KR102797860B1 - Ａｌａｓ1 유전자의 발현을 억제하기 위한 조성물 및 방법 - Google Patents

Ａｌａｓ1 유전자의 발현을 억제하기 위한 조성물 및 방법 Download PDF

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KR102797860B1
KR102797860B1 KR1020227024509A KR20227024509A KR102797860B1 KR 102797860 B1 KR102797860 B1 KR 102797860B1 KR 1020227024509 A KR1020227024509 A KR 1020227024509A KR 20227024509 A KR20227024509 A KR 20227024509A KR 102797860 B1 KR102797860 B1 KR 102797860B1
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delete delete
dsrna
porphyria
irna
alas1
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KR20220106851A (ko
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브라이언 베텐코트
케빈 피츠제럴드
윌리엄 퀘르베스
마키코 야스다
로버트 제이. 데스닉
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알닐람 파마슈티칼스 인코포레이티드
이칸 스쿨 오브 메디슨 엣 마운트 시나이
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Application filed by 알닐람 파마슈티칼스 인코포레이티드, 이칸 스쿨 오브 메디슨 엣 마운트 시나이 filed Critical 알닐람 파마슈티칼스 인코포레이티드
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KR1020227024509A 2012-04-10 2013-04-10 Ａｌａｓ1 유전자의 발현을 억제하기 위한 조성물 및 방법 Active KR102797860B1 (ko)

Priority Applications (1)

Application Number Priority Date Filing Date Title
KR1020257012214A KR20250058771A (ko) 2012-04-10 2013-04-10 Ａｌａｓ1 유전자의 발현을 억제하기 위한 조성물 및 방법

Applications Claiming Priority (6)

Application Number Priority Date Filing Date Title
US201261622288P 2012-04-10 2012-04-10
US61/622,288 2012-04-10
US13/835,613 2013-03-15
US13/835,613 US9133461B2 (en) 2012-04-10 2013-03-15 Compositions and methods for inhibiting expression of the ALAS1 gene
KR1020207021475A KR102423326B1 (ko) 2012-04-10 2013-04-10 Ａｌａｓ1 유전자의 발현을 억제하기 위한 조성물 및 방법
PCT/US2013/036006 WO2013155204A2 (en) 2012-04-10 2013-04-10 Compositions and methods for inhibiting expression of the alas1 gene

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KR1020207021475A Division KR102423326B1 (ko) 2012-04-10 2013-04-10 Ａｌａｓ1 유전자의 발현을 억제하기 위한 조성물 및 방법

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