JP7577291B6 - Ａａｖカプシド設計 - Google Patents

Ａａｖカプシド設計 Download PDF

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JP7577291B6
JP7577291B6 JP2019520377A JP2019520377A JP7577291B6 JP 7577291 B6 JP7577291 B6 JP 7577291B6 JP 2019520377 A JP2019520377 A JP 2019520377A JP 2019520377 A JP2019520377 A JP 2019520377A JP 7577291 B6 JP7577291 B6 JP 7577291B6
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hsa
mir
aav
raav
transgene
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JP7577291B2 (ja
JP2019530463A (ja
JP2019530463A5 (OSRAM
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ガオ，グワンピン
シュウ，グワンチャオ
タイ，フィリップ
ウェイ，ユカン
ルオ，リー
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ユニバーシティ オブ マサチューセッツ
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  • Diabetes (AREA)
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JP2019520377A 2016-10-13 2017-10-13 Ａａｖカプシド設計 Active JP7577291B6 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2023015896A JP7742533B2 (ja) 2016-10-13 2023-02-06 Ａａｖカプシド設計

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US201662408022P 2016-10-13 2016-10-13
US62/408,022 2016-10-13
US201662417756P 2016-11-04 2016-11-04
US62/417,756 2016-11-04
US201762486642P 2017-04-18 2017-04-18
US62/486,642 2017-04-18
PCT/US2017/056614 WO2018071831A1 (en) 2016-10-13 2017-10-13 Aav capsid designs

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2023015896A Division JP7742533B2 (ja) 2016-10-13 2023-02-06 Ａａｖカプシド設計

Publications (4)

Publication Number Publication Date
JP2019530463A JP2019530463A (ja) 2019-10-24
JP2019530463A5 JP2019530463A5 (OSRAM) 2020-11-26
JP7577291B2 JP7577291B2 (ja) 2024-11-05
JP7577291B6 true JP7577291B6 (ja) 2024-11-26

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JP2019520377A Active JP7577291B6 (ja) 2016-10-13 2017-10-13 Ａａｖカプシド設計
JP2023015896A Active JP7742533B2 (ja) 2016-10-13 2023-02-06 Ａａｖカプシド設計

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Country Link
US (2) US11578340B2 (OSRAM)
EP (1) EP3526333A4 (OSRAM)
JP (2) JP7577291B6 (OSRAM)
KR (2) KR20190075964A (OSRAM)
CN (1) CN110506119A (OSRAM)
AU (2) AU2017341849B2 (OSRAM)
CA (1) CA3040483A1 (OSRAM)
WO (1) WO2018071831A1 (OSRAM)

Families Citing this family (44)

* Cited by examiner, † Cited by third party
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WO2010138263A2 (en) 2009-05-28 2010-12-02 University Of Massachusetts Novel aav 's and uses thereof
EP3209311B1 (en) 2014-10-21 2024-03-06 University of Massachusetts Recombinant aav variants and uses thereof
GB201508026D0 (en) 2015-05-11 2015-06-24 Ucl Business Plc Capsid
AU2017341849B2 (en) 2016-10-13 2024-03-21 University Of Massachusetts AAV capsid designs
US20200316221A1 (en) * 2016-10-13 2020-10-08 University Of Massachusetts Aav capsid designs
US20180182497A1 (en) * 2016-12-22 2018-06-28 DxRx, Inc. Creating engagement with an inner circle social network in substance abuse treatment
CN110462037A (zh) * 2017-01-30 2019-11-15 学校法人日本医科大学 腺相关病毒(aav)衣壳蛋白的突变体
MX2019012113A (es) 2017-04-14 2020-09-10 Univ Nat Taiwan Terapia génica para la deficiencia de la aadc.
WO2019158619A1 (en) * 2018-02-15 2019-08-22 Bjoerklund Tomas Modified viral capsids
US12421525B2 (en) 2018-02-28 2025-09-23 University of Pittsburgh—of the Commonwealth System of Higher Education Conjugates comprising AAVs and CAS9 polypeptides
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