SG11201906147VA - Optimized strategy for exon skipping modifications using crispr/cas9 with triple guide sequences - Google Patents

Optimized strategy for exon skipping modifications using crispr/cas9 with triple guide sequences

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Publication number
SG11201906147VA
SG11201906147VA SG11201906147VA SG11201906147VA SG11201906147VA SG 11201906147V A SG11201906147V A SG 11201906147VA SG 11201906147V A SG11201906147V A SG 11201906147VA SG 11201906147V A SG11201906147V A SG 11201906147VA SG 11201906147V A SG11201906147V A SG 11201906147VA
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Singapore
Prior art keywords
international
cas9
crispr
blvd
pct
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SG11201906147VA
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English (en)
Inventor
Leonela Amoasii
Eric Olson
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Univ Texas
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Publication of SG11201906147VA publication Critical patent/SG11201906147VA/en

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SG11201906147VA 2017-01-05 2018-01-05 Optimized strategy for exon skipping modifications using crispr/cas9 with triple guide sequences SG11201906147VA (en)

Applications Claiming Priority (4)

Application Number Priority Date Filing Date Title
US201762442606P 2017-01-05 2017-01-05
US201762544449P 2017-08-11 2017-08-11
US201762596298P 2017-12-08 2017-12-08
PCT/US2018/012558 WO2018129296A1 (en) 2017-01-05 2018-01-05 Optimized strategy for exon skipping modifications using crispr/cas9 with triple guide sequences

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SG11201906147VA true SG11201906147VA (en) 2019-08-27

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US (1) US20190338311A1 (OSRAM)
EP (1) EP3565897B1 (OSRAM)
JP (1) JP2020503869A (OSRAM)
KR (1) KR102606174B1 (OSRAM)
CN (1) CN110506115A (OSRAM)
AU (1) AU2018205521A1 (OSRAM)
BR (1) BR112019013962A2 (OSRAM)
CA (1) CA3048635A1 (OSRAM)
CL (1) CL2019001882A1 (OSRAM)
CO (1) CO2019008181A2 (OSRAM)
CR (1) CR20190326A (OSRAM)
DK (1) DK3565897T3 (OSRAM)
DO (1) DOP2019000179A (OSRAM)
EC (1) ECSP19056408A (OSRAM)
IL (1) IL267786A (OSRAM)
JO (1) JOP20190166A1 (OSRAM)
MA (1) MA47239A (OSRAM)
MX (1) MX2019008064A (OSRAM)
PE (1) PE20191357A1 (OSRAM)
PH (1) PH12019501561A1 (OSRAM)
SG (1) SG11201906147VA (OSRAM)
WO (1) WO2018129296A1 (OSRAM)

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CN116096394A (zh) * 2020-02-13 2023-05-09 特纳亚治疗股份有限公司 用于治疗心脏病的基因疗法载体
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