RU2727015C2 - Векторы aav, нацеленные на центральную нервную систему - Google Patents

Векторы aav, нацеленные на центральную нервную систему Download PDF

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RU2727015C2
RU2727015C2 RU2017121593A RU2017121593A RU2727015C2 RU 2727015 C2 RU2727015 C2 RU 2727015C2 RU 2017121593 A RU2017121593 A RU 2017121593A RU 2017121593 A RU2017121593 A RU 2017121593A RU 2727015 C2 RU2727015 C2 RU 2727015C2
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aav
nucleic acid
capsid
particle
cells
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RU2017121593A
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RU2017121593A3 (enExample
RU2017121593A (ru
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Стивен Грэй
Томас МАККАУН
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Дзе Юниверсити Оф Норт Каролина Эт Чепел Хилл
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    • A61K31/711Natural deoxyribonucleic acids, i.e. containing only 2'-deoxyriboses attached to adenine, guanine, cytosine or thymine and having 3'-5' phosphodiester links
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RU2017121593A 2014-11-21 2015-11-20 Векторы aav, нацеленные на центральную нервную систему RU2727015C2 (ru)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201462082897P 2014-11-21 2014-11-21
US62/082,897 2014-11-21
US201562218857P 2015-09-15 2015-09-15
US62/218,857 2015-09-15
PCT/US2015/061788 WO2016081811A1 (en) 2014-11-21 2015-11-20 Aav vectors targeted to the central nervous system

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RU2017121593A RU2017121593A (ru) 2018-12-21
RU2017121593A3 RU2017121593A3 (enExample) 2019-12-18
RU2727015C2 true RU2727015C2 (ru) 2020-07-17

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US (4) US10532110B2 (enExample)
EP (2) EP4344741A3 (enExample)
JP (4) JP2017536116A (enExample)
KR (2) KR20240063169A (enExample)
CN (2) CN107532173A (enExample)
AU (2) AU2015349759B2 (enExample)
BR (1) BR112017010447A2 (enExample)
CA (1) CA2967393A1 (enExample)
IL (1) IL252072B (enExample)
MX (1) MX2017006652A (enExample)
RU (1) RU2727015C2 (enExample)
WO (1) WO2016081811A1 (enExample)

Cited By (1)

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RU2821568C1 (ru) * 2023-10-16 2024-06-25 федеральное государственное автономное образовательное учреждение высшего образования "Казанский (Приволжский) федеральный университет" (ФГАОУ ВО КФУ) Рекомбинантная генетическая конструкция, аденоассоциированный вирус для терапии метахроматической лейкодистрофии

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