JPWO2022018516A5 - - Google Patents

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Publication number
JPWO2022018516A5
JPWO2022018516A5 JP2023512663A JP2023512663A JPWO2022018516A5 JP WO2022018516 A5 JPWO2022018516 A5 JP WO2022018516A5 JP 2023512663 A JP2023512663 A JP 2023512663A JP 2023512663 A JP2023512663 A JP 2023512663A JP WO2022018516 A5 JPWO2022018516 A5 JP WO2022018516A5
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JP
Japan
Prior art keywords
promoter
sequence
seq
aav
acid sequence
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Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023512663A
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English (en)
Japanese (ja)
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JP2023540464A (ja
Publication date
Priority claimed from CN202010706658.XA external-priority patent/CN113952474A/zh
Priority claimed from CN202010706505.5A external-priority patent/CN113952473A/zh
Application filed filed Critical
Priority claimed from PCT/IB2021/000498 external-priority patent/WO2022018516A1/en
Publication of JP2023540464A publication Critical patent/JP2023540464A/ja
Publication of JPWO2022018516A5 publication Critical patent/JPWO2022018516A5/ja
Pending legal-status Critical Current

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JP2023512663A 2020-07-21 2021-07-20 眼疾患の処置のための組成物および方法 Pending JP2023540464A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
CN202010706658.XA CN113952474A (zh) 2020-07-21 2020-07-21 用于治疗眼部疾病的组合物和方法
CN202010706505.5A CN113952473A (zh) 2020-07-21 2020-07-21 用于治疗眼部疾病的组合物和方法
PCT/IB2021/000498 WO2022018516A1 (en) 2020-07-21 2021-07-20 Composition and method for treating eye diseases

Publications (2)

Publication Number Publication Date
JP2023540464A JP2023540464A (ja) 2023-09-25
JPWO2022018516A5 true JPWO2022018516A5 (enExample) 2024-07-26

Family

ID=79728536

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023512663A Pending JP2023540464A (ja) 2020-07-21 2021-07-20 眼疾患の処置のための組成物および方法

Country Status (7)

Country Link
US (1) US20230295243A1 (enExample)
EP (1) EP4185333A4 (enExample)
JP (1) JP2023540464A (enExample)
CN (1) CN116323949A (enExample)
AU (1) AU2021313839A1 (enExample)
CA (1) CA3186830A1 (enExample)
WO (1) WO2022018516A1 (enExample)

Families Citing this family (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
JP2021506861A (ja) 2017-12-19 2021-02-22 アコーオス インコーポレイテッド 内耳への治療用抗体のaav媒介送達
IL303317A (en) 2020-12-01 2023-07-01 Akouos Inc ANTI-NATURAL ANTIBODY STRUCTURES AND RELATED METHODS FOR THE TREATMENT OF SYMPTOMS ASSOCIATED WITH VESTIBULAR SWANNOMA
CA3243256A1 (en) * 2022-02-02 2023-08-10 Adverum Biotechnologies Inc Methods of treating ocular neovascular diseases using aav2 variants encoding aflibercept
AU2024234810A1 (en) * 2023-03-10 2025-09-04 Adverum Biotechnologies, Inc. Recombinant adeno-associated virus (raav) production in insect cells
WO2025030169A2 (en) * 2023-08-03 2025-02-06 Arcum Vision Inc. Enhanced formulation of polymyxin b/ trimethoprim and rifampin and methods for ophthalmic uses

Family Cites Families (15)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
DK1776460T3 (da) * 2004-08-03 2010-04-12 Geneart Ag Fremgangsmåde til modulering af genekspression ved ændring af CpG-indholdet
DE102004037611B4 (de) * 2004-08-03 2013-10-02 Geneart Ag Induzierbare Genexpression
WO2015109898A1 (zh) * 2014-01-24 2015-07-30 上海恒瑞医药有限公司 VEGF与PDGFRβ双特异性融合蛋白及其用途
CA2977355A1 (en) * 2015-02-20 2016-08-25 University Of Iowa Research Foundation Methods and compositions for treating genetic eye diseases
HUE051953T2 (hu) * 2016-06-16 2021-04-28 Adverum Biotechnologies Inc Idõskori makula degeneráció kezelése AAV2 variáns és aflibercept alkalmazásával
AU2018350990A1 (en) * 2017-10-18 2020-05-21 Regenxbio Inc. Treatment of ocular diseases and metastatic colon cancer with human post-translationally modified VEGF-Trap
AU2018372235B9 (en) * 2017-11-27 2022-03-10 4D Molecular Therapeutics Inc. Adeno-associated virus variant capsids and use for inhibiting angiogenesis
JP2021506861A (ja) * 2017-12-19 2021-02-22 アコーオス インコーポレイテッド 内耳への治療用抗体のaav媒介送達
EP3773743A1 (en) * 2018-04-03 2021-02-17 Stridebio, Inc. Virus vectors for targeting ophthalmic tissues
WO2020102645A1 (en) * 2018-11-16 2020-05-22 Asklepios Biopharmaceutical, Inc. Therapeutic adeno-associated virus for treating pompe disease
WO2021050649A1 (en) * 2019-09-11 2021-03-18 Adverum Biotechnologies, Inc. Methods of treating ocular neovascular diseases using aav2 variants encoding aflibercept
AU2021362770A1 (en) * 2020-10-16 2022-12-08 Gyroscope Therapeutics Limited Nucleic acid encoding an anti-VEGF entity and a negative complement regulator and uses thereof for the treatment of age-related macular degeneration
JP2024516128A (ja) * 2021-04-09 2024-04-12 アビラマックス・バイオファーマ・インコーポレイテッド 眼での導入遺伝子発現のための組成物および方法
WO2022232178A1 (en) * 2021-04-27 2022-11-03 4D Molecular Therapeutics Inc. Compositions and methods for treatment of ocular disease associated with angiogenesis
MX2023014041A (es) * 2021-05-28 2023-12-15 Shanghai Regenelead Therapies Co Ltd Virus adenoasociado recombinante que tiene una capsida variante y su aplicacion.

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