 (ja) | 2017-06-14 | 2022-05-13 | 学校法人 明治薬科大学 | ファブリー病治療用医薬の組合せ物及びその利用 |
| CA3090496C (en) * | 2018-02-06 | 2024-03-26 | Amicus Therapeutics, Inc. | Use of migalastat for treating fabry disease in pregnant patients |
| PL3840753T3 (pl) * | 2018-08-20 | 2025-01-20 | Amicus Therapeutics, Inc. | Migalastat do zastosowania w sposobach leczenia choroby fabry'ego u pacjentów mających mutację w genie gla |
| KR102785528B1 (ko) | 2019-03-22 | 2025-03-21 | 코그노아, 인크. | 개인 맞춤식 디지털 치료 방법 및 디바이스 |
| AU2020253455A1 (en) | 2019-04-03 | 2021-11-04 | Genzyme Corporation | Anti-alpha beta TCR binding polypeptides with reduced fragmentation |
| AR120055A1 (es) * | 2019-06-11 | 2022-02-02 | Amicus Therapeutics Inc | Métodos para tratar la enfermedad de fabry en pacientes que tienen insuficiencia renal |
| CA3147055A1 (en) | 2019-08-07 | 2021-02-11 | Elfrida Benjamin | Methods of treating fabry disease in patients having a mutation in the gla gene |
| US11623916B2 (en) | 2020-12-16 | 2023-04-11 | Amicus Therapeutics, Inc. | Highly purified batches of pharmaceutical grade migalastat and methods of producing the same |
| US20240120050A1 (en) * | 2022-10-07 | 2024-04-11 | Insight Direct Usa, Inc. | Machine learning method for predicting a health outcome of a patient using video and audio analytics |
| US20240197706A1 (en) * | 2022-12-13 | 2024-06-20 | Amicus Therapeutics, Inc. | Methods of improving the pharmacokinetics of migalastat |
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| US4551177A (en) * | 1984-04-23 | 1985-11-05 | National Starch And Chemical Corporation | Compressible starches as binders for tablets or capsules |
| US6274597B1 (en) | 1998-06-01 | 2001-08-14 | Mount Sinai School Of Medicine Of New York University | Method of enhancing lysosomal α-Galactosidase A |
| PT2444102E (pt) * | 2003-01-31 | 2015-09-17 | Sinai School Medicine | Terapia combinada para o tratamento de distúrbios de deficiência proteica |
| US7879354B2 (en) * | 2004-01-13 | 2011-02-01 | Mcneil-Ppc, Inc. | Rapidly disintegrating gelatinous coated tablets |
| CN100457106C (zh) * | 2005-06-15 | 2009-02-04 | 同济大学 | 1-脱氧野尻霉素在制备治疗糖尿病肾病药物中的应用 |
| FI3457135T3 (fi) * | 2006-05-16 | 2025-03-08 | Amicus Therapeutics Inc | Fabryn taudin hoitovaihtoehtoja |
| WO2008121826A2 (en) * | 2007-03-30 | 2008-10-09 | Amicus Therapeutics, Inc. | Method for the treatment of fabry disease using pharmacological chaperones |
| WO2008134628A2 (en) * | 2007-04-26 | 2008-11-06 | Amicus Therapeutics, Inc. | Dosing regimens for the treatment of lysosomal storage diseases using pharmacological chaperones |
| US20100291060A1 (en) * | 2007-08-29 | 2010-11-18 | Shire Human Genetic Therapies, Inc | Subcutaneous administration of alpha-galactosidase a |
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2012
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- 2012-03-12 TW TW101108345A patent/TWI624258B/zh not_active IP Right Cessation
- 2012-03-12 TW TW106126844A patent/TW201740945A/zh unknown
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2013
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2016
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2017
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2018
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2019
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2021
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2022
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2023
- 2023-03-22 JP JP2023045001A patent/JP2023093448A/ja active Pending
- 2023-07-17 US US18/222,745 patent/US20240115708A1/en active Pending
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2024
- 2024-07-31 AU AU2024205251A patent/AU2024205251A1/en active Pending
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