JP7420710B2 - 組換えａａｖ９由来ベクターの治療有効量の網膜下送達を含む、対象の錐体視細胞において目的のポリヌクレオチドを発現させる方法 - Google Patents
組換えａａｖ９由来ベクターの治療有効量の網膜下送達を含む、対象の錐体視細胞において目的のポリヌクレオチドを発現させる方法 Download PDFInfo
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| JP2024520558A (ja) * | 2021-05-26 | 2024-05-24 | スパーリングヴィジョン | Ｇタンパク質ゲート－ｋ＋チャネルを介した桿体－錐体ジストロフィー（ｒｃｄ）における光感受性の増強 |
| CN120303405A (zh) | 2022-10-20 | 2025-07-11 | 节约视觉公司 | 用于治疗视网膜退行性疾病的组合物和方法 |
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| WO2016141078A1 (en) | 2015-03-02 | 2016-09-09 | Avalanche Biotechnologies, Inc. | Compositions and methods for intravitreal delivery of polynucleotides to retinal cones |
| JP2017510296A (ja) | 2014-03-17 | 2017-04-13 | アドヴェラム バイオテクノロジーズ， インコーポレイテッド | 錐体細胞における増強された遺伝子発現のための組成物および方法 |
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| CA2265460A1 (en) | 1996-09-11 | 1998-03-19 | The Government Of The United States Of America, Represented By The Secre Tary, Department Of Health And Human Services | Aav4 vector and uses thereof |
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| KR102763312B1 (ko) | 2025-02-07 |
| JP2021500030A (ja) | 2021-01-07 |
| US20210268125A1 (en) | 2021-09-02 |
| KR20200103634A (ko) | 2020-09-02 |
| EP3697448A1 (en) | 2020-08-26 |
| CN111867635A (zh) | 2020-10-30 |
| US11723988B2 (en) | 2023-08-15 |
| WO2019077159A1 (en) | 2019-04-25 |
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