PT2283134E - Método eficiente para exão (44) saltando distrofia muscular duchenne e meios associados - Google Patents

Método eficiente para exão (44) saltando distrofia muscular duchenne e meios associados Download PDF

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Publication number
PT2283134E
PT2283134E PT97468078T PT09746807T PT2283134E PT 2283134 E PT2283134 E PT 2283134E PT 97468078 T PT97468078 T PT 97468078T PT 09746807 T PT09746807 T PT 09746807T PT 2283134 E PT2283134 E PT 2283134E
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Portugal
Prior art keywords
jumping
examination
muscular dystrophy
efficient method
duchenne muscular
Prior art date
Application number
PT97468078T
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English (en)
Portuguese (pt)
Inventor
Garrit-Jan Boudewijn Van Ommen
Gerardus Johannes Platenburg
Josephus Johannes De Kimpe
Judith Christina Theodora Van Deutekom
Annemieke Aartsma-Rus
Original Assignee
Academisch Ziekenhuis Leiden
Biomarin Technologies B V
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Application filed by Academisch Ziekenhuis Leiden, Biomarin Technologies B V filed Critical Academisch Ziekenhuis Leiden
Publication of PT2283134E publication Critical patent/PT2283134E/pt

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    • C12N15/09—Recombinant DNA-technology
    • C12N15/11—DNA or RNA fragments; Modified forms thereof; Non-coding nucleic acids having a biological activity
    • C12N15/113—Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides; Antisense DNA or RNA; Triplex- forming oligonucleotides; Catalytic nucleic acids, e.g. ribozymes; Nucleic acids used in co-suppression or gene silencing
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    • A61P21/00—Drugs for disorders of the muscular or neuromuscular system
    • A—HUMAN NECESSITIES
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    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P21/00—Drugs for disorders of the muscular or neuromuscular system
    • A61P21/04—Drugs for disorders of the muscular or neuromuscular system for myasthenia gravis
    • A—HUMAN NECESSITIES
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    • C12N2320/30—Special therapeutic applications
    • C12N2320/33—Alteration of splicing

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  • Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
  • Ultra Sonic Daignosis Equipment (AREA)
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PT97468078T 2008-05-14 2009-05-14 Método eficiente para exão (44) saltando distrofia muscular duchenne e meios associados PT2283134E (pt)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
EP08156193A EP2119783A1 (en) 2008-05-14 2008-05-14 Method for efficient exon (44) skipping in Duchenne Muscular Dystrophy and associated means
US12801008P 2008-05-15 2008-05-15

Publications (1)

Publication Number Publication Date
PT2283134E true PT2283134E (pt) 2015-12-24

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PT97468078T PT2283134E (pt) 2008-05-14 2009-05-14 Método eficiente para exão (44) saltando distrofia muscular duchenne e meios associados
PT141799791T PT2813570T (pt) 2008-05-14 2009-05-14 Resumo

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PT141799791T PT2813570T (pt) 2008-05-14 2009-05-14 Resumo

Country Status (17)

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US (4) US9139828B2 (https=)
EP (5) EP2119783A1 (https=)
JP (2) JP5696039B2 (https=)
CN (1) CN102171342B (https=)
AU (5) AU2009247037B2 (https=)
CA (3) CA2723968C (https=)
CY (1) CY1117098T1 (https=)
DK (2) DK2283134T3 (https=)
ES (3) ES2656904T3 (https=)
HR (2) HRP20151053T1 (https=)
HU (2) HUE038111T2 (https=)
IL (6) IL300399B2 (https=)
LT (1) LT2813570T (https=)
NZ (2) NZ600183A (https=)
PL (2) PL2283134T3 (https=)
PT (2) PT2283134E (https=)
WO (1) WO2009139630A2 (https=)

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