JP7261583B2 - 補体媒介性疾患を処置するための組成物及び方法 - Google Patents

補体媒介性疾患を処置するための組成物及び方法 Download PDF

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JP7261583B2
JP7261583B2 JP2018515539A JP2018515539A JP7261583B2 JP 7261583 B2 JP7261583 B2 JP 7261583B2 JP 2018515539 A JP2018515539 A JP 2018515539A JP 2018515539 A JP2018515539 A JP 2018515539A JP 7261583 B2 JP7261583 B2 JP 7261583B2
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complement
mice
variant
aav
vector
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JP2018527941A (ja
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宋文超
ガリパリ，ダモダル
三輪隆史
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ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア
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    • C—CHEMISTRY; METALLURGY
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    • C07K14/00—Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof
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    • C12N2750/14011—Parvoviridae
    • C12N2750/14111—Dependovirus, e.g. adenoassociated viruses
    • C12N2750/14171—Demonstrated in vivo effect

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JP2018515539A 2015-09-24 2016-09-23 補体媒介性疾患を処置するための組成物及び方法 Active JP7261583B2 (ja)

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JP2021128847A JP7324253B2 (ja) 2015-09-24 2021-08-05 補体媒介性疾患を処置するための組成物及び方法
JP2023123167A JP2023139256A (ja) 2015-09-24 2023-07-28 補体媒介性疾患を処置するための組成物及び方法
JP2024209719A JP2025029082A (ja) 2015-09-24 2024-12-02 補体媒介性疾患を処置するための組成物及び方法

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US201562232008P 2015-09-24 2015-09-24
US62/232,008 2015-09-24
PCT/US2016/053347 WO2017053732A2 (en) 2015-09-24 2016-09-23 Composition and method for treating complement-mediated disease

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JP2018527941A JP2018527941A (ja) 2018-09-27
JP2018527941A5 JP2018527941A5 (https=) 2019-11-07
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JP2021128847A Active JP7324253B2 (ja) 2015-09-24 2021-08-05 補体媒介性疾患を処置するための組成物及び方法
JP2023123167A Pending JP2023139256A (ja) 2015-09-24 2023-07-28 補体媒介性疾患を処置するための組成物及び方法
JP2024209719A Pending JP2025029082A (ja) 2015-09-24 2024-12-02 補体媒介性疾患を処置するための組成物及び方法

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JP2023123167A Pending JP2023139256A (ja) 2015-09-24 2023-07-28 補体媒介性疾患を処置するための組成物及び方法
JP2024209719A Pending JP2025029082A (ja) 2015-09-24 2024-12-02 補体媒介性疾患を処置するための組成物及び方法

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US (4) US10988519B2 (https=)
EP (1) EP3359663A4 (https=)
JP (4) JP7261583B2 (https=)
KR (1) KR102773865B1 (https=)
CN (2) CN108291216B (https=)
AU (3) AU2016326627B2 (https=)
CA (1) CA2999299A1 (https=)
HK (1) HK1251482A1 (https=)
IL (2) IL258024B2 (https=)
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Cited By (1)

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JP2023139256A (ja) * 2015-09-24 2023-10-03 ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア 補体媒介性疾患を処置するための組成物及び方法

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