JP5696039B2 - デュシェンヌ型筋ジストロフィーにおける効率的なエクソン（４４）スキッピングのための方法及び関連手段 - Google Patents

デュシェンヌ型筋ジストロフィーにおける効率的なエクソン（４４）スキッピングのための方法及び関連手段 Download PDF

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JP5696039B2
JP5696039B2 JP2011509428A JP2011509428A JP5696039B2 JP 5696039 B2 JP5696039 B2 JP 5696039B2 JP 2011509428 A JP2011509428 A JP 2011509428A JP 2011509428 A JP2011509428 A JP 2011509428A JP 5696039 B2 JP5696039 B2 JP 5696039B2
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exon
seq
oligonucleotide
skipping
dystrophin
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JP2011520444A (ja
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ヨハネス プラテンブルク、ジェラルドゥス
ヨハネス プラテンブルク、ジェラルドゥス
キンペ、ヨセフス ヨハネス デ
キンペ、ヨセフス ヨハネス デ
ドイテコム、ジュディス クリスティーナ テオドラ ファン
ドイテコム、ジュディス クリスティーナ テオドラ ファン
オメン、ギャリット − ヤン ボウデヴィン ファン
オメン、ギャリット − ヤン ボウデヴィン ファン
− ラス、アンネミーケ アールツマ
− ラス、アンネミーケ アールツマ
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プロセンサ テクノロジーズ ベー．フェー．
プロセンサ テクノロジーズ ベー．フェー．
アカデミシュ ジーケンハウス ライデン
アカデミシュ ジーケンハウス ライデン
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JP2011509428A 2008-05-14 2009-05-14 デュシェンヌ型筋ジストロフィーにおける効率的なエクソン（４４）スキッピングのための方法及び関連手段 Expired - Fee Related JP5696039B2 (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
EP08156193.8 2008-05-14
EP08156193A EP2119783A1 (en) 2008-05-14 2008-05-14 Method for efficient exon (44) skipping in Duchenne Muscular Dystrophy and associated means
US12801008P 2008-05-15 2008-05-15
US61/128,010 2008-05-15
PCT/NL2009/050258 WO2009139630A2 (en) 2008-05-14 2009-05-14 Method for efficient exon (44) skipping in duchenne muscular dystrophy and associated means

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JP2014135349A Division JP5891268B2 (ja) 2008-05-14 2014-06-30 デュシェンヌ型筋ジストロフィーにおける効率的なエクソン（４４）スキッピングのための方法及び関連手段

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JP2011520444A JP2011520444A (ja) 2011-07-21
JP2011520444A5 JP2011520444A5 (https=) 2012-06-28
JP5696039B2 true JP5696039B2 (ja) 2015-04-08

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JP2014135349A Expired - Fee Related JP5891268B2 (ja) 2008-05-14 2014-06-30 デュシェンヌ型筋ジストロフィーにおける効率的なエクソン（４４）スキッピングのための方法及び関連手段

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US (4) US9139828B2 (https=)
EP (5) EP2119783A1 (https=)
JP (2) JP5696039B2 (https=)
CN (1) CN102171342B (https=)
AU (5) AU2009247037B2 (https=)
CA (3) CA2723968C (https=)
CY (1) CY1117098T1 (https=)
DK (2) DK2283134T3 (https=)
ES (3) ES2656904T3 (https=)
HR (2) HRP20151053T1 (https=)
HU (2) HUE038111T2 (https=)
IL (6) IL300399B2 (https=)
LT (1) LT2813570T (https=)
NZ (2) NZ600183A (https=)
PL (2) PL2283134T3 (https=)
PT (2) PT2283134E (https=)
WO (1) WO2009139630A2 (https=)

Cited By (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
JP2014221058A (ja) * 2008-05-14 2014-11-27 プロセンサ テクノロジーズ ベー．フェー． デュシェンヌ型筋ジストロフィーにおける効率的なエクソン（４４）スキッピングのための方法及び関連手段

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