JP7374119B2 - 減少した肝臓向性を有するＡＡＶ９とＡＡＶｒｈ７４とのハイブリッド組換えアデノ随伴ウイルス血清型 - Google Patents
減少した肝臓向性を有するＡＡＶ９とＡＡＶｒｈ７４とのハイブリッド組換えアデノ随伴ウイルス血清型 Download PDFInfo
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| CN114127088B (zh) * | 2019-04-23 | 2024-05-14 | 国家医疗保健研究所 | 变体衣壳蛋白和腺相关病毒aav变体及其药物组合物 |
| JP7651562B2 (ja) | 2019-09-19 | 2025-03-26 | ジェネトン | Ｆｋｒｐの心毒性を軽減する遺伝子治療発現系 |
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| US12188039B2 (en) | 2019-11-08 | 2025-01-07 | The Board Of Regents Of The University Of Texas System | Recombinant adeno-associated viral vector for gene delivery |
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| EP4077684A1 (en) | 2019-12-18 | 2022-10-26 | Genethon | Production of recombinant viral vectors from plant hairy roots |
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| WO2022226301A1 (en) * | 2021-04-23 | 2022-10-27 | The University Of North Carolina At Chapel Hill | Chimeric heart tropic aav capsids |
| EP4381077A1 (en) | 2021-08-04 | 2024-06-12 | Genethon | Hybrid promoters for gene expression in muscles and in the cns |
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| US12037362B2 (en) | 2024-07-16 |
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| RU2020136195A (ru) | 2022-05-06 |
| MA51353A1 (fr) | 2021-09-30 |
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| ZA202005422B (en) | 2023-03-29 |
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| US20240317814A1 (en) | 2024-09-26 |
| TN2020000187A1 (en) | 2022-04-04 |
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