JPWO2022018518A5 - - Google Patents

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Publication number
JPWO2022018518A5
JPWO2022018518A5 JP2023512665A JP2023512665A JPWO2022018518A5 JP WO2022018518 A5 JPWO2022018518 A5 JP WO2022018518A5 JP 2023512665 A JP2023512665 A JP 2023512665A JP 2023512665 A JP2023512665 A JP 2023512665A JP WO2022018518 A5 JPWO2022018518 A5 JP WO2022018518A5
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JP
Japan
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sequence
promoter
seq
aav
identity
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Pending
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JP2023512665A
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English (en)
Japanese (ja)
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JP2023542279A (ja
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Priority claimed from CN202010705069.XA external-priority patent/CN113952472A/zh
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Publication of JP2023542279A publication Critical patent/JP2023542279A/ja
Publication of JPWO2022018518A5 publication Critical patent/JPWO2022018518A5/ja
Pending legal-status Critical Current

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JP2023512665A 2020-07-21 2021-07-20 眼疾患の処置のための組成物および方法 Pending JP2023542279A (ja)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
CN202010705069.XA CN113952472A (zh) 2020-07-21 2020-07-21 用于治疗眼部疾病的组合物和方法
PCT/IB2021/000509 WO2022018518A1 (en) 2020-07-21 2021-07-20 Compositions and methods for the treatment of eye diseases

Publications (2)

Publication Number Publication Date
JP2023542279A JP2023542279A (ja) 2023-10-06
JPWO2022018518A5 true JPWO2022018518A5 (enExample) 2024-07-26

Family

ID=79459955

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023512665A Pending JP2023542279A (ja) 2020-07-21 2021-07-20 眼疾患の処置のための組成物および方法

Country Status (7)

Country Link
US (1) US20230321281A1 (enExample)
EP (1) EP4185319A4 (enExample)
JP (1) JP2023542279A (enExample)
CN (2) CN113952472A (enExample)
AU (1) AU2021312379A1 (enExample)
CA (1) CA3186826A1 (enExample)
WO (1) WO2022018518A1 (enExample)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP4208156A4 (en) * 2020-09-02 2025-01-15 4D Molecular Therapeutics Inc. CODON-OPTIMIZED RPGRRF-15 GENES AND USES THEREOF

Family Cites Families (13)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP1567198A4 (en) * 2002-12-02 2006-05-31 Genvec Inc MATERIALS AND METHOD FOR THE TREATMENT OF EYE DISEASES
CA2878171C (en) * 2012-07-11 2021-04-27 The Trustees Of The University Of Pennsylvania Aav-mediated gene therapy for rpgr x-linked retinal degeneration
JP5971661B2 (ja) * 2012-09-19 2016-08-17 国立大学法人 東京大学 神経活動依存的プロモータ活性を有するdna、及びこれを含むベクター
US11246947B2 (en) * 2013-08-05 2022-02-15 Academisch Ziekenhuis Leiden H.O.D. N. Leids Universitair Medisch Centrum Recombinant AAV-crumbs homologue composition and methods for treating LCA-8 and progressive RP
WO2015082690A1 (en) * 2013-12-06 2015-06-11 INSERM (Institut National de la Santé et de la Recherche Médicale) Methods and pharmaceutical compositions for expressing a polynucleotide of interest in the retinal pigment epithelium of a subject
JP6635942B2 (ja) * 2014-04-15 2020-01-29 アプライド ジェネティック テクノロジーズ コーポレイション 網膜色素変性症gtpアーゼレギュレーター(rpgr)をコードするコドン最適化核酸
EP4600255A3 (en) * 2014-05-02 2025-10-22 Genzyme Corporation Aav vectors for retinal and cns gene therapy
GB201516066D0 (en) * 2015-09-10 2015-10-28 Young & Co Llp D Treatment of retinitis pigmentosa
JP7071332B2 (ja) * 2016-07-29 2022-05-18 ザ リージェンツ オブ ザ ユニバーシティ オブ カリフォルニア 変異カプシドを有するアデノ随伴ウイルスビリオン及びその使用方法
US20200121746A1 (en) * 2017-06-30 2020-04-23 The Regents Of The University Of California Adeno-associated virus virions with variant capsids and methods of use thereof
SG11202006722RA (en) * 2018-01-31 2020-08-28 Res Inst Nationwide Childrens Hospital Gene therapy for limb-girdle muscular dystrophy type 2c
JOP20210054A1 (ar) * 2018-09-21 2020-03-21 Nightstarx Ltd تركيبات وطرق لعلاج التهاب الشبكية الصباغي
EP4087617A4 (en) * 2020-01-10 2024-05-01 Solid Biosciences Inc. VIRAL VECTOR FOR COMBINATION THERAPY

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