JP7261583B2 - 補体媒介性疾患を処置するための組成物及び方法 - Google Patents
補体媒介性疾患を処置するための組成物及び方法 Download PDFInfo
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| GB201800620D0 (en) * | 2018-01-15 | 2018-02-28 | Univ Manchester | C3b Binding Polypeptide |
| CA3119531A1 (en) * | 2018-12-12 | 2020-06-18 | Flagship Pioneering Innovations V, Inc. | Anellosomes for delivering secreted therapeutic modalities |
| GB201821082D0 (en) * | 2018-12-21 | 2019-02-06 | Gyroscope Therapeutics Ltd | Combination of complement factors i and h, and vector encoding thereof |
| EP3966231A4 (en) * | 2019-04-10 | 2022-12-21 | University of Massachusetts | Factor h vectors and uses thereof |
| AU2020371663A1 (en) * | 2019-10-22 | 2022-05-19 | Applied Genetic Technologies Corporation | Adeno-associated virus (AAV)vectors for the treatment of age-related macular degeneration and other ocular diseases and disorders |
| WO2021081401A1 (en) * | 2019-10-23 | 2021-04-29 | Gemini Therapeutics Inc. | Methods for treating patients having cfh mutations with cfh-encoding vectors |
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| GB202010009D0 (en) * | 2020-06-30 | 2020-08-12 | Syncona Investment Man Ltd | Vector |
| AU2022214429A1 (en) | 2021-02-01 | 2023-09-14 | Tern Therapeutics, Llc | Gene therapy for neuronal ceroid lipofuscinoses |
| KR20240112733A (ko) | 2023-01-11 | 2024-07-19 | 포항공과대학교 산학협력단 | 조현병의 예방 또는 치료용 나노바디 |
| WO2024240095A1 (zh) * | 2023-05-19 | 2024-11-28 | 合肥星眸生物科技有限公司 | 用于治疗补体旁路相关疾病的aav载体 |
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| JP2023139256A (ja) * | 2015-09-24 | 2023-10-03 | ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア | 補体媒介性疾患を処置するための組成物及び方法 |
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