JPWO2020006458A5 - - Google Patents

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JPWO2020006458A5
JPWO2020006458A5 JP2020572953A JP2020572953A JPWO2020006458A5 JP WO2020006458 A5 JPWO2020006458 A5 JP WO2020006458A5 JP 2020572953 A JP2020572953 A JP 2020572953A JP 2020572953 A JP2020572953 A JP 2020572953A JP WO2020006458 A5 JPWO2020006458 A5 JP WO2020006458A5
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Japan
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muscle
promoter
weeks
raav
muscle fiber
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JP2020572953A
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JP2021528983A (ja
JP7507697B2 (ja
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JP2020572953A 2018-06-29 2019-06-28 肢帯型筋ジストロフィー2aを治療するための組換えアデノ随伴ウイルス産物及び方法 Active JP7507697B2 (ja)

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JP2024098061A JP2024123110A (ja) 2018-06-29 2024-06-18 肢帯型筋ジストロフィー2aを治療するための組換えアデノ随伴ウイルス産物及び方法

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US201862691934P 2018-06-29 2018-06-29
US62/691,934 2018-06-29
US201962865081P 2019-06-21 2019-06-21
US62/865,081 2019-06-21
PCT/US2019/039893 WO2020006458A1 (en) 2018-06-29 2019-06-28 Recombinant adeno-associated virus products and methods for treating limb girdle muscular dystrophy 2a

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JP2024098061A Division JP2024123110A (ja) 2018-06-29 2024-06-18 肢帯型筋ジストロフィー2aを治療するための組換えアデノ随伴ウイルス産物及び方法

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JP2021528983A JP2021528983A (ja) 2021-10-28
JPWO2020006458A5 true JPWO2020006458A5 (enExample) 2022-06-02
JP7507697B2 JP7507697B2 (ja) 2024-06-28

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JP2024098061A Pending JP2024123110A (ja) 2018-06-29 2024-06-18 肢帯型筋ジストロフィー2aを治療するための組換えアデノ随伴ウイルス産物及び方法

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Country Status (15)

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US (1) US12391928B2 (enExample)
EP (1) EP3814514A1 (enExample)
JP (2) JP7507697B2 (enExample)
KR (1) KR20210028162A (enExample)
CN (1) CN112543810A (enExample)
AU (2) AU2019295779B2 (enExample)
BR (1) BR112020026853A2 (enExample)
CA (1) CA3105216A1 (enExample)
CL (1) CL2020003384A1 (enExample)
CO (1) CO2021000914A2 (enExample)
IL (1) IL279789B1 (enExample)
MX (2) MX2020014119A (enExample)
SG (1) SG11202012715UA (enExample)
TW (1) TWI854984B (enExample)
WO (1) WO2020006458A1 (enExample)

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