JP6669664B2 - 網膜色素変性症のための遺伝子治療 - Google Patents
網膜色素変性症のための遺伝子治療 Download PDFInfo
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| US201461969027P | 2014-03-21 | 2014-03-21 | |
| US61/969,027 | 2014-03-21 | ||
| PCT/US2015/021896 WO2015143418A2 (en) | 2014-03-21 | 2015-03-20 | Gene therapy for retinitis pigmentosa |
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| JP2017509632A JP2017509632A (ja) | 2017-04-06 |
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| JP2022046280A Active JP7534348B2 (ja) | 2014-03-21 | 2022-03-23 | 網膜色素変性症のための遺伝子治療 |
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| JP2022046280A Active JP7534348B2 (ja) | 2014-03-21 | 2022-03-23 | 網膜色素変性症のための遺伝子治療 |
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Cited By (1)
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| JP2020059737A (ja) * | 2014-03-21 | 2020-04-16 | ジェンザイム・コーポレーション | 網膜色素変性症のための遺伝子治療 |
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| HK1247641A1 (zh) | 2015-02-10 | 2018-09-28 | Genzyme Corporation | 变体RNAi |
| ES2886664T3 (es) * | 2015-12-03 | 2021-12-20 | Friedrich Miescher Institute For Biomedical Res | SynP162, un promotor para la expresión específica de genes en fotorreceptores de bastón |
| US10994026B2 (en) | 2015-12-03 | 2021-05-04 | Friedrich Miescher Institute For Biomedical Research | SynP160, a promoter for the specific expression of genes in rod photoreceptors |
| AU2016363830C1 (en) * | 2015-12-04 | 2022-03-24 | Centre National De La Recherche Scientifique | Promoters and uses thereof |
| AU2017227776C1 (en) * | 2016-03-01 | 2024-01-25 | The Trustees Of The University Of Pennsylvania | AAV vectors for treatment of dominant retinitis pigmentosa |
| EP3481434A4 (en) * | 2016-07-05 | 2020-06-24 | The Johns Hopkins University | Crispr/cas9-based compositions and methods for treating retinal degenerations |
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Cited By (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| JP2020059737A (ja) * | 2014-03-21 | 2020-04-16 | ジェンザイム・コーポレーション | 網膜色素変性症のための遺伝子治療 |
| JP7048563B2 (ja) | 2014-03-21 | 2022-04-05 | ジェンザイム・コーポレーション | 網膜色素変性症のための遺伝子治療 |
| US12201698B2 (en) | 2014-03-21 | 2025-01-21 | Genzyme Corporation | Gene therapy for retinitis pigmentosa |
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